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Results for “Sickle B+ Thalassemia”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Ended earlyNCT03333486
What this trial is testing

Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer

Who this might be right for
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 PositiveAcute Leukemia in RemissionAcute Lymphoblastic Leukemia+34 more
Roswell Park Cancer Institute 31
Testing effectiveness (Phase 2)Active Not RecruitingNCT00061568
What this trial is testing

Improving the Results of Bone Marrow Transplantation for Patients With Severe Congenital Anemias

Who this might be right for
Congenital Hemolytic AnemiaSickle Cell Disease
National Heart, Lung, and Blood Institute (NHLBI) 130
Not applicableEnded earlyNCT02179359
What this trial is testing

Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more
Masonic Cancer Center, University of Minnesota 38
Testing effectiveness (Phase 2)UnknownNCT00408447
What this trial is testing

Stem Cell Transplant in Sickle Cell Disease and Thalassemia

Who this might be right for
Sickle Cell DiseaseBeta Thalassemia
Columbia University 53
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Testing effectiveness (Phase 2)Ended earlyNCT00034528
What this trial is testing

Stem Cell Transplantation After Reduced-Dose Chemotherapy for Patients With Sickle Cell Disease or Thalassemia

Who this might be right for
HemoglobinopathiesAnemia, Sickle CellHemoglobin SC Disease+2 more
National Institute of Allergy and Infectious Diseases (NIAID) 2
Early research (Phase 1)Ended earlyNCT07431398
What this trial is testing

Single-dose Pharmacokinetics of Pociredir in Participants With Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
Fulcrum Therapeutics 13
Not applicableStudy completedNCT06831799
What this trial is testing

ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19

Who this might be right for
HemoglobinopathiesSickle Cell DiseaseSickle Cell Anemia+21 more
Hospital Universitari Vall d'Hebron Research Institute 684
Not applicableUnknownNCT05635266
What this trial is testing

Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives

Who this might be right for
Age-Related Macular DegenerationAllergiesAlpha-Gal Syndrome+44 more
Sanguine Biosciences 20,000
Testing effectiveness (Phase 2)Study completedNCT00004412
What this trial is testing

Phase II Randomized Trial:Arginine Butyrate Plus Standard Local Therapy in Patients With Refractory Sickle Cell Ulcers

Who this might be right for
Skin UlcersSickle Cell Anemia
Susan P. Perrine 23
Not applicableLooking for participantsNCT05799118
What this trial is testing

Study of the Role of Genetic Modifiers in Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseThalassemia, BetaThalassemia Alpha+1 more
Cyprus Institute of Neurology and Genetics 30,000
Testing effectiveness (Phase 2)Active Not RecruitingNCT00977691
What this trial is testing

Haploidentical PBMC Transplant for Severe Congenital Anemias

Who this might be right for
Sickle Cell Anemia
National Heart, Lung, and Blood Institute (NHLBI) 23
Early research (Phase 1)UnknownNCT02380079
What this trial is testing

Dose-Escalation Study of SCD-101 in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseSickle-Beta Zero Thalassemia
Invenux, LLC 60
Not applicableStudy completedNCT05687474
What this trial is testing

Baby Detect : Genomic Newborn Screening

Who this might be right for
Congenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more
Centre Hospitalier Universitaire de Liege 6,824
Not applicableStudy completedNCT05506358
What this trial is testing

Evaluation of Low-cost Techniques for Detecting Sickle Cell Disease and β-thalassemia in Nepal and Canada

Who this might be right for
Sickle Cell DiseaseSickle Cell TraitBeta-Thalassemia+2 more
University of British Columbia 145
Not applicableStudy completedNCT00005893
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders

Who this might be right for
NeutropeniaSickle Cell AnemiaThalassemia Major+1 more
Fairview University Medical Center
Not applicableActive Not RecruitingNCT03655223
What this trial is testing

Early Check: Expanded Screening in Newborns

Who this might be right for
Spinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more
RTI International 30,000
Large-scale testing (Phase 3)UnknownNCT01511848
What this trial is testing

Study Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron Overload

Who this might be right for
Beta-thalassemia MajorSickle Cell DiseaseIron Hemosiderosis
Ain Shams University 60
Testing effectiveness (Phase 2)Looking for participantsNCT03653338
What this trial is testing

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Who this might be right for
Sickle Cell AnemiaBeta-thalassemia MajorDiamond-blackfan Anemia
Paul Szabolcs 5
Not applicableStudy completedNCT02326597
What this trial is testing

Decision Aid for Therapeutic Options In Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseSickle Cell AnemiaHemoglobin SS+2 more
Emory University 134
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