Not applicableStudy completedNCT00466349What this trial is testingInternational SMA Patient RegistryWho this might be right forMuscular Atrophy, Spinal Indiana University 3,000
Not applicableStudy completedNCT00756821What this trial is testingA Pilot Study of Biomarkers for Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Carelon Research 130
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025What this trial is testingLong-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioiWho this might be right forSpinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more Novartis Gene Therapies 85
Not applicableUnknownNCT02831296What this trial is testingProspective Evaluation of Infants With Spinal Muscular Atrophy:Who this might be right forSpinal Muscular Atrophy Massachusetts General Hospital 1,000
Not applicableNot Yet RecruitingNCT07208903What this trial is testingPsychological Evaluation of the Parental Experience of Newborn Screening for Infantile Spinal Muscular Atrophy in the Grand Est and Nouvelle-Aquitaine RegionsWho this might be right forSpinal Muscular Atrophy (SMA)Spinal Muscular Atrophy Type I University Hospital, Strasbourg, France 36
Testing effectiveness (Phase 2)UnknownNCT02855112What this trial is testingAllogeneic Adipose Derived Stem Cells for Werdnig Hoffman PatientsWho this might be right forInfantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman] Tehran University of Medical Sciences 10
Not applicableStudy completedNCT05878418What this trial is testingThe Effect of Spinal Orthosis on the Development of Scoliosis and Chest Deformity in Type I Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Type IScoliosisChest Deformities+3 more Medipol University 20
Not applicableLooking for participantsNCT05954455What this trial is testingExploring Bulbar Function, Speech And Communication Development in SMA Type 1Who this might be right forSMA1 Institute of Child Health 30
Not applicableStudy completedNCT02061189What this trial is testingPilot Study of an Innovative Physiotherapy in Patients With Infantile Spinal Muscular Atrophy (SMA)Who this might be right forInfantile Spinal Muscular Atrophy of Type 2 or 3 Assistance Publique - Hôpitaux de Paris 19
Not applicableActive Not RecruitingNCT06191354What this trial is testingA Clinical Study Evaluating the Safety and Efficacy of SKG0201 Injection in Patients With Spinal Muscular Atrophy Type 1Who this might be right forSpinal Muscular Atrophy 1 Kun Sun 12
Very early researchStudy completedNCT06576388What this trial is testingClinical Trial to Evaluate the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy Type IWho this might be right forType I Spinal Muscular Atrophy Guangzhou Jiayin Biotech Ltd 2
Not applicableEnded earlyNCT01547871What this trial is testingInfants With Spinal Muscular Atrophy Type IWho this might be right forSpinal Muscular Atrophy National Institute of Neurological Disorders and Stroke (NINDS) 4
Testing effectiveness (Phase 2)Looking for participantsNCT07554924What this trial is testingA Phase I/II Clinical Study to Evaluate SKG0201 Injection in Subjects With Spinal Muscular Atrophy Type IWho this might be right forSpinal Muscular Atrophy 1 Lanyue Biotech (Hangzhou) Co., Ltd. 11
Not applicableLooking for participantsNCT06562283What this trial is testingEvaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular AtrophyWho this might be right forSpinal AmyotrophyInfantile Spinal Muscular AtrophyJuvenile Spinal Muscular Atrophy Centre Hospitalier Universitaire de Saint Etienne 80
Not applicableStudy completedNCT05715749What this trial is testingBody Weight Support Harness System in Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Type ISpinal Muscular Atrophy Type II Nationwide Children's Hospital 33
Not applicableStudy completedNCT01862042What this trial is testingPalliative Care in Spinal Muscular Atrophy (SMA) 1Who this might be right forSpinal Muscular Atrophy 1 Assistance Publique - Hôpitaux de Paris 39
Not applicableLooking for participantsNCT06152302What this trial is testingTest of Aquatic Mobility of SMA InfantsWho this might be right forInfantile Spinal Muscular Atrophy Assistance Publique - Hôpitaux de Paris 15
Not applicableActive Not RecruitingNCT03421977What this trial is testingLong-Term Follow-up Study for Patients From AVXS-101-CL-101Who this might be right forSpinal Muscular Atrophy 1 Novartis Gene Therapies 13
Testing effectiveness (Phase 2)Ended earlyNCT00439218What this trial is testingClinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type IWho this might be right forSpinal Muscular Atrophy Type I Westat 5
Not applicableStudy completedNCT06632730What this trial is testingTherapeutic Management and Use of Resources and Costs of Spinal Muscular Atrophy in SpainWho this might be right forSpinal Muscular Atrophy Type ISpinal Muscular Atrophy Type II Novartis 69