Large-scale testing (Phase 3)Looking for participantsNCT07503444What this trial is testingFenfluramine Hydrochloride in Rett SyndromeWho this might be right forRett Syndrome UCB BIOSCIENCES, Inc. 200
Not applicableStudy completedNCT00496210What this trial is testingPredictors of Caregiver Adaptation to Pervasive Developmental DisordersWho this might be right forAutismAsperger's SyndromeRett's Disorder National Human Genome Research Institute (NHGRI) 324
Large-scale testing (Phase 3)Ended earlyNCT03848832What this trial is testingEfficacy and Safety of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett SyndromeWho this might be right forRett SyndromeRTT Jazz Pharmaceuticals 29
Testing effectiveness (Phase 2)Looking for participantsNCT04041713What this trial is testingA Pilot Study of an Antioxidant Cocktail vs. Placebo in the Treatment of Children and Adolescents With Rett SyndromeWho this might be right forRett Syndrome Holland Bloorview Kids Rehabilitation Hospital 35
Testing effectiveness (Phase 2)Study completedNCT03758924What this trial is testingStudy of ANAVEX2-73 in Patients With Rett SyndromeWho this might be right forRett Syndrome Anavex Life Sciences Corp. 31
Not applicableActive Not RecruitingNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Early research (Phase 1)Looking for participantsNCT07150013What this trial is testingRett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett SyndromeWho this might be right forRett Syndrome Unravel Biosciences, Inc. 15
Not applicableStudy completedNCT06335368What this trial is testingAssessment of Nutritional and Growth Status in Rett Syndrome PatientsWho this might be right forRett SyndromeNeurologic Disorder National Taiwan University Hospital 70
Not applicableStudy completedNCT02885090What this trial is testingNew Genes Involved in Molecular Etiology of Rett Syndrome Through DNA Microarray Comparative Genomic HybridizationWho this might be right forRett Syndrome Central Hospital, Nancy, France 17
Large-scale testing (Phase 3)Not Yet RecruitingNCT07257978What this trial is testingEfficacy and Safety of NTI164 in Children and Young Adults With Rett SyndromeWho this might be right forRETT Syndrome With Proven MECP2 MutationRett Syndrome Fenix Innovation Group 40
Not applicableActive Not RecruitingNCT07151950What this trial is testingObi Medical Robot: Evaluating Effectiveness Related to UsabilityWho this might be right forUpper Extremity ImpairmentsCerebral Palsy (CP)ALS - Amyotrophic Lateral Sclerosis+1 more Desin LLC 50
Not applicableStudy completedNCT05352373What this trial is testingThe Role of Dietary Calcium for the Treatment of Osteopenia in Girls With Rett SyndromeWho this might be right forRett Syndrome Baylor College of Medicine 32
Not applicableStudy completedNCT00004656What this trial is testingNutritional Aspects of Rett SyndromeWho this might be right forRett Syndrome Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Large-scale testing (Phase 3)Active Not RecruitingNCT07480564What this trial is testingSafety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett SyndromeWho this might be right forRett Syndrome Taysha Gene Therapies, Inc. 4
Not applicableLooking for participantsNCT04900493What this trial is testingThe Rett Syndrome Global RegistryWho this might be right forRett Syndrome Rett Syndrome Research Trust 5,000
Not applicableStudy completedNCT05691582What this trial is testingTolerability of the Immersive Virtual Reality System Grail in Subjects Affected by Rett SyndromeWho this might be right forRett Syndrome IRCCS Eugenio Medea 9
Not applicableUnknownNCT04014985What this trial is testingPatients With RETT SyndromeWho this might be right forRett Syndrome Assistance Publique Hopitaux De Marseille 100
Testing effectiveness (Phase 2)Looking for participantsNCT06430385What this trial is testingATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)Who this might be right forMethyl CpG Binding Protein 2 (MECP2) Duplication Syndrome Ionis Pharmaceuticals, Inc. 48
Testing effectiveness (Phase 2)Ended earlyNCT00593957What this trial is testingTrial of Dextromethorphan in Rett SyndromeWho this might be right forRett Syndrome Hugo W. Moser Research Institute at Kennedy Krieger, Inc. 38
Testing effectiveness (Phase 2)UnknownNCT03059160What this trial is testingOpen Label Trial of Triheptanoin (UX007) in Treatment of Rett Syndrome.Who this might be right forRett Syndrome Sheba Medical Center 10