Not applicableStudy completedNCT04419233What this trial is testingNon-Interventional, Postmarketing Surveillance Study of Nusinersen Sodium InjectionWho this might be right forMuscular Atrophy, Spinal Biogen 50
Not applicableStudy completedNCT01611610What this trial is testingClinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)Who this might be right forSpinal Muscular Atrophy Institut de Myologie, France 4
Not applicableActive Not RecruitingNCT07796776What this trial is testingThe Aim of the Study is to Characterize Patients Exhibiting Muscular Atrophy and Weakness Who Require a Muscle Biopsy for Diagnosis (IBM vs Atypical MND), Through an Innovative Technique Which Enables the Evaluation of the Neuromuscular Junction Involvement in Each ConditionWho this might be right forInclusion Body Myositis (IBM)Motor Neuron Disease, Amyotrophic Lateral Sclerosis IRCCS San Raffaele 30
Testing effectiveness (Phase 2)Looking for participantsNCT07336446What this trial is testingA Trial to Learn How Safe AZD9750 is and How Well it Works in People With Metastatic Prostate Cancer When Given With or Without Other Anticancer DrugsWho this might be right forProstate Cancer AstraZeneca 300
Not applicableUnknownNCT05589987What this trial is testingSpinal Muscular Atrophy on Wheels, Using Power MobilityWho this might be right forSpinal Muscular Atrophy University of Castilla-La Mancha 20
Testing effectiveness (Phase 2)Study completedNCT05808764What this trial is testingInvestigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular AtrophyWho this might be right forMuscular Atrophy, Spinal Hoffmann-La Roche 11
Not applicableLooking for participantsNCT07286565What this trial is testingActive NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn ScreeningWho this might be right forSpinal Muscular Atrophy (SMA)Duchenne Muscular Dystrophy (DMD) Centre Hospitalier Universitaire de Liege 100
Large-scale testing (Phase 3)Study completedNCT02801071What this trial is testingL-Citrulline in Patients With Post-Polio SyndromeWho this might be right forPost-Polio Syndrome Dirk Fischer 30
Not applicableNo Longer AvailableNCT06877689What this trial is testingEAP of Apitegromab for Patients With Spinal Muscular AtrophyWho this might be right forSMA Scholar Rock, Inc.
Not applicableStudy completedNCT01522079What this trial is testingSpinal Muscular Atrophy and Cardiac Autonomic FunctionWho this might be right forSpinal Muscular Atrophy Centro Universitário Augusto Motta 9
Testing effectiveness (Phase 2)Looking for participantsNCT05824169What this trial is testingEvaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 PatientsWho this might be right forSpinal Muscular Atrophy GeneCradle Inc 18
Not applicableUnknownNCT05272969What this trial is testingPompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe DiseaseWho this might be right forPompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more LMU Klinikum 95
Not applicableStudy completedNCT04387864What this trial is testingWhole Body Vibration on Muscle Strength in Patients With Postpolio SyndromeWho this might be right forPostpolio Syndrome Koç University 14
Not applicableStudy completedNCT05341453What this trial is testingEquine-Assisted Physiotherapy for Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Charles University, Czech Republic 21
Early research (Phase 1)Study completedNCT00374075What this trial is testingStudy of Safety and Dosing Effect on SMN Levels of Valproic Acid (VPA) in Patients With Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy University of Utah 42
Testing effectiveness (Phase 2)Study completedNCT05694819What this trial is testingDarolutamide in Patients With Androgen Receptor-Positive Salivary Gland Carcinoma (DISCOVARY)Who this might be right forSalivary Gland Cancer National Cancer Center Hospital East 57
Testing effectiveness (Phase 2)Study completedNCT02941328What this trial is testingSPACE Trial: Pyridostigmine vs Placebo in SMA Types 2, 3 and 4Who this might be right forSpinal Muscular AtrophySMAKugelberg-Welander Disease UMC Utrecht 39
Not applicableLooking for participantsNCT06019637What this trial is testingA Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With ZolgensmaWho this might be right forSpinal Muscular Atrophies Novartis Pharmaceuticals 50
Not applicableEnrolling By InvitationNCT06772402What this trial is testingGCB-001 in Treatment of Patients With Type II (SMA) Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Type 2 Genecombio Ltd. 6
Not applicableLooking for participantsNCT07488338What this trial is testingHABIT-ILE + FST in Children With SMA: Preliminary EffectivenessWho this might be right forSpinal Muscular Atrophy (SMA) Teachers College, Columbia University 20