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Results for “Variant Late-Infantile Neuronal Ceroid Lipofuscinosis”

3 trials

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Showing 3 of 3 results

Testing effectiveness (Phase 2)Study completedNCT02725580
What this trial is testing

Gene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 (vLINCL6) Disease

Who this might be right for
Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
Emily de los Reyes 13
Not applicableEnded earlyNCT04644549
What this trial is testing

Natural History Study of Batten Disease

Who this might be right for
Batten DiseaseNeuronal Ceroid Lipofuscinosis CLN6Neuronal Ceroid Lipofuscinosis CLN3
Emily de los Reyes 10
Not applicableLooking for participantsNCT01793168
What this trial is testing

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Who this might be right for
Rare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more
Sanford Health 20,000