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Results for “Spinal Muscular Atrophy 1”

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Showing 20 of 0 results

Not applicableStudy completedNCT05715749
What this trial is testing

Body Weight Support Harness System in Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type II
Nationwide Children's Hospital 33
Not applicableUnknownNCT02831296
What this trial is testing

Prospective Evaluation of Infants With Spinal Muscular Atrophy:

Who this might be right for
Spinal Muscular Atrophy
Massachusetts General Hospital 1,000
Not applicableStudy completedNCT01862042
What this trial is testing

Palliative Care in Spinal Muscular Atrophy (SMA) 1

Who this might be right for
Spinal Muscular Atrophy 1
Assistance Publique - Hôpitaux de Paris 39
Early research (Phase 1)Study completedNCT02122952
What this trial is testing

Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1

Who this might be right for
Spinal Muscular Atrophy 1
Novartis Gene Therapies 15
Not applicableStudy completedNCT00466349
What this trial is testing

International SMA Patient Registry

Who this might be right for
Muscular Atrophy, Spinal
Indiana University 3,000
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Testing effectiveness (Phase 2)Looking for participantsNCT07554924
What this trial is testing

A Phase I/II Clinical Study to Evaluate SKG0201 Injection in Subjects With Spinal Muscular Atrophy Type I

Who this might be right for
Spinal Muscular Atrophy 1
Lanyue Biotech (Hangzhou) Co., Ltd. 11
Not applicableStudy completedNCT01059240
What this trial is testing

SMN Copy Number Distribution in Mali, West Africa

Who this might be right for
Spinal Muscular Atrophy
National Institute of Neurological Disorders and Stroke (NINDS) 701
Testing effectiveness (Phase 2)Looking for participantsNCT07070999
What this trial is testing

Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1

Who this might be right for
Spinal Muscular Atrophy Type I
Gemma Biotherapeutics 22
Not applicableUnknownNCT06194539
What this trial is testing

Assessing the Fertility Status of Men With Spinal Muscular Atrophy (SMA)

Who this might be right for
Fertility Issues
Bar-Chama, Natan, M.D. 75
Not applicableLooking for participantsNCT06152302
What this trial is testing

Test of Aquatic Mobility of SMA Infants

Who this might be right for
Infantile Spinal Muscular Atrophy
Assistance Publique - Hôpitaux de Paris 15
Early research (Phase 1)Study completedNCT02162836
What this trial is testing

A Safety Study of JNJ-56021927 in Participants With Metastatic Castration-Resistant Prostate Cancer

Who this might be right for
Prostatic Neoplasms, Castration-Resistant
Janssen Pharmaceutical K.K. 6
Testing effectiveness (Phase 2)Ended earlyNCT00439218
What this trial is testing

Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I

Who this might be right for
Spinal Muscular Atrophy Type I
Westat 5
Testing effectiveness (Phase 2)Study completedNCT02268552
What this trial is testing

An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)

Who this might be right for
Spinal Muscular Atrophy
Novartis Pharmaceuticals 40
Not applicableApproved For MarketingNCT04256265
What this trial is testing

An Expanded Access Program for Risdiplam in Participants With Spinal Muscular Atrophy (SMA)

Who this might be right for
Muscular Atrophy, Spinal
Genentech, Inc.
Not applicableLooking for participantsNCT07136844
What this trial is testing

Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology

Who this might be right for
Neuromuscular DiseasesObesity (Disorder)Myotonic Dystrophy 1+9 more
Centre Hospitalier Universitaire de Liege 300
Not applicableStudy completedNCT04193228
What this trial is testing

Muscle Structure, Function and Gait in dHMN

Who this might be right for
Distal Hereditary Motor Neuropathy, Type IIDistal Hereditary Motor Neuropathy, Type VDistal Hereditary Motor Neuronopathy Type I+1 more
University College London Hospitals 11
Not applicableStudy completedNCT00756821
What this trial is testing

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
Carelon Research 130
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025
What this trial is testing

Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more
Novartis Gene Therapies 85
Not applicableActive Not RecruitingNCT03655223
What this trial is testing

Early Check: Expanded Screening in Newborns

Who this might be right for
Spinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more
RTI International 30,000
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