Testing effectiveness (Phase 2)Active Not RecruitingNCT07222371
What this trial is testing
An Open-label, Single Center, Single Participant Study of an Experimental Antisense Oligonucleotide Treatment for TUBB4A-related Leukodystrophy
Who this might be right for
Genetic DiseaseTUBB4A-Related Leukodystrophy
University of California, San Diego 1