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Results for “SMA - Spinal Muscular Atrophy”

367 trials

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Showing 20 of 367 results

Not applicableUnknownNCT05272969
What this trial is testing

Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more
LMU Klinikum 95
Not applicableUnknownNCT03300869
What this trial is testing

Natural History of Types 2 and 3 SMA in Taiwan

Who this might be right for
Spinal Muscular Atrophy
Kaohsiung Medical University Chung-Ho Memorial Hospital 300
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Not applicableEnrolling By InvitationNCT07072676
What this trial is testing

The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.

Who this might be right for
Inclusion Body MyositisMyotonic Dystrophy 1Myotonic Dystrophy 2+10 more
LMU Klinikum 30
Not applicableLooking for participantsNCT06147414
What this trial is testing

Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders

Who this might be right for
Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, IncludingSickle Cell DiseaseCystic Fibrosis+12 more
Assistance Publique - Hôpitaux de Paris 550
Not applicableLooking for participantsNCT07521930
What this trial is testing

Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)

Who this might be right for
Tetraplegia/TetraparesisAmyotrophic Lateral Sclerosis (ALS)Muscular Disorders, Atrophic+6 more
Johns Hopkins University 5
Not applicableStudy completedNCT01233817
What this trial is testing

Progressive Strength Training in Spinal Muscular Atrophy

Who this might be right for
Muscular Atrophy, Spinal
University of Utah 12
Not applicableLooking for participantsNCT06978985
What this trial is testing

Adult SMA Research and Clinical Hub

Who this might be right for
Spinal Muscular Atrophy (SMA)
Newcastle-upon-Tyne Hospitals NHS Trust 600
Not applicableNot Yet RecruitingNCT07530926
What this trial is testing

Adrenal& Bone Complications in Paediatric Patients Living With Spinal Muscular Atrophy (SMA)

Who this might be right for
SMA - Spinal Muscular Atrophy
Sheffield Children's NHS Foundation Trust 550
Not applicableLooking for participantsNCT07286565
What this trial is testing

Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening

Who this might be right for
Spinal Muscular Atrophy (SMA)Duchenne Muscular Dystrophy (DMD)
Centre Hospitalier Universitaire de Liege 100
Not applicableStudy completedNCT06178393
What this trial is testing

Real-World Use of Novel Treatments in Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Chart Review of Pediatric SMA Patients Outside of the United States

Who this might be right for
Spinal Muscular Atrophy
Novartis Pharmaceuticals 162
Testing effectiveness (Phase 2)Looking for participantsNCT05747261
What this trial is testing

Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy (BLUEBELL)

Who this might be right for
Spinal Muscular Atrophy (SMA)
Biocad 40
Not applicableUnknownNCT04710186
What this trial is testing

AR, IGF-IR, IR and Peripheral Artery Disease

Who this might be right for
Androgen Receptor AbnormalInsulin-Like Growth Factor I DeficiencyInsulin Receptor, Defect in
University of Catanzaro 30
Not applicableUnknownNCT04859179
What this trial is testing

Prenatal Carrier Screening for Spinal Muscular Atrophy Among Thai Pregnant Women

Who this might be right for
Spinal Muscular Atrophy
Mahidol University 200
Not applicableNo Longer AvailableNCT06877689
What this trial is testing

EAP of Apitegromab for Patients With Spinal Muscular Atrophy

Who this might be right for
SMA
Scholar Rock, Inc.
Not applicableStudy completedNCT01611610
What this trial is testing

Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)

Who this might be right for
Spinal Muscular Atrophy
Institut de Myologie, France 4
Testing effectiveness (Phase 2)Study completedNCT00227266
What this trial is testing

Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
University of Utah 94
Testing effectiveness (Phase 2)Study completedNCT00568802
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 27
Not applicableStudy completedNCT02795897
What this trial is testing

Genomic Translation for Amyotrophic Lateral Sclerosis Care

Who this might be right for
ALS
Columbia University 254
Large-scale testing (Phase 3)Ended earlyNCT04869943
What this trial is testing

Efficacy Evaluation of Enobosarm Monotherapy in Treatment of AR+/ER+/HER2- Metastatic Breast Cancer

Who this might be right for
Metastatic Breast Cancer
Veru Inc. 52
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