Early research (Phase 1)Not Yet RecruitingNCT06592131What this trial is testingBF844 Safety and Pharmacokinetic Study in Healthy VolunteersWho this might be right forUsher Syndrome Type 3 EyeXCel Pty. Ltd. 76
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Testing effectiveness (Phase 2)Study completedNCT01530659What this trial is testingRetinal Imaging in CNTF -Releasing Encapsulated Cell Implant Treated Patients for Early-stage Retinitis PigmentosaWho this might be right forRetinitis PigmentosaUsher Syndrome Type 2Usher Syndrome Type 3 Neurotech Pharmaceuticals 22