Not applicableStudy completedNCT00351156What this trial is testingStudy to Evaluate Blood Cell Lines From Patients With Gaucher DiseaseWho this might be right forGaucher Disease Amicus Therapeutics 50
Large-scale testing (Phase 3)Study completedNCT01074944What this trial is testingEliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease to Evaluate Once Daily Versus Twice Daily Dosing (EDGE)Who this might be right forGaucher Disease Genzyme, a Sanofi Company 170
Early research (Phase 1)Looking for participantsNCT03721068What this trial is testingStudy of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory OsteosarcomaWho this might be right forNeuroblastomaOsteosarcoma UNC Lineberger Comprehensive Cancer Center 18
Not applicableUnknownNCT04055831What this trial is testingImmune Biomarkers Related to Bone Pathology in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Type 1 Lysosomal and Rare Disorders Research and Treatment Center, Inc. 40
Not applicableLooking for participantsNCT05253560What this trial is testingProdromal Parkinsonian Features in GBA1 Mutation CarriersWho this might be right forGaucher Disease, Type 1Healthy Shaare Zedek Medical Center 600
Testing effectiveness (Phase 2)Temporarily pausedNCT01463215What this trial is testingClinical Trial of Ambroxol in Patients With Type I Gaucher DiseaseWho this might be right forType I Gaucher Disease Exsar Corporation 20
Testing effectiveness (Phase 2)Study completedNCT00813865What this trial is testingA Long-Term Extension Study of AT2101 (Afegostat Tartrate) in Type 1 Gaucher PatientsWho this might be right forGaucher DiseaseType 1 Gaucher DiseaseGaucher Disease, Type 1 Amicus Therapeutics 8
Not applicableStudy completedNCT02067247What this trial is testingComparison of BMD Measurement by DEXA to BeamMed Speed-of-Sound Measurement at Forearm in Patients With Gaucher DiseaseWho this might be right forGaucher Disease Type 1 Shaare Zedek Medical Center 100
Not applicableLooking for participantsNCT02437396What this trial is testingOxidative Stress and Inflammatory Biomarkers in Gaucher DiseaseWho this might be right forGaucher Disease Type IOxidative StressInflammation University of Minnesota 34
Not applicableWithdrawnNCT00795197What this trial is testingA Screening Study Evaluating Disease Status of Gaucher Type I PatientsWho this might be right forGaucher Disease, Type 1 Genzyme, a Sanofi Company
Post-approval studies (Phase 4)WithdrawnNCT03021941What this trial is testingPharmacokinetics, Pharmacodynamics And Safety Study Of Elelyso(tm) In Pediatric Subjects With Type 1 Gaucher DiseaseWho this might be right forType 1 Gaucher Disease Pfizer
Early research (Phase 1)Study completedNCT05324943What this trial is testingA Gene Therapy Study in Patients With Gaucher Disease Type 1Who this might be right forGaucher Disease, Type 1 Spur Therapeutics 10
Early research (Phase 1)Study completedNCT00004294What this trial is testingPhase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher DiseaseWho this might be right forGaucher's Disease National Center for Research Resources (NCRR) 15
Testing effectiveness (Phase 2)Study completedNCT02583672What this trial is testingRole of Oxidative Stress and Inflammation in Type 1 Gaucher Disease (GD1)Who this might be right forGaucher Disease Type 1 University of Minnesota 33
Large-scale testing (Phase 3)Study completedNCT00553631What this trial is testingStudy of Gene-Activated® Human Glucocerebrosidase (GA-GCB) ERT Compared With Imiglucerase in Type I Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 Shire 34
Very early researchActive Not RecruitingNCT06528080What this trial is testingA Clinical Study for the Treatment of Pediatric and Adolescent Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Shanghai Jiao Tong University School of Medicine 3
Not applicableLooking for participantsNCT04528355What this trial is testingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more Paul Szabolcs 50
Testing effectiveness (Phase 2)Looking for participantsNCT01962415What this trial is testingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more Paul Szabolcs 100
Post-approval studies (Phase 4)Study completedNCT03702361What this trial is testingRapid Intravenous Infusion of Velaglucerase Alfa (VPRIV) in Treatment-naive Patients With Type 1 Gaucher DiseaseWho this might be right forPrimary Disease Shaare Zedek Medical Center 15
Large-scale testing (Phase 3)Study completedNCT00635427What this trial is testingAn Open-Label Extension Study of GA-GCB ERT in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 Shire 95