Large-scale testing (Phase 3)Active Not RecruitingNCT04042025
What this trial is testing
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more
Novartis Gene Therapies 85