Not applicableUnknownNCT02903056What this trial is testingThe Findings of MR Imaging in Rett SyndromeWho this might be right forRett Syndrome National Taiwan University Hospital 100
Large-scale testing (Phase 3)Ended earlyNCT04252586What this trial is testingA Long-term Safety Study of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett SyndromeWho this might be right forRett SyndromeRTT Jazz Pharmaceuticals 21
Testing effectiveness (Phase 2)WithdrawnNCT02226458What this trial is testingAn Exploratory Open Label Study of EPI-743 (Vincerinone TM) in Children With Autism Spectrum DisorderWho this might be right forAutism Spectrum Disorder Edison Pharmaceuticals Inc
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Not applicableLooking for participantsNCT06338267What this trial is testingValidating Innovative Biosensors for Rett Autonomic Symptom TrackingWho this might be right forRett Syndrome Rett Syndrome Research Trust 30
Large-scale testing (Phase 3)Looking for participantsNCT05606614What this trial is testingA Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)Who this might be right forRett Syndrome Taysha Gene Therapies, Inc. 15
Testing effectiveness (Phase 2)Looking for participantsNCT07430046What this trial is testingRepurposing Mirtazapine in Rett SyndromeWho this might be right forRETT Syndrome With Proven MECP2 Mutation University of Trieste 54
Large-scale testing (Phase 3)Ended earlyNCT04776746What this trial is testingOpen-Label Extension Study of Trofinetide for Rett SyndromeWho this might be right forRett Syndrome ACADIA Pharmaceuticals Inc. 77
Not applicableStudy completedNCT00891956What this trial is testingThe Role of Family Functioning in Adaptation to Being a Caregiver of an Individual With Rett SyndromeWho this might be right forRett Syndrome National Human Genome Research Institute (NHGRI) 426
Large-scale testing (Phase 3)Looking for participantsNCT07480564What this trial is testingSafety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett SyndromeWho this might be right forRett Syndrome Taysha Gene Therapies, Inc. 3
Not applicableLooking for participantsNCT05740761What this trial is testingGene Editing as a Therapeutic Approach for Rett SyndromeWho this might be right forRett Syndrome University of Siena 40
Not applicableStudy completedNCT02670694What this trial is testingSleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PWWho this might be right forRett SyndromePrader-Willi SyndromeAngelman Syndrome+1 more Baylor College of Medicine 804
Not applicableLooking for participantsNCT04900493What this trial is testingThe Rett Syndrome Global RegistryWho this might be right forRett Syndrome Rett Syndrome Research Trust 5,000
Not applicableUnknownNCT04014985What this trial is testingPatients With RETT SyndromeWho this might be right forRett Syndrome Assistance Publique Hopitaux De Marseille 100
Not applicableStudy completedNCT06335368What this trial is testingAssessment of Nutritional and Growth Status in Rett Syndrome PatientsWho this might be right forRett SyndromeNeurologic Disorder National Taiwan University Hospital 70
Testing effectiveness (Phase 2)Study completedNCT03633058What this trial is testingEvaluate Ketamine for the Treatment of Rett SyndromeWho this might be right forRett Syndrome Rett Syndrome Research Trust 23
Very early researchActive Not RecruitingNCT06856759What this trial is testingSingle-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett SyndromeWho this might be right forRett Syndrome Guangzhou Women and Children's Medical Center 8
Not applicableStudy completedNCT00496210What this trial is testingPredictors of Caregiver Adaptation to Pervasive Developmental DisordersWho this might be right forAutismAsperger's SyndromeRett's Disorder National Human Genome Research Institute (NHGRI) 324
Large-scale testing (Phase 3)Study completedNCT03941444What this trial is testingANAVEX2-73 Study in Patients With Rett SyndromeWho this might be right forRett Syndrome Anavex Life Sciences Corp. 33
Large-scale testing (Phase 3)Looking for participantsNCT06840496What this trial is testingTo Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett SyndromeWho this might be right forRett Syndrome Biomed Industries, Inc. 210