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Results for “Severe Thalassemia”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Looking for participantsNCT06490627
What this trial is testing

Unraveling the Impact of Thalidomide at Diverse Doses in Transfusion Dependent Beta Thalassemia

Who this might be right for
Fetal HemoglobinThalassemia MajorGenetic Disease
National Institute of Blood and Marrow Transplant (NIBMT), Pakistan 54
Early research (Phase 1)Looking for participantsNCT06465550
What this trial is testing

Gene-modified Autologous Hematopoietic Stem Cell (BD211) Treating β-thalassemia Major

Who this might be right for
β-thalassemia
Shanghai BDgene Co., Ltd. 9
Not applicableNot Yet RecruitingNCT07509996
What this trial is testing

Risk Factors Affecting Growth in Thalassemic Children at AUCH

Who this might be right for
Thalassemia Majors (Beta-Thalassemia Major)
Assiut University 85
Not applicableStudy completedNCT00972231
What this trial is testing

Iron Overload and Growth Velocity in Thalassemia and Sickle Cell Anemia

Who this might be right for
ThalassemiaSickle Cell Disease
HaEmek Medical Center, Israel 93
Testing effectiveness (Phase 2)Active Not RecruitingNCT05444894
What this trial is testing

EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)

Who this might be right for
Transfusion Dependent Beta ThalassemiaHemoglobinopathiesThalassemia Major+1 more
Editas Medicine, Inc. 9
Testing effectiveness (Phase 2)Ended earlyNCT00040469
What this trial is testing

Bone Marrow Transplant From Related Donor for Patients With High Risk Hemoglobinopathies

Who this might be right for
Sickle Cell AnemiaHemoglobinopathyThalassemia
Baylor College of Medicine 15
Testing effectiveness (Phase 2)Ended earlyNCT01459718
What this trial is testing

Safety and Efficacy of Deferasirox in Combination With Desferoxamine in β-thalassaemia Patients With Severe Cardiac Iron Overload

Who this might be right for
Transfusion-dependent β-thalassemia PatientsCardiac Iron Overload
Novartis Pharmaceuticals 32
Not applicableNot Yet RecruitingNCT07204015
What this trial is testing

Body Composition in Pediatric Patients With Thalassemia Major

Who this might be right for
Body Composition in Thalassemia Major
Assiut University 115
Testing effectiveness (Phase 2)Study completedNCT01740713
What this trial is testing

Pharmacokinetic Study of Deferiprone in Paediatric Patients

Who this might be right for
Chronic Iron Overload
Consorzio per Valutazioni Biologiche e Farmacologiche 23
Very early researchStudy completedNCT06065189
What this trial is testing

Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major

Who this might be right for
Beta-Thalassemia
Children's Hospital of Fudan University 2
Testing effectiveness (Phase 2)WithdrawnNCT02038478
What this trial is testing

Allograft for Sickle Cell Disease and Thalassemia

Who this might be right for
Sickle Cell Disease and Thalassemia
University of Texas Southwestern Medical Center
Post-approval studies (Phase 4)Study completedNCT03095326
What this trial is testing

Pneumococcal Vaccination for Splenectomised Thalassemia Major Patients in Indonesia

Who this might be right for
ThalassemiaPneumococcal Infection
Fakultas Kedokteran Universitas Indonesia 56
Testing effectiveness (Phase 2)Study completedNCT02559648
What this trial is testing

Denosumab vs Placebo in Patients With Thalassemia Major and Osteoporosis

Who this might be right for
Thalassemia MajorOsteoporosis
Ersi Voskaridou 63
Not applicableStudy completedNCT00456690
What this trial is testing

Endocrine and Nutritional Assessment in B Thalassemia Major

Who this might be right for
Thalassemia
HaEmek Medical Center, Israel 133
Post-approval studies (Phase 4)Study completedNCT04009525
What this trial is testing

Hematopoietic Stem Cell Transplantation for Patients With Thalassemia Major: A Multicenter, Prospective Clinical Study

Who this might be right for
Thalassemia Major
First Affiliated Hospital of Guangxi Medical University 823
Not applicableStudy completedNCT02904252
What this trial is testing

The Prevalence and Severity of HCV Infection in Thalassemia Major and Thalassemia Intermedia in Siriraj Hospital

Who this might be right for
Hepatitis CFibrosisThalassemia
Mahidol University 158
Not applicableStudy completedNCT07153926
What this trial is testing

Elastography vs Iron Regulators in the Diagnosis of Hepatic Fibrosis- Iron Overload in Children With Beta- Thalassemia

Who this might be right for
Liver FibrosisBeta Thalassemia Major
Tanta University 100
Testing effectiveness (Phase 2)Study completedNCT01005576
What this trial is testing

Reduced Intensity Transplant Conditioning Regimen for Severe Thalassemia

Who this might be right for
Severe Thalassemia
Washington University School of Medicine 21
Not applicableStudy completedNCT04211480
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
β Thalassemia Major
Bioray Laboratories 6
Large-scale testing (Phase 3)Study completedNCT01740531
What this trial is testing

Study to Evaluate Efficacy and Safety of S303 Treated Red Blood Cells (RBCs)in Subjects With Thalassemia Major Requiring Chronic RBC Transfusion

Who this might be right for
Thalassemia Major
Cerus Corporation 86
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