Very early researchLooking for participantsNCT06565026What this trial is testingCS-206 in Patients With Sickle Cell DiseaseWho this might be right forSickle Cell Disease CorrectSequence Therapeutics Co., Ltd 5
Not applicableLooking for participantsNCT06539169What this trial is testingFLOWER: Following Longitudinal Outcomes With Epidemiology for Rare DiseasesWho this might be right forAlpha-ThalassemiaBeta-ThalassemiaAmyloidosis+14 more xCures 1,000
Testing effectiveness (Phase 2)Active Not RecruitingNCT03924401What this trial is testingAcute GVHD Suppression Using Costimulation Blockade to Expand Non-malignant TransplantWho this might be right forGraft Versus Host Disease Emory University 30
Testing effectiveness (Phase 2)UnknownNCT02776202What this trial is testingHLA-Identical Sibling Donor Bone Marrow Transplantation for Individuals With Severe Sickle Cell Disease Using a Reduced Intensity Conditioning RegimenWho this might be right forSickle Cell Disease National Guard Health Affairs 15
Not applicableStudy completedNCT02242058What this trial is testingQST-Pupillometry in Sickle Cell Disease PatientsWho this might be right forSCD With Severe Phenotype (HbSS, HbSβ0 Thalassemia, HbSOARab) Julia Finkel 96
Not applicableLooking for participantsNCT07145411What this trial is testingHPC Offered for PRESERVE ExpansionWho this might be right forBone Marrow Transplant (BMT) Ossium Health, Inc. 10
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Very early researchEnded earlyNCT03421756What this trial is testingStem Cell Transplant in Patients With Severe Sickle Cell DiseaseWho this might be right forSickle Cell Disease Kathleen Dorritie 1
Testing effectiveness (Phase 2)Study completedNCT03240731What this trial is testingHLA Haploidentical Bone Marrow Transplant in Patients With Severe Sickle Cell DiseaseWho this might be right forSickle Cell Disease Centre Hospitalier Intercommunal Creteil 25
Testing effectiveness (Phase 2)Looking for participantsNCT03653338What this trial is testingT-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other AnemiasWho this might be right forSickle Cell AnemiaBeta-thalassemia MajorDiamond-blackfan Anemia Paul Szabolcs 5
Not applicableActive Not RecruitingNCT05145062What this trial is testingLong - Term Follow Up of Sickle Cell Disease and Beta-thalassemia Subjects Previously Exposed to BIVV003 or ST-400.Who this might be right forBlood and Lymphatic Diseases Sangamo Therapeutics 8
Testing effectiveness (Phase 2)Looking for participantsNCT03128996What this trial is testingReduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant DisordersWho this might be right forSevere Sickle Cell DiseaseBone Marrow Failure SyndromesMetabolic Disorders+3 more Washington University School of Medicine 29
Large-scale testing (Phase 3)Study completedNCT03745287What this trial is testingA Safety and Efficacy Study Evaluating CTX001 in Subjects With Severe Sickle Cell DiseaseWho this might be right forSickle Cell DiseaseHematological DiseasesHemoglobinopathies Vertex Pharmaceuticals Incorporated 63
Testing effectiveness (Phase 2)UnknownNCT03944447What this trial is testingOutcomes Mandate National Integration With Cannabis as MedicineWho this might be right forChronic PainChronic Pain SyndromeChronic Pain Due to Injury+30 more OMNI Medical Services, LLC 200,000
Testing effectiveness (Phase 2)Study completedNCT03634488What this trial is testingManagement of Severe Acute Malnutrition in SCD, in Northern NigeriaWho this might be right forSickle Cell AnemiaSevere Acute Malnutrition Vanderbilt University Medical Center 132
Early research (Phase 1)Ended earlyNCT04443907What this trial is testingStudy of Safety and Efficacy of Genome-edited Hematopoietic Stem and Progenitor Cells in Sickle Cell Disease (SCD)Who this might be right forSickle Cell Disease Novartis Pharmaceuticals 4
Testing effectiveness (Phase 2)Study completedNCT00745420What this trial is testingEvaluating the Safety and Effectiveness of Bone Marrow Transplants in Children With Sickle Cell Disease (BMT CTN 0601)Who this might be right forSickle Cell Disease Medical College of Wisconsin 30
Large-scale testing (Phase 3)UnknownNCT01511848What this trial is testingStudy Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron OverloadWho this might be right forBeta-thalassemia MajorSickle Cell DiseaseIron Hemosiderosis Ain Shams University 60
Early research (Phase 1)Looking for participantsNCT07015684What this trial is testing131I-apamistamab-based Conditioning for Hematopoietic Stem Cell Transplant (HSCT) in Advanced Sickle Cell Disease (SCD)Who this might be right forSickling Disorder Due to Hemoglobin S Columbia University 24
Testing effectiveness (Phase 2)Active Not RecruitingNCT01966367What this trial is testingCD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell TransplantationWho this might be right forBone Marrow Failure SyndromeSevere Aplastic AnemiaSevere Congenital Neutropenia+13 more Diane George 37