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Results for “Type 2 Spinal Muscular Atrophy”

61 trials

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Showing 20 of 61 results

Not applicableUnknownNCT05272969
What this trial is testing

Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more
LMU Klinikum 95
Not applicableUnknownNCT03300869
What this trial is testing

Natural History of Types 2 and 3 SMA in Taiwan

Who this might be right for
Spinal Muscular Atrophy
Kaohsiung Medical University Chung-Ho Memorial Hospital 300
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Not applicableEnrolling By InvitationNCT07072676
What this trial is testing

The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.

Who this might be right for
Inclusion Body MyositisMyotonic Dystrophy 1Myotonic Dystrophy 2+10 more
LMU Klinikum 30
Not applicableStudy completedNCT01611610
What this trial is testing

Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)

Who this might be right for
Spinal Muscular Atrophy
Institut de Myologie, France 4
Testing effectiveness (Phase 2)Study completedNCT00227266
What this trial is testing

Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
University of Utah 94
Testing effectiveness (Phase 2)Study completedNCT00568802
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 27
Large-scale testing (Phase 3)Study completedNCT05156320
What this trial is testing

Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+7 more
Scholar Rock, Inc. 188
Not applicableStudy completedNCT04576494
What this trial is testing

Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms)

Who this might be right for
Spinal Muscular Atrophy
CHU de Reims 4
Not applicableLooking for participantsNCT01793168
What this trial is testing

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Who this might be right for
Rare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more
Sanford Health 20,000
Not applicableActive Not RecruitingNCT04159987
What this trial is testing

Monitoring to the Evolution of Motor Function in SMA Type II Adults Patients Treated With SPINRAZA®

Who this might be right for
Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Nice 20
Large-scale testing (Phase 3)Study completedNCT03837184
What this trial is testing

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

Who this might be right for
Spinal Muscular Atrophy Type I
Novartis Gene Therapies 2
Not applicableStudy completedNCT00756821
What this trial is testing

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
Carelon Research 130
Not applicableStudy completedNCT04193228
What this trial is testing

Muscle Structure, Function and Gait in dHMN

Who this might be right for
Distal Hereditary Motor Neuropathy, Type IIDistal Hereditary Motor Neuropathy, Type VDistal Hereditary Motor Neuronopathy Type I+1 more
University College London Hospitals 11
Not applicableUnknownNCT04888702
What this trial is testing

Holter of Movement in Patients with SMA Undergoing Treatment.

Who this might be right for
Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Liege 30
Testing effectiveness (Phase 2)Study completedNCT02908685
What this trial is testing

Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants

Who this might be right for
Muscular Atrophy, Spinal
Hoffmann-La Roche 231
Testing effectiveness (Phase 2)Study completedNCT03921528
What this trial is testing

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+6 more
Scholar Rock, Inc. 58
Not applicableStudy completedNCT03395795
What this trial is testing

Trial Evaluating the Interest of Noninvasive Ventilation in NAVA Mode in Respiratory Decompensations Children With Infantile Spinal Muscular Atrophy Type II

Who this might be right for
Infantile Spinal Muscular Atrophy
Assistance Publique - Hôpitaux de Paris 1
Testing effectiveness (Phase 2)Looking for participantsNCT07047144
What this trial is testing

Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySMASpinal Muscular Atrophy Type 2+3 more
Scholar Rock, Inc. 52
Testing effectiveness (Phase 2)Active Not RecruitingNCT05901987
What this trial is testing

Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients

Who this might be right for
SMA II
GeneCradle Inc 33
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