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Results for “Type I Gaucher Disease”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Active Not RecruitingNCT02843035
What this trial is testing

Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extension

Who this might be right for
Gaucher Disease Type 1Gaucher Disease Type 3
Genzyme, a Sanofi Company 12
Large-scale testing (Phase 3)WithdrawnNCT01161914
What this trial is testing

The Safety and Efficacy Study of ISU302 in Patient With Type I Gaucher Disease

Who this might be right for
Gaucher Disease
ISU Abxis Co., Ltd.
Post-approval studies (Phase 4)WithdrawnNCT02528617
What this trial is testing

The Effect of Velaglucerase Alfa (Vpriv) on Skeletal Development in Pediatric Gaucher Disease

Who this might be right for
Gaucher Disease Type 1Gaucher Disease Type 3
Baylor Research Institute
Post-approval studies (Phase 4)Study completedNCT00364858
What this trial is testing

Safety and Efficacy of Cerezyme® Infusions Every 4 Weeks Versus Every 2 Weeks in Type 1 Gaucher Disease

Who this might be right for
Gaucher Disease, Type 1Cerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency Disease+2 more
Genzyme, a Sanofi Company 95
Large-scale testing (Phase 3)Study completedNCT00319046
What this trial is testing

Clinical Study to Evaluate the Long Term Efficacy, Safety and Tolerability of Miglustat in Patients With Stable Type 1 Gaucher Disease

Who this might be right for
Gaucher Disease Type 1
Actelion 42
Not applicableUnknownNCT02605603
What this trial is testing

SRT in Comparison to ERT on Immune Aspects and Bone Involvement in Gaucher Disease

Who this might be right for
Gaucher Disease
Lysosomal and Rare Disorders Research and Treatment Center, Inc. 30
Testing effectiveness (Phase 2)Ended earlyNCT04145037
What this trial is testing

Lentiviral Vector Gene Therapy - The Guard1 Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease

Who this might be right for
Gaucher Disease
AVROBIO 8
Not applicableStudy completedNCT04353466
What this trial is testing

Assessing the Impact of Elelyso on Bone Involvement Currently Treated With Other ERTs

Who this might be right for
Gaucher Disease, Type 1
Shaare Zedek Medical Center 30
Large-scale testing (Phase 3)Looking for participantsNCT07223944
What this trial is testing

A Gaucher Disease Gene Therapy Trial With FLT201

Who this might be right for
Gaucher Disease Type 1
Spur Therapeutics 45
Not applicableEnded earlyNCT04836377
What this trial is testing

A Long-Term Follow-up Study of Subjects With Gaucher Disease Who Previously Received AVR-RD-02

Who this might be right for
Type 1 Gaucher Disease
AVROBIO 4
Early research (Phase 1)Looking for participantsNCT04532047
What this trial is testing

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

Who this might be right for
MPS IMPS IIMPS IVA+6 more
University of California, San Francisco 10
Not applicableUnknownNCT01274208
What this trial is testing

Examining the Immune Response in Patients With Gaucher Disease and Hepatitis C

Who this might be right for
Gaucher DiseaseHepatitis C
Shaare Zedek Medical Center 80
Testing effectiveness (Phase 2)Looking for participantsNCT06818838
What this trial is testing

A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher Disease

Who this might be right for
Gaucher Disease Type 1
Lingyi Biotech Co., Ltd. 12
Large-scale testing (Phase 3)Study completedNCT02770625
What this trial is testing

Phase III Study of ISU302 in Patients With Type 1 Gaucher Disease

Who this might be right for
Gaucher Disease, Type 1
ISU Abxis Co., Ltd. 8
Not applicableLooking for participantsNCT06162338
What this trial is testing

The Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type I

Who this might be right for
Gaucher Disease Type I
He Huang 3
Testing effectiveness (Phase 2)Study completedNCT00446550
What this trial is testing

Oral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher Disease

Who this might be right for
Gaucher DiseaseType 1 Gaucher DiseaseGaucher Disease, Type 1
Amicus Therapeutics 19
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07603050
What this trial is testing

A Phase I/II Clinical Study to Evaluate the Safety and Efficacy of VGN-R08b in Patients With Type III Gaucher's Disease

Who this might be right for
Gaucher Disease Type 3
Shanghai Vitalgen BioPharma Co., Ltd. 12
Not applicableStudy completedNCT02053896
What this trial is testing

A Switch-Over Study of the Safety and Efficacy of ISU302 in Patients With Type 1 Gaucher Disease

Who this might be right for
Gaucher Disease
ISU Abxis Co., Ltd. 5
Testing effectiveness (Phase 2)Study completedNCT00001416
What this trial is testing

Bone Response to Enzyme Replacement in Gaucher's Disease

Who this might be right for
Gaucher's Disease
National Institute of Neurological Disorders and Stroke (NINDS) 100
Testing effectiveness (Phase 2)Study completedNCT00391625
What this trial is testing

Open-Label Extension Study Evaluating Long Term Safety in Patients With Type 1 Gaucher Disease Receiving DRX008A (ERT)

Who this might be right for
Gaucher Disease
Shire 10
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