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Results for “Severe Thalassemia”

184 trials

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Showing 20 of 184 results

Large-scale testing (Phase 3)Study completedNCT01125254
What this trial is testing

Amlodipine Use in the Prevention and Treatment of Iron Overload in Patients With Thalassemia Major

Who this might be right for
Thalassemia Major
University of Campinas, Brazil 10
Not applicableUnknownNCT02067130
What this trial is testing

Utility of Fibroscan in Estimating Hepatic Iron Concentration

Who this might be right for
Hereditary Anemias
University of British Columbia 30
Post-approval studies (Phase 4)UnknownNCT01323608
What this trial is testing

The Effect of Vitamin D Supplementation on Calcium Excretion in Thalassemia: a Dose Response Study

Who this might be right for
Thalassemia Major
Weill Medical College of Cornell University 40
Testing effectiveness (Phase 2)Study completedNCT01005576
What this trial is testing

Reduced Intensity Transplant Conditioning Regimen for Severe Thalassemia

Who this might be right for
Severe Thalassemia
Washington University School of Medicine 21
Post-approval studies (Phase 4)UnknownNCT02984475
What this trial is testing

The Potential Hepatoprotective Effect of Metformin in Patients With Beta Thalassemia Major

Who this might be right for
Beta Thalassemia Major Anemia
Cairo University 60
Large-scale testing (Phase 3)Looking for participantsNCT05477563
What this trial is testing

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

Who this might be right for
Beta-ThalassemiaThalassemiaHematologic Diseases+4 more
Vertex Pharmaceuticals Incorporated 26
Large-scale testing (Phase 3)UnknownNCT00999349
What this trial is testing

Therapeutic Effects of Silymarin in Patients With B-thalassemia Major

Who this might be right for
Beta-thalassemia MajorIron Overload
Isfahan University of Medical Sciences 140
Not applicableLooking for participantsNCT06466304
What this trial is testing

Inspiratory Muscle Training in Children With Beta Thalasemia

Who this might be right for
Beta Thalassemia Major
Ahram Canadian University 40
Not applicableStudy completedNCT03161899
What this trial is testing

Evaluation of Nutritional Status in Thalassemia Major Patients in Assiut Children Hospital

Who this might be right for
Thalassemia Major
Assiut University 246
Not applicableStudy completedNCT00658385
What this trial is testing

Assess the Feasibility and Safety of Granulocyte Colony Stimulating Factor (GCSF) Mobilization of CD34+ Hematopoietic Progenitor Cells in Patients With Betathalassemia Major

Who this might be right for
Beta Thalassemia MajorCongenital Anemias
Memorial Sloan Kettering Cancer Center 5
Large-scale testing (Phase 3)UnknownNCT01511848
What this trial is testing

Study Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron Overload

Who this might be right for
Beta-thalassemia MajorSickle Cell DiseaseIron Hemosiderosis
Ain Shams University 60
Large-scale testing (Phase 3)UnknownNCT01016093
What this trial is testing

Zoledronic Acid for the Prevention of Bone Loss Post-bone Marrow Transplantation for Thalassemia Major Patients

Who this might be right for
Beta-ThalassemiaBone Marrow Transplantation
Tehran University of Medical Sciences 50
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Not applicableStudy completedNCT00005893
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders

Who this might be right for
NeutropeniaSickle Cell AnemiaThalassemia Major+1 more
Fairview University Medical Center
Testing effectiveness (Phase 2)Study completedNCT00730314
What this trial is testing

Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells

Who this might be right for
Sickle Cell DiseaseThalassemiaAnemia+9 more
Children's Hospital Los Angeles 25
Testing effectiveness (Phase 2)Looking for participantsNCT03653338
What this trial is testing

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Who this might be right for
Sickle Cell AnemiaBeta-thalassemia MajorDiamond-blackfan Anemia
Paul Szabolcs 5
Large-scale testing (Phase 3)Study completedNCT02065492
What this trial is testing

Amlodipine for Myocardial Iron in Thalassemia

Who this might be right for
Thalassemia
Aga Khan University 20
Not applicableUnknownNCT03101423
What this trial is testing

Monitoring of Chimerism After Transplantation in Patients With β Thalassemia Major and the Treatment Strategies for the Reduction of Chimerism

Who this might be right for
Beta Thalassemia Major
First Affiliated Hospital of Guangxi Medical University 30
Early research (Phase 1)Study completedNCT00744692
What this trial is testing

Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders

Who this might be right for
Non Malignant DisordersImmunodeficienciesCongenital Marrow Failures+5 more
Duke University 22
Not applicableStudy completedNCT02090699
What this trial is testing

MR Imaging of Diffuse Myocardial Fibrosis in Transfusion-Dependent Anemias

Who this might be right for
Thalassemia MajorChronic Blood Transfusion Related Iron Overload
University Health Network, Toronto 42
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