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Results for “Type 3 Spinal Muscular Atrophy”

49 trials

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Showing 20 of 49 results

Not applicableUnknownNCT05272969
What this trial is testing

Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more
LMU Klinikum 95
Not applicableUnknownNCT03300869
What this trial is testing

Natural History of Types 2 and 3 SMA in Taiwan

Who this might be right for
Spinal Muscular Atrophy
Kaohsiung Medical University Chung-Ho Memorial Hospital 300
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Testing effectiveness (Phase 2)Study completedNCT00227266
What this trial is testing

Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
University of Utah 94
Testing effectiveness (Phase 2)Study completedNCT00568802
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 27
Testing effectiveness (Phase 2)Looking for participantsNCT06421831
What this trial is testing

Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients

Who this might be right for
Spinal Muscular Atrophy Type 3
GeneCradle Inc 21
Testing effectiveness (Phase 2)Ended earlyNCT03819660
What this trial is testing

Long Term Safety of Amifampridine Phosphate in Spinal Muscular Atrophy 3

Who this might be right for
Spinal Muscular Atrophy Type 3
Catalyst Pharmaceuticals, Inc. 13
Large-scale testing (Phase 3)Study completedNCT05156320
What this trial is testing

Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+7 more
Scholar Rock, Inc. 188
Not applicableStudy completedNCT04576494
What this trial is testing

Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms)

Who this might be right for
Spinal Muscular Atrophy
CHU de Reims 4
Not applicableLooking for participantsNCT01793168
What this trial is testing

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Who this might be right for
Rare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more
Sanford Health 20,000
Large-scale testing (Phase 3)Study completedNCT03837184
What this trial is testing

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

Who this might be right for
Spinal Muscular Atrophy Type I
Novartis Gene Therapies 2
Not applicableStudy completedNCT00756821
What this trial is testing

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
Carelon Research 130
Not applicableUnknownNCT04888702
What this trial is testing

Holter of Movement in Patients with SMA Undergoing Treatment.

Who this might be right for
Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Liege 30
Testing effectiveness (Phase 2)Study completedNCT02908685
What this trial is testing

Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants

Who this might be right for
Muscular Atrophy, Spinal
Hoffmann-La Roche 231
Not applicableLooking for participantsNCT07400198
What this trial is testing

Gait and Bone Health in SMA

Who this might be right for
Spinal Muscular Atrophy Type 3Ambulatory Spinal Muscular Atrophy
Jacqueline Montes 22
Testing effectiveness (Phase 2)Study completedNCT03921528
What this trial is testing

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+6 more
Scholar Rock, Inc. 58
Testing effectiveness (Phase 2)Looking for participantsNCT07047144
What this trial is testing

Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySMASpinal Muscular Atrophy Type 2+3 more
Scholar Rock, Inc. 52
Not applicableActive Not RecruitingNCT06300996
What this trial is testing

Spinal Cord Stimulation for the Treatment of Motor Deficits in People With Spinal Muscular Atrophy - Upper Limb

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type II+2 more
Marco Capogrosso 3
Testing effectiveness (Phase 2)Study completedNCT05794139
What this trial is testing

Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
NMD Pharma A/S 52
Not applicableUnknownNCT06137612
What this trial is testing

Spinal Cord Gray Matter Imaging in Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type IIISpinal Muscular Atrophy Type II
University Hospital, Basel, Switzerland 52
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