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Results for “Severe Osteopetrosis”

11 trials

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Showing 11 of 11 results

Large-scale testing (Phase 3)Study completedNCT00775931
What this trial is testing

Allogeneic Transplantation For Severe Osteopetrosis

Who this might be right for
Severe Osteopetrosis
Masonic Cancer Center, University of Minnesota 7
Large-scale testing (Phase 3)Study completedNCT01019876
What this trial is testing

Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant Diseases

Who this might be right for
Bone Marrow FailureOsteopetrosisFanconi Anemia+1 more
Columbia University 38
Testing effectiveness (Phase 2)Ended earlyNCT00638820
What this trial is testing

Reduced Intensity AlloTransplant For Osteopetrosis

Who this might be right for
Osteopetrosis
Masonic Cancer Center, University of Minnesota 3
Testing effectiveness (Phase 2)Study completedNCT00730314
What this trial is testing

Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells

Who this might be right for
Sickle Cell DiseaseThalassemiaAnemia+9 more
Children's Hospital Los Angeles 25
Early research (Phase 1)Ended earlyNCT04525352
What this trial is testing

A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis

Who this might be right for
Infantile Malignant Osteopetrosis
Rocket Pharmaceuticals Inc. 1
Testing effectiveness (Phase 2)Active Not RecruitingNCT02171104
What this trial is testing

MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

Who this might be right for
Mucopolysaccharidosis DisordersHurler SyndromeHunter Syndrome+26 more
Masonic Cancer Center, University of Minnesota 149
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Not applicableLooking for participantsNCT04528355
What this trial is testing

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more
Paul Szabolcs 50
Not applicableStudy completedNCT00043329
What this trial is testing

Post Marketing Surveillance Study of Actimmune in Patients With Severe, Malignant Osteopetrosis

Who this might be right for
Osteopetrosis
InterMune 6
Large-scale testing (Phase 3)Study completedNCT00004402
What this trial is testing

Phase III Randomized Study of Interferon Gamma in Children With Severe, Congenital Osteopetrosis

Who this might be right for
Osteopetrosis
FDA Office of Orphan Products Development 30
Not applicableNo Longer AvailableNCT01200017
What this trial is testing

Expanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell Transplant

Who this might be right for
Acute Lymphoblastic LeukemiaAcute Myeloid LeukemiaChronic Myeloid Leukemia+9 more
Christopher Dvorak