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Results for “Alpha; Thalassemia”

40 trials

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Showing 20 of 40 results

Not applicableLooking for participantsNCT06539169
What this trial is testing

FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

Who this might be right for
Alpha-ThalassemiaBeta-ThalassemiaAmyloidosis+14 more
xCures 1,000
Early research (Phase 1)Ended earlyNCT02986698
What this trial is testing

In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM)

Who this might be right for
Alpha Thalassemia MajorHemoglobinopathy; With ThalassemiaHemoglobinopathies+6 more
University of California, San Francisco 6
Not applicableEnrolling By InvitationNCT03655223
What this trial is testing

Early Check: Expanded Screening in Newborns

Who this might be right for
Spinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more
RTI International 30,000
Not applicableStudy completedNCT00159029
What this trial is testing

Genetics of Alpha Thalassemia in Israeli Ethnic Groups

Who this might be right for
Alpha Thalassemia
Deborah Rund 100
Not applicableStudy completedNCT06831799
What this trial is testing

ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19

Who this might be right for
HemoglobinopathiesSickle Cell DiseaseSickle Cell Anemia+21 more
Hospital Universitari Vall d'Hebron Research Institute 684
Not applicableStudy completedNCT03948737
What this trial is testing

The Effect of Alpha-tocopherol in Hemolysis and Oxidative Stress Marker on the Red Cell Membrane Beta-thalassemia Major

Who this might be right for
Beta Thalassemia Major AnemiaHemolysisOxidative Stress
Indonesia University 40
Not applicableStudy completedNCT00971984
What this trial is testing

Demographic, Clinical and Laboratory Characteristics of Children With Alpha Thalassemia in Northern Israel

Who this might be right for
Thalassemia AlphaHemolytic Anemia
HaEmek Medical Center, Israel 50
Not applicableActive Not RecruitingNCT03412760
What this trial is testing

Hydrops: Diagnosing & Redefining Outcomes With Precision Study

Who this might be right for
Hydrops FetalisBirth DefectFetal Anomaly
University of California, San Francisco 500
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Testing effectiveness (Phase 2)Study completedNCT04987489
What this trial is testing

Etavopivat in Patients With Thalassemia or Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseThalassemia
Forma Therapeutics, Inc. 53
Not applicableLooking for participantsNCT03937817
What this trial is testing

Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants

Who this might be right for
Alpha and Beta ThalassemiaSickle Cell DiseaseMalaria+1 more
National Institute of Allergy and Infectious Diseases (NIAID) 300
Not applicableEnded earlyNCT02179359
What this trial is testing

Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more
Masonic Cancer Center, University of Minnesota 38
Not applicableLooking for participantsNCT05799118
What this trial is testing

Study of the Role of Genetic Modifiers in Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseThalassemia, BetaThalassemia Alpha+1 more
Cyprus Institute of Neurology and Genetics 30,000
Testing effectiveness (Phase 2)Study completedNCT00873041
What this trial is testing

Efficacy and Safety of Deferasirox in Non-transfusion Dependent Thalassemia Patients With Iron Overload and a One Year Open-label Extension Study

Who this might be right for
Non-transfusion Dependent Thalassemia
Novartis Pharmaceuticals 166
Not applicableEnrolling By InvitationNCT05528796
What this trial is testing

Uncovering the Etiologies of Non-immune Hydrops Fetalis

Who this might be right for
Non-Immune Hydrops Fetalis
University of California, San Francisco 500
Testing effectiveness (Phase 2)Looking for participantsNCT05735717
What this trial is testing

MT2021-08T Cell Receptor Alpha/Beta Depletion PBSC Transplantation for Heme Malignancies

Who this might be right for
Hematologic MalignancyAcute LeukemiaRemission+21 more
Masonic Cancer Center, University of Minnesota 70
Not applicableLooking for participantsNCT04528355
What this trial is testing

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more
Paul Szabolcs 50
Large-scale testing (Phase 3)Not Yet RecruitingNCT07517133
What this trial is testing

Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia

Who this might be right for
Non-Transfusion-dependent Alpha-ThalassemiaNon-Transfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 45
Not applicableLooking for participantsNCT06213402
What this trial is testing

RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)

Who this might be right for
Sickle Cell DiseaseThalassemiaHemolytic; Anemia, Hereditary, Due to Enzyme Disorder+6 more
Hospital Universitari Vall d'Hebron Research Institute 32,564
Not applicableLooking for participantsNCT03775954
What this trial is testing

Fetal Electrophysiologic Abnormalities in High-Risk Pregnancies Associated With Fetal Demise

Who this might be right for
High Risk PregnancyCongenital Heart DiseaseFetal Hydrops+16 more
Medical College of Wisconsin 30
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