Testing effectiveness (Phase 2)Study completedNCT02715115What this trial is testingA Safety Study of NNZ-2566 in Pediatric Rett SyndromeWho this might be right forRett Syndrome Neuren Pharmaceuticals Limited 82
Not applicableStudy completedNCT00004656What this trial is testingNutritional Aspects of Rett SyndromeWho this might be right forRett Syndrome Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Not applicableUnknownNCT03259971What this trial is testingThe Role of Probiotics PS128 in Movement DisordersWho this might be right forRett SyndromeTourette SyndromeTic Disorders National Taiwan University Hospital 500
Not applicableStudy completedNCT05691582What this trial is testingTolerability of the Immersive Virtual Reality System Grail in Subjects Affected by Rett SyndromeWho this might be right forRett Syndrome IRCCS Eugenio Medea 9
Very early researchLooking for participantsNCT06856759What this trial is testingSingle-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett SyndromeWho this might be right forRett Syndrome Guangzhou Women and Children's Medical Center 8
Testing effectiveness (Phase 2)Not Yet RecruitingNCT04041713What this trial is testingA Pilot Study of an Antioxidant Cocktail vs. Placebo in the Treatment of Children and Adolescents With Rett SyndromeWho this might be right forRett Syndrome Holland Bloorview Kids Rehabilitation Hospital 35
Large-scale testing (Phase 3)Study completedNCT04304482What this trial is testingANAVEX2-73 Study in Pediatric Patients With Rett SyndromeWho this might be right forRett Syndrome Anavex Life Sciences Corp. 92
Large-scale testing (Phase 3)Study completedNCT04181723What this trial is testingStudy of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™)Who this might be right forRett Syndrome ACADIA Pharmaceuticals Inc. 187
Early research (Phase 1)Study completedNCT01253317What this trial is testingTreatment of Rett Syndrome With rhIGF-1 (Mecasermin [rDNA]Injection)Who this might be right forRett Syndrome Boston Children's Hospital 12
Not applicableStudy completedNCT02670694What this trial is testingSleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PWWho this might be right forRett SyndromePrader-Willi SyndromeAngelman Syndrome+1 more Baylor College of Medicine 804
Not applicableUnknownNCT04014985What this trial is testingPatients With RETT SyndromeWho this might be right forRett Syndrome Assistance Publique Hopitaux De Marseille 100
Very early researchActive Not RecruitingNCT06199700What this trial is testingEsketamine for the Treatment of Rett SyndromeWho this might be right forRett Syndrome Children's Hospital of Fudan University 3
Not applicableLooking for participantsNCT05432349What this trial is testingRett Syndrome RegistryWho this might be right forRett SyndromeRett Syndrome, AtypicalGenetic Disease+7 more International Rett Syndrome Foundation 3,000
Testing effectiveness (Phase 2)Active Not RecruitingNCT06152237What this trial is testingSafety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)Who this might be right forRett Syndrome Taysha Gene Therapies, Inc. 6
Large-scale testing (Phase 3)Study completedNCT06849973What this trial is testingTo Study the Efficacy & Safety of Oral NA-921 (Bionetide) in Girls and Women with Rett SyndromeWho this might be right forRett Syndrome Biomed Industries, Inc. 187
Early research (Phase 1)Not Yet RecruitingNCT07150013What this trial is testingRett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett SyndromeWho this might be right forRett Syndrome Unravel Biosciences, Inc. 15
Not applicableLooking for participantsNCT04463316What this trial is testingGROWing Up With Rare GENEtic SyndromesWho this might be right forPrader-Willi SyndromePWS-like SyndromeSilver Russel Syndrome+30 more dr. Laura C. G. de Graaff-Herder 600
Large-scale testing (Phase 3)Looking for participantsNCT05606614What this trial is testingA Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)Who this might be right forRett Syndrome Taysha Gene Therapies, Inc. 15
Not applicableEnrolling By InvitationNCT06739434What this trial is testingGCB-002 in Treatment of Patients With Rett SyndromeWho this might be right forRETT Syndrome With Proven MECP2 Mutation Genecombio Ltd. 6
Large-scale testing (Phase 3)Looking for participantsNCT05898620What this trial is testingA Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett SyndromeWho this might be right forRett Syndrome Neurogene Inc. 33