Early research (Phase 1)Study completedNCT01253317What this trial is testingTreatment of Rett Syndrome With rhIGF-1 (Mecasermin [rDNA]Injection)Who this might be right forRett Syndrome Boston Children's Hospital 12
Not applicableStudy completedNCT00630422What this trial is testingFunctional Abilities in Rett SyndromeWho this might be right forRett Syndrome Faculdades Metropolitanas Unidas 64
Not applicableEnrolling By InvitationNCT03836300What this trial is testingParent and Infant Inter(X)Action Intervention (PIXI)Who this might be right forFragile X SyndromeAngelman SyndromePrader-Willi Syndrome+11 more RTI International 120
Large-scale testing (Phase 3)Study completedNCT04181723What this trial is testingStudy of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™)Who this might be right forRett Syndrome ACADIA Pharmaceuticals Inc. 187
Large-scale testing (Phase 3)Ended earlyNCT04252586What this trial is testingA Long-term Safety Study of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett SyndromeWho this might be right forRett SyndromeRTT Jazz Pharmaceuticals 21
Testing effectiveness (Phase 2)Ended earlyNCT00593957What this trial is testingTrial of Dextromethorphan in Rett SyndromeWho this might be right forRett Syndrome Hugo W. Moser Research Institute at Kennedy Krieger, Inc. 38
Testing effectiveness (Phase 2)Study completedNCT02563860What this trial is testingPharmacological Treatment of Rett Syndrome With StatinsWho this might be right forRett Syndrome Montefiore Medical Center 20
Large-scale testing (Phase 3)Study completedNCT03941444What this trial is testingANAVEX2-73 Study in Patients With Rett SyndromeWho this might be right forRett Syndrome Anavex Life Sciences Corp. 33
Not applicableActive Not RecruitingNCT06014541What this trial is testingObservational Study to Characterize Biomarkers and Disease Progression in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication SyndromeWho this might be right forMethyl CpG Binding Protein 2 (MECP2) Duplication Syndrome Ionis Pharmaceuticals, Inc. 29
Testing effectiveness (Phase 2)Study completedNCT01703533What this trial is testingA Safety Study of NNZ-2566 in Patients With Rett SyndromeWho this might be right forRett Syndrome Neuren Pharmaceuticals Limited 67
Not applicableStudy completedNCT02670694What this trial is testingSleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PWWho this might be right forRett SyndromePrader-Willi SyndromeAngelman Syndrome+1 more Baylor College of Medicine 804
Not applicableStudy completedNCT05352373What this trial is testingThe Role of Dietary Calcium for the Treatment of Osteopenia in Girls With Rett SyndromeWho this might be right forRett Syndrome Baylor College of Medicine 32
Not applicableUnknownNCT04167059What this trial is testingTelehealth Support to Increase Physical Activity in Rett SyndromeWho this might be right forRett Syndrome Telethon Kids Institute 60
Not applicableStudy completedNCT04920110What this trial is testingDevelopment of the ORCA Communication Measure for Rett SyndromeWho this might be right forRett Syndrome Rett Syndrome Research Trust 272
Not applicableStudy completedNCT05687214What this trial is testingOsteopathic Manipulative Treatment for Constipation in People With Rett SyndromeWho this might be right forRett Syndrome Ariel University 12
Not applicableStudy completedNCT06335368What this trial is testingAssessment of Nutritional and Growth Status in Rett Syndrome PatientsWho this might be right forRett SyndromeNeurologic Disorder National Taiwan University Hospital 70
Not applicableStudy completedNCT00004656What this trial is testingNutritional Aspects of Rett SyndromeWho this might be right forRett Syndrome Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Not applicableStudy completedNCT01147575What this trial is testingEffects of Creatine Supplementation in Rett SyndromeWho this might be right forRett Syndrome Medical University of Vienna 21
Not applicableStudy completedNCT00464477What this trial is testingAdvanced Grandparental Age as a Risk Factor for AutismWho this might be right forAutistic DisorderPervasive Developmental DisorderAsperger Syndrome+2 more University of Mississippi Medical Center 100
Large-scale testing (Phase 3)Looking for participantsNCT06840496What this trial is testingTo Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett SyndromeWho this might be right forRett Syndrome Biomed Industries, Inc. 210