Not applicableStudy completedNCT02003937What this trial is testingAerobic Training in Patients With Spinal Muscular Atrophy Type IIIWho this might be right forSpinal Muscular Atrophy Rigshospitalet, Denmark 15
Not applicableActive Not RecruitingNCT04690998What this trial is testingOutcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV PatientsWho this might be right forSpinal Muscular Atrophy Assistance Publique Hopitaux De Marseille 104
Large-scale testing (Phase 3)Study completedNCT03306277What this trial is testingGene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1Who this might be right forSMA - Spinal Muscular AtrophyGene Therapy Novartis Gene Therapies 22
Not applicableEnded earlyNCT03056144What this trial is testingWhole Body Vibration Therapy in Children With Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Type 3 The Hong Kong Polytechnic University 1
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025What this trial is testingLong-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioiWho this might be right forSpinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more Novartis Gene Therapies 85
Not applicableActive Not RecruitingNCT03709784What this trial is testingSpinraza in Adult Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type 3 Washington University School of Medicine 148
Testing effectiveness (Phase 2)Active Not RecruitingNCT05794139What this trial is testingSafety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy NMD Pharma A/S 54
Not applicableUnknownNCT05272969What this trial is testingPompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe DiseaseWho this might be right forPompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more LMU Klinikum 95
Not applicableUnknownNCT02831296What this trial is testingProspective Evaluation of Infants With Spinal Muscular Atrophy:Who this might be right forSpinal Muscular Atrophy Massachusetts General Hospital 1,000
Testing effectiveness (Phase 2)Looking for participantsNCT07047144What this trial is testingEvaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySMASpinal Muscular Atrophy Type 2+3 more Scholar Rock, Inc. 52
Not applicableUnknownNCT03300869What this trial is testingNatural History of Types 2 and 3 SMA in TaiwanWho this might be right forSpinal Muscular Atrophy Kaohsiung Medical University Chung-Ho Memorial Hospital 300
Testing effectiveness (Phase 2)Study completedNCT03781479What this trial is testingControlled Trial to Evaluate Amifampridine Phosphate in Spinal Muscular Atrophy Type 3 PatientsWho this might be right forMuscular Atrophy, Spinal Catalyst Pharmaceuticals, Inc. 13
Not applicableUnknownNCT05839145What this trial is testingHome Monitoring of Adult Patients With SMA: a Pilot Multicenter Validation StudyWho this might be right forMuscular Atrophy, Spinal, Type IIMuscular Atrophy, Spinal, Type III Institut de Myologie, France 60
Not applicableUnknownNCT05544994What this trial is testingThe Effect of Aerobic Exercise Training in Patients With Type III Spinal Muscular AtrophyWho this might be right forNeuromuscular DiseasesSpinal Muscular Atrophy Type 3 Istanbul Medipol University Hospital 20
Testing effectiveness (Phase 2)Study completedNCT03921528What this trial is testingAn Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+6 more Scholar Rock, Inc. 58
Not applicableStudy completedNCT02895789What this trial is testingOxidative Capacity and Exercise Tolerance in Ambulatory SMAWho this might be right forSpinal Muscular Atrophy Type 3Mitochondrial Myopathy Columbia University 42
Testing effectiveness (Phase 2)Study completedNCT00227266What this trial is testingValproic Acid and Carnitine in Patients With Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy University of Utah 94
Not applicableStudy completedNCT00756821What this trial is testingA Pilot Study of Biomarkers for Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Carelon Research 130
Not applicableActive Not RecruitingNCT04888702What this trial is testingHolter of Movement in Patients with SMA Undergoing Treatment.Who this might be right forSpinal Muscular Atrophy Centre Hospitalier Universitaire de Liege 30
Not applicableLooking for participantsNCT06839469What this trial is testingEstablishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular DisordersWho this might be right forSpinal Muscular Atrophy Type 3Duchenne Muscular Dystrophy (DMD) Columbia University 106