Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • About
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Rare Anemia Disorders”

53 trials

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 53 results

Not applicableLooking for participantsNCT06539169
What this trial is testing

FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

Who this might be right for
Alpha-ThalassemiaBeta-ThalassemiaAmyloidosis+14 more
xCures 1,000
Not applicableEnrolling By InvitationNCT03655223
What this trial is testing

Early Check: Expanded Screening in Newborns

Who this might be right for
Spinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more
RTI International 30,000
Testing effectiveness (Phase 2)Study completedNCT00006136
What this trial is testing

Phase II Study of Arginine Butyrate With or Without Epoetin Alfa in Patients With Thalassemia Intermedia

Who this might be right for
Beta-Thalassemia
Boston University 15
Not applicableStudy completedNCT00004378
What this trial is testing

Stem Cell Transplantation (SCT) for Genetic Diseases

Who this might be right for
ThrombocytopeniaMetachromatic LeukodystrophyFanconi's Anemia+3 more
National Center for Research Resources (NCRR)
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07331818
What this trial is testing

Luspatercept in Patients Affected With Rare Inherited Anemias

Who this might be right for
Hereditary Red Blood Cell Disorder (Disorder)
EuroBloodNet Association 45
Early research (Phase 1)UnknownNCT00005896
What this trial is testing

Phase I Pilot Study of CD34 Enriched, Fanconi's Anemia Complementation Group C Gene Transduced Autologous Peripheral Blood Stem Cell Transplantation in Patients With Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
University of Minnesota 6
Not applicableLooking for participantsNCT06065852
What this trial is testing

National Registry of Rare Kidney Diseases

Who this might be right for
Adenine Phosphoribosyltransferase DeficiencyAH AmyloidosisAHL Amyloidosis+81 more
UK Kidney Association 35,000
Not applicableStudy completedNCT00004797
What this trial is testing

Pilot Study of Fructose for Sickle Cell Crisis

Who this might be right for
Sickle Cell Anemia
National Center for Research Resources (NCRR) 20
Testing effectiveness (Phase 2)Study completedNCT00004464
What this trial is testing

Study of High Dose Cyclophosphamide in Patients With Severe Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Aplastic AnemiaParoxysmal Hemoglobinuria, Nocturnal
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins 69
Not applicableStudy completedNCT00005893
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders

Who this might be right for
NeutropeniaSickle Cell AnemiaThalassemia Major+1 more
Fairview University Medical Center
Not applicableLooking for participantsNCT04746066
What this trial is testing

Observational Study for Patients With Hemoglobinopathies and Rare Inherited Anemia and Covid 19

Who this might be right for
Haemoglobinopathies
Società Italiana Talassemie ed Emoglobinopatie 10,000
Post-approval studies (Phase 4)Study completedNCT01250951
What this trial is testing

This Study Will Evaluate Efficacy and Safety of Deferasirox in Patients With Myelodysplastic Syndromes (MDS), Thalassemia and Rare Anemia Types Having Transfusion-induced Iron Overload.

Who this might be right for
Myelodysplastic SyndromeThalassemia
Novartis Pharmaceuticals 111
Post-approval studies (Phase 4)Study completedNCT00171301
What this trial is testing

Extension Study of the Efficacy and Safety of Deferasirox Treatment in Beta-thalassemia Patients With Transfusional Hemosiderosis (Study Amended to 2-year Duration)

Who this might be right for
Beta-thalassemia MajorHemosiderosisIron Overload+1 more
Novartis Pharmaceuticals 233
Large-scale testing (Phase 3)Study completedNCT04679103
What this trial is testing

A Safety and Immunogenicity Study in Long-term Treatment of Eculizumab (JSC "GENERIUM", Russian Federation)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
AO GENERIUM 50
Not applicableStudy completedNCT06831799
What this trial is testing

ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19

Who this might be right for
HemoglobinopathiesSickle Cell DiseaseSickle Cell Anemia+21 more
Hospital Universitari Vall d'Hebron Research Institute 684
Early research (Phase 1)UnknownNCT00006127
What this trial is testing

Phase I Study of Amifostine in Patients With Bone Marrow Failure Related to Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
Dana-Farber Cancer Institute 21
Large-scale testing (Phase 3)Study completedNCT00004474
What this trial is testing

Phase III Randomized Study of Cyclophosphamide With or Without Antithymocyte Globulin Before Bone Marrow Transplantation in Patients With Aplastic Anemia

Who this might be right for
Aplastic Anemia
Roswell Park Cancer Institute 224
Early research (Phase 1)Ended earlyNCT02630927
What this trial is testing

A Safety and Tolerability Study of AG-519 in Healthy Subjects

Who this might be right for
Anemia
Agios Pharmaceuticals, Inc. 108
Not applicableLooking for participantsNCT06250595
What this trial is testing

European Rare Blood Disorders Platform (ENROL)

Who this might be right for
AnemiaBone Marrow FailureBleeding Disorder+9 more
Hospital Universitari Vall d'Hebron Research Institute 37,090
Not applicableWithdrawnNCT04541875
What this trial is testing

Medication Adherence and Non-adherence in Adults With Rare Disease

Who this might be right for
Cystic FibrosisHemophilia AHemophilia B+3 more
Xperiome
Load More Results