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Results for “Scheie Syndrome”

Showing 2 of 0 results

Not applicableEnded earlyNCT04628871
What this trial is testing

Long Term Follow-up (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

Who this might be right for
Hemophilia BMucopolysaccharidosis IMucopolysaccharidosis II
Sangamo Therapeutics 13
Not applicableStudy completedNCT00144794
What this trial is testing

Mucopolysaccharidosis I (MPS I) Registry

Who this might be right for
Mucopolysaccharidosis I (MPS I)
Genzyme, a Sanofi Company 1,406

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Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
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Completed
Enrolling by Invitation