Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • About
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Rare Disease”

979 trials

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 979 results

Testing effectiveness (Phase 2)Study completedNCT02923934
What this trial is testing

A Phase II Trial of Ipilimumab and Nivolumab for the Treatment of Rare Cancers

Who this might be right for
Gastrointestinal CancerNeuroendocrine TumoursMalignant Female Reproductive System Neoplasm
Olivia Newton-John Cancer Research Institute 120
Testing effectiveness (Phase 2)Ended earlyNCT04171700
What this trial is testing

Evaluate Rucaparib in Participants With Solid Tumors and With Deleterious Mutations in HRR Genes

Who this might be right for
Solid Tumor
pharmaand GmbH 83
Not applicableLooking for participantsNCT04265144
What this trial is testing

Cohort of Patients With Systemic Sclerosis Within the Framework of the RESO Reference Centre

Who this might be right for
SclerodermaSystemic Sclerosis
University Hospital, Bordeaux 500
Not applicableStudy completedNCT04200664
What this trial is testing

Audiovestibular Function in Infratentorial Superficial Siderosis

Who this might be right for
SiderosisNeurological DisorderRare Diseases+2 more
University College, London 11
Not applicableUnknownNCT05347511
What this trial is testing

Study of the Pronostic Impact of Immunohistochemical, Histological and Radiological Factors in Patients With Primary Central Nervous System Lymphoma.

Who this might be right for
Rare Disease With Poor Outcome
Central Hospital, Nancy, France 94
Testing effectiveness (Phase 2)Study completedNCT00004464
What this trial is testing

Study of High Dose Cyclophosphamide in Patients With Severe Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Aplastic AnemiaParoxysmal Hemoglobinuria, Nocturnal
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins 69
Large-scale testing (Phase 3)Study completedNCT00659100
What this trial is testing

A Trial to Assess Consumer Self-Selection and Use of Gabapentin for Occasional Sleeplessness in an Over-the-Counter Environment

Who this might be right for
Transient Insomnia
Pfizer's Upjohn has merged with Mylan to form Viatris Inc. 1,254
Testing effectiveness (Phase 2)Study completedNCT00004658
What this trial is testing

Phase II Study of Ribose, Uridine, and Thymidine for a Complex Syndrome Involving Excessive 5'-Nucleotidase Activity

Who this might be right for
5'-Nucleotidase Syndrome
National Center for Research Resources (NCRR)
Not applicableStudy completedNCT00004832
What this trial is testing

Randomized Study of 3,4-Diaminopyridine for Lambert-Eaton Myasthenic Syndrome

Who this might be right for
Lambert-Eaton Myasthenic Syndrome
FDA Office of Orphan Products Development 26
Not applicableAvailableNCT06931834
What this trial is testing

Expanded Access Program for R007 (Probucol) Tablets in Adults With Mitochondrial Disease and Chronic Kidney Disease

Who this might be right for
Mitochondrial DiseaseChronic Kidney Disease
RiboNova Inc.
Not applicableUnknownNCT04353609
What this trial is testing

Covid-19 in Patients With Chronic Inflammatory Rheumatism, Auto-immune or Auto-inflammatory Rare and Non-rare Diseases

Who this might be right for
Sars-CoV2Chronic Inflammatory RheumatismAutoimmune Diseases
University Hospital, Lille 13,770
Not applicableLooking for participantsNCT03305835
What this trial is testing

Monogenic Kidney Stone - Genetic Testing

Who this might be right for
Rare Kidney Stone Diseases
Mayo Clinic 6,000
Testing effectiveness (Phase 2)UnknownNCT05548348
What this trial is testing

First-line Furmonertinib in Advanced NSCLC Patients With EGFR Uncommon Mutation

Who this might be right for
Non-small Cell Lung CancerEGFR G719XEGFR L861Q+1 more
Chongqing University Cancer Hospital 30
Testing effectiveness (Phase 2)Looking for participantsNCT04372615
What this trial is testing

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

Who this might be right for
Autoimmune EncephalitisEncephalitis
University of Utah 116
Early research (Phase 1)Study completedNCT00004806
What this trial is testing

Phase I Study of Liposome-Mediated Gene Transfer in Patients With Cystic Fibrosis

Who this might be right for
Cystic Fibrosis
University of Alabama at Birmingham 9
Testing effectiveness (Phase 2)Study completedNCT00004485
What this trial is testing

Bone Marrow Transplantation in Treating Children With Sickle Cell Disease

Who this might be right for
Sickle Cell Anemia
Fred Hutchinson Cancer Center 50
Not applicableLooking for participantsNCT06573723
What this trial is testing

Institutional Registry of Rare Diseases

Who this might be right for
Rare DiseasesAmyloidosisSarcoidosis+23 more
Hospital Italiano de Buenos Aires 380
Testing effectiveness (Phase 2)UnknownNCT00004310
What this trial is testing

Phase II Randomized Study of Intravenous Versus Oral Clomipramine in Patients With Obsessive Compulsive Disorder

Who this might be right for
Obsessive-Compulsive Disorder
National Center for Research Resources (NCRR) 76
Not applicableStudy completedNCT00007059
What this trial is testing

Study of the Pharmacokinetics of Mycophenolate Mofetil in Patients Who Have Undergone Orthotopic Liver Transplantation

Who this might be right for
Graft Versus Host Disease
National Center for Research Resources (NCRR) 20
Not applicableUnknownNCT04315727
What this trial is testing

Identification of the Genetic Causes of Rare Diseases With Negative Exome Findings

Who this might be right for
Rare DiseasesGenetic Predisposition to Disease
University Hospital Tuebingen 100
Load More Results