Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • About
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “SMA1”

33 trials

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 33 results

Testing effectiveness (Phase 2)Enrolling By InvitationNCT05614531
What this trial is testing

Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients with Spinal Muscular Atrophy Type 1

Who this might be right for
Spinal Muscular Atrophy Type I
Guangzhou Jiayin Biotech Ltd 12
Not applicableUnknownNCT05475691
What this trial is testing

Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America

Who this might be right for
Spinal Muscular Atrophy
Hospital Israelita Albert Einstein 361
Not applicableStudy completedNCT05715749
What this trial is testing

Body Weight Support Harness System in Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type II
Nationwide Children's Hospital 33
Not applicableLooking for participantsNCT06562283
What this trial is testing

Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal AmyotrophyInfantile Spinal Muscular AtrophyJuvenile Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Saint Etienne 80
Not applicableNot Yet RecruitingNCT07208903
What this trial is testing

Psychological Evaluation of the Parental Experience of Newborn Screening for Infantile Spinal Muscular Atrophy in the Grand Est and Nouvelle-Aquitaine Regions

Who this might be right for
Spinal Muscular Atrophy (SMA)Spinal Muscular Atrophy Type I
University Hospital, Strasbourg, France 36
Not applicableStudy completedNCT00756821
What this trial is testing

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
Carelon Research 130
Testing effectiveness (Phase 2)Study completedNCT00661453
What this trial is testing

CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I

Who this might be right for
Spinal Muscular Atrophy Type I
University of Utah 40
Testing effectiveness (Phase 2)UnknownNCT02855112
What this trial is testing

Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients

Who this might be right for
Infantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]
Tehran University of Medical Sciences 10
Testing effectiveness (Phase 2)Study completedNCT00568698
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 29
Testing effectiveness (Phase 2)Looking for participantsNCT07070999
What this trial is testing

Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1

Who this might be right for
Spinal Muscular Atrophy Type I
Gemma Biotherapeutics 22
Not applicableNot Yet RecruitingNCT07596277
What this trial is testing

Exploring Lived Experiences of Families of Children With Spinal Muscular Atrophy(SMA) Type 1 Regarding Feeding and Communication

Who this might be right for
Spinal Muscular Atrophy 1
Guy's and St Thomas' NHS Foundation Trust 15
Not applicableEnded earlyNCT02550691
What this trial is testing

Identification of a Biomarker Associated With Cis-duplication of the SMN1 Gene

Who this might be right for
Spinal Muscular Atrophy
University Hospital, Rouen 48
Very early researchStudy completedNCT06576388
What this trial is testing

Clinical Trial to Evaluate the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy Type I

Who this might be right for
Type I Spinal Muscular Atrophy
Guangzhou Jiayin Biotech Ltd 2
Not applicableUnknownNCT02831296
What this trial is testing

Prospective Evaluation of Infants With Spinal Muscular Atrophy:

Who this might be right for
Spinal Muscular Atrophy
Massachusetts General Hospital 1,000
Not applicableLooking for participantsNCT06152302
What this trial is testing

Test of Aquatic Mobility of SMA Infants

Who this might be right for
Infantile Spinal Muscular Atrophy
Assistance Publique - Hôpitaux de Paris 15
Not applicableStudy completedNCT06632730
What this trial is testing

Therapeutic Management and Use of Resources and Costs of Spinal Muscular Atrophy in Spain

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type II
Novartis 69
Not applicableStudy completedNCT05878418
What this trial is testing

The Effect of Spinal Orthosis on the Development of Scoliosis and Chest Deformity in Type I Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type IScoliosisChest Deformities+3 more
Medipol University 20
Not applicableUnknownNCT06256887
What this trial is testing

Sleep Spindles Organization as an Early Neural Marker of Neuromotor Outcome

Who this might be right for
EEG Sleep SpindlesMotor OutcomeCerebral Palsy+1 more
IRCCS Fondazione Stella Maris 80
Not applicableActive Not RecruitingNCT03421977
What this trial is testing

Long-Term Follow-up Study for Patients From AVXS-101-CL-101

Who this might be right for
Spinal Muscular Atrophy 1
Novartis Gene Therapies 13
Testing effectiveness (Phase 2)Ended earlyNCT00439218
What this trial is testing

Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I

Who this might be right for
Spinal Muscular Atrophy Type I
Westat 5
Load More Results