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Results for “SMA1”

31 trials

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Showing 20 of 31 results

Not applicableStudy completedNCT06632730
What this trial is testing

Therapeutic Management and Use of Resources and Costs of Spinal Muscular Atrophy in Spain

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type II
Novartis 69
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025
What this trial is testing

Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more
Novartis Gene Therapies 85
Testing effectiveness (Phase 2)Looking for participantsNCT07070999
What this trial is testing

Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1

Who this might be right for
Spinal Muscular Atrophy Type I
Gemma Biotherapeutics 22
Not applicableUnknownNCT02831296
What this trial is testing

Prospective Evaluation of Infants With Spinal Muscular Atrophy:

Who this might be right for
Spinal Muscular Atrophy
Massachusetts General Hospital 1,000
Not applicableEnded earlyNCT01547871
What this trial is testing

Infants With Spinal Muscular Atrophy Type I

Who this might be right for
Spinal Muscular Atrophy
National Institute of Neurological Disorders and Stroke (NINDS) 4
Testing effectiveness (Phase 2)Study completedNCT00661453
What this trial is testing

CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I

Who this might be right for
Spinal Muscular Atrophy Type I
University of Utah 40
Testing effectiveness (Phase 2)Ended earlyNCT00439218
What this trial is testing

Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I

Who this might be right for
Spinal Muscular Atrophy Type I
Westat 5
Not applicableStudy completedNCT01862042
What this trial is testing

Palliative Care in Spinal Muscular Atrophy (SMA) 1

Who this might be right for
Spinal Muscular Atrophy 1
Assistance Publique - Hôpitaux de Paris 39
Not applicableStudy completedNCT00756821
What this trial is testing

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
Carelon Research 130
Not applicableActive Not RecruitingNCT06191354
What this trial is testing

A Clinical Study Evaluating the Safety and Efficacy of SKG0201 Injection in Patients With Spinal Muscular Atrophy Type 1

Who this might be right for
Spinal Muscular Atrophy 1
Kun Sun 12
Not applicableLooking for participantsNCT06562283
What this trial is testing

Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal AmyotrophyInfantile Spinal Muscular AtrophyJuvenile Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Saint Etienne 80
Not applicableStudy completedNCT06864767
What this trial is testing

Impact of Motor and Oral Motor Function on Quality of Life in Children With SMA

Who this might be right for
Spinal Muscular Atrophy Type I
Zeynep HOŞBAY 23
Not applicableActive Not RecruitingNCT03421977
What this trial is testing

Long-Term Follow-up Study for Patients From AVXS-101-CL-101

Who this might be right for
Spinal Muscular Atrophy 1
Novartis Gene Therapies 13
Not applicableStudy completedNCT03395795
What this trial is testing

Trial Evaluating the Interest of Noninvasive Ventilation in NAVA Mode in Respiratory Decompensations Children With Infantile Spinal Muscular Atrophy Type II

Who this might be right for
Infantile Spinal Muscular Atrophy
Assistance Publique - Hôpitaux de Paris 1
Not applicableLooking for participantsNCT07332702
What this trial is testing

Long Read Analysis in Spinal Muscular Atrophy - LOREASI

Who this might be right for
Spinal Muscular Atrophy (SMA)
University Hospital, Rouen 27
Not applicableEnrolling By InvitationNCT06256887
What this trial is testing

Sleep Spindles Organization as an Early Neural Marker of Neuromotor Outcome

Who this might be right for
EEG Sleep SpindlesMotor OutcomeCerebral Palsy+1 more
IRCCS Fondazione Stella Maris 80
Testing effectiveness (Phase 2)Study completedNCT00568698
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 29
Not applicableEnded earlyNCT02550691
What this trial is testing

Identification of a Biomarker Associated With Cis-duplication of the SMN1 Gene

Who this might be right for
Spinal Muscular Atrophy
University Hospital, Rouen 48
Not applicableUnknownNCT05475691
What this trial is testing

Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America

Who this might be right for
Spinal Muscular Atrophy
Hospital Israelita Albert Einstein 361
Testing effectiveness (Phase 2)UnknownNCT02855112
What this trial is testing

Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients

Who this might be right for
Infantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]
Tehran University of Medical Sciences 10
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