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Results for “Sickle Cell Thalassemia”

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Showing 20 of 0 results

Not applicableStudy completedNCT00480974
What this trial is testing

Long Term Follow up in Sickle Cell Patients Treated by Hydroxyurea

Who this might be right for
Sickle Cell AnemiaSickle Cell Thalassemia
HaEmek Medical Center, Israel 20
Not applicableStudy completedNCT03609814
What this trial is testing

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmunodeficiencies+5 more
University of California, San Francisco 30
Testing effectiveness (Phase 2)UnknownNCT00408447
What this trial is testing

Stem Cell Transplant in Sickle Cell Disease and Thalassemia

Who this might be right for
Sickle Cell DiseaseBeta Thalassemia
Columbia University 53
Testing effectiveness (Phase 2)Active Not RecruitingNCT04053803
What this trial is testing

An Extension Study of IMR-687 in Adult Patients With Sickle Cell Anemia

Who this might be right for
Sickle Cell Disease
Imara, Inc. 30
Not applicableStudy completedNCT00736060
What this trial is testing

Clinical and Laboratory Characteristics of Sickle Cell Anemia Patients Admitted With Fever

Who this might be right for
Sickle Cell AnemiaSickle Cell Thalassemia
HaEmek Medical Center, Israel 60
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Testing effectiveness (Phase 2)Ended earlyNCT00034528
What this trial is testing

Stem Cell Transplantation After Reduced-Dose Chemotherapy for Patients With Sickle Cell Disease or Thalassemia

Who this might be right for
HemoglobinopathiesAnemia, Sickle CellHemoglobin SC Disease+2 more
National Institute of Allergy and Infectious Diseases (NIAID) 2
Not applicableLooking for participantsNCT07206095
What this trial is testing

Integrative Diagnosis for SCD and Other RADs

Who this might be right for
Sickle Cell DiseaseThalassaemiaCongenital Dyserythropoietic Anemia (CDA)+6 more
Hospital Universitari Vall d'Hebron Research Institute 200
Early research (Phase 1)Ended earlyNCT07431398
What this trial is testing

Single-dose Pharmacokinetics of Pociredir in Participants With Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
Fulcrum Therapeutics 13
Early research (Phase 1)Study completedNCT02165007
What this trial is testing

Haploidentical Hematopoietic Stem Cell Transplantation

Who this might be right for
Sickle Cell-thalassemia DiseaseThalassemia
Catherine Bollard 7
Not applicableStudy completedNCT06831799
What this trial is testing

ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19

Who this might be right for
HemoglobinopathiesSickle Cell DiseaseSickle Cell Anemia+21 more
Hospital Universitari Vall d'Hebron Research Institute 684
Testing effectiveness (Phase 2)UnknownNCT01202812
What this trial is testing

Trial of LOVAZA in Pediatric Sickle Cell Disease (SCD)

Who this might be right for
Sickle Cell DiseaseHEMOGLOBIN SSHemoglobin S Beta-0 Thalassemia+2 more
Thomas Jefferson University 48
Not applicableUnknownNCT05635266
What this trial is testing

Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives

Who this might be right for
Age-Related Macular DegenerationAllergiesAlpha-Gal Syndrome+44 more
Sanguine Biosciences 20,000
Testing effectiveness (Phase 2)Study completedNCT00004412
What this trial is testing

Phase II Randomized Trial:Arginine Butyrate Plus Standard Local Therapy in Patients With Refractory Sickle Cell Ulcers

Who this might be right for
Skin UlcersSickle Cell Anemia
Susan P. Perrine 23
Not applicableLooking for participantsNCT05799118
What this trial is testing

Study of the Role of Genetic Modifiers in Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseThalassemia, BetaThalassemia Alpha+1 more
Cyprus Institute of Neurology and Genetics 30,000
Not applicableStudy completedNCT02239016
What this trial is testing

Screening Patients With Sickle Cell Disease for Kidney Damage

Who this might be right for
Sickle Cell Disease
Children's Hospital Medical Center, Cincinnati 320
Testing effectiveness (Phase 2)Active Not RecruitingNCT00977691
What this trial is testing

Haploidentical PBMC Transplant for Severe Congenital Anemias

Who this might be right for
Sickle Cell Anemia
National Heart, Lung, and Blood Institute (NHLBI) 23
Early research (Phase 1)UnknownNCT02380079
What this trial is testing

Dose-Escalation Study of SCD-101 in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseSickle-Beta Zero Thalassemia
Invenux, LLC 60
Not applicableStudy completedNCT05687474
What this trial is testing

Baby Detect : Genomic Newborn Screening

Who this might be right for
Congenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more
Centre Hospitalier Universitaire de Liege 6,824
Not applicableStudy completedNCT05506358
What this trial is testing

Evaluation of Low-cost Techniques for Detecting Sickle Cell Disease and β-thalassemia in Nepal and Canada

Who this might be right for
Sickle Cell DiseaseSickle Cell TraitBeta-Thalassemia+2 more
University of British Columbia 145
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