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Results for “Severe Thalassemia”

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Showing 20 of 0 results

Not applicableUnknownNCT03462784
What this trial is testing

Complications in Children With B- Thalassemia Major

Who this might be right for
Beta-thalassemia
Assiut University 201
Very early researchWithdrawnNCT04776850
What this trial is testing

Pre-transplant Immunosuppression and Donor Stem Cell Transplant for the Treatment of Severe Hemoglobinopathies

Who this might be right for
Beta Thalassemia MajorSickle Beta 0 ThalassemiaSickle Beta Plus Thalassemia+3 more
M.D. Anderson Cancer Center
Not applicableTemporarily pausedNCT05442346
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
Thalassemia Major
Bioray Laboratories 5
Not applicableStudy completedNCT04171635
What this trial is testing

Quantitative Susceptibility Mapping (QSM) to Guide Iron Chelating Therapy

Who this might be right for
MRI Scans
Weill Medical College of Cornell University 55
Testing effectiveness (Phase 2)Ended earlyNCT04205435
What this trial is testing

Β-globin Restored Autologous HSC in β-thalassemia Major Patients

Who this might be right for
β-thalassemia Major
Bioray Laboratories 2
Not applicableUnknownNCT06041620
What this trial is testing

Safety and Efficacy Evaluation of Autologous CRISPR-Cas12b Edited Hematopoietic Stem Cells

Who this might be right for
Thalassemia, BetaThalassemia Major
Institute of Hematology & Blood Diseases Hospital, China 2
Post-approval studies (Phase 4)Study completedNCT06606886
What this trial is testing

Effects of Hydroxyurea and Metformin in Transfusion Dependent Beta-Thalassemia

Who this might be right for
Transfusion Dependent Beta-thalassemia
Bahria University 96
Not applicableStudy completedNCT03947632
What this trial is testing

Anthropometric Measurements in Children Having Transfusion-dependent Beta Thalassemia

Who this might be right for
Beta Thalassemia Major
Aga Khan University 367
Testing effectiveness (Phase 2)Study completedNCT01140321
What this trial is testing

Efficacy and Safety of Neridronate (Nerixia®)to Treat Osteoporosis in Patients With TM and TI

Who this might be right for
OsteoporosisThalassemia MajorThalassemia Intermedia
Ente Ospedaliero Ospedali Galliera 120
Testing effectiveness (Phase 2)Study completedNCT00730314
What this trial is testing

Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells

Who this might be right for
Sickle Cell DiseaseThalassemiaAnemia+9 more
Children's Hospital Los Angeles 25
Testing effectiveness (Phase 2)Looking for participantsNCT03653338
What this trial is testing

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Who this might be right for
Sickle Cell AnemiaBeta-thalassemia MajorDiamond-blackfan Anemia
Paul Szabolcs 5
Not applicableStudy completedNCT03948737
What this trial is testing

The Effect of Alpha-tocopherol in Hemolysis and Oxidative Stress Marker on the Red Cell Membrane Beta-thalassemia Major

Who this might be right for
Beta Thalassemia Major AnemiaHemolysisOxidative Stress
Universitas Indonesia 40
Large-scale testing (Phase 3)Study completedNCT01125254
What this trial is testing

Amlodipine Use in the Prevention and Treatment of Iron Overload in Patients With Thalassemia Major

Who this might be right for
Thalassemia Major
University of Campinas, Brazil 10
Large-scale testing (Phase 3)UnknownNCT01511848
What this trial is testing

Study Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron Overload

Who this might be right for
Beta-thalassemia MajorSickle Cell DiseaseIron Hemosiderosis
Ain Shams University 60
Testing effectiveness (Phase 2)Study completedNCT02151526
What this trial is testing

A Study Evaluating the Safety and Efficacy of LentiGlobin BB305 Drug Product in β-Thalassemia Major (Also Referred to as Transfusion-dependent β-Thalassemia [TDT]) and Sickle Cell Disease

Who this might be right for
Beta-Thalassemia MajorSickle Cell Disease
Genetix Biotherapeutics Inc. 7
Not applicableStudy completedNCT03311243
What this trial is testing

Periodontal Therapy in Thalassemia Major Patients

Who this might be right for
Thalassemia MajorChronic Periodontitis
King Saud University 52
Testing effectiveness (Phase 2)Ended earlyNCT01000155
What this trial is testing

Efficacy of Vorinostat to Induce Fetal Hemoglobin in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseSickle Cell Anemia
Dana-Farber Cancer Institute 5
Testing effectiveness (Phase 2)Study completedNCT00005934
What this trial is testing

5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia

Who this might be right for
Beta Thalassemia
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 24
Very early researchLooking for participantsNCT05745532
What this trial is testing

Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients

Who this might be right for
β-thalassemia
Shenzhen Hemogen 10
Not applicableStudy completedNCT02674607
What this trial is testing

The Potential Immunomodulatory Effects of Spirulina on Thalassemic Children

Who this might be right for
Beta Thalassemia Major
Tanta University 60
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