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Results for “Anemia, Hypoplastic, Congenital”

139 trials

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Showing 20 of 139 results

Early research (Phase 1)Ended earlyNCT01034592
What this trial is testing

Pilot Lenalidomide in Adult Diamond-Blackfan Anemia Patients w/ RBC Transfusion-Dependent Anemia

Who this might be right for
AnemiaLeukemiaAcute Myeloid Leukemia (AML)+1 more
Jason Robert Gotlib 2
Not applicableLooking for participantsNCT07649031
What this trial is testing

MRI as Noninvasive Innovative Approach in Detection and Monitoring of Malignant Oral Lesions in Fanconi Anemia Patients

Who this might be right for
Fanconi Anemia
University of Minnesota 80
Not applicableStudy completedNCT01565005
What this trial is testing

Microcephaly Genetic Deficiency in Neural Progenitors

Who this might be right for
Microcephaly
Assistance Publique - Hôpitaux de Paris 98
Testing effectiveness (Phase 2)Looking for participantsNCT03579875
What this trial is testing

Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders

Who this might be right for
Fanconi AnemiaSevere Aplastic AnemiaMyelodysplastic Syndromes+5 more
Masonic Cancer Center, University of Minnesota 48
Testing effectiveness (Phase 2)Study completedNCT02931071
What this trial is testing

Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1

Who this might be right for
Fanconi Anemia
Hospital Universitari Vall d'Hebron Research Institute 13
Testing effectiveness (Phase 2)WithdrawnNCT01419704
What this trial is testing

Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies

Who this might be right for
Anemia, Sickle CellComplex and Transfusion-dependent HemoglobinopathiesThalassemia+4 more
Talaris Therapeutics Inc.
Not applicableLooking for participantsNCT05687149
What this trial is testing

Defining the Natural History of Squamous Cell Carcinoma in Fanconi Anemia

Who this might be right for
Fanconi AnemiaInherited Bone Marrow Failure Syndrome
National Cancer Institute (NCI) 200
Testing effectiveness (Phase 2)Study completedNCT06045052
What this trial is testing

Eltrombopag for Treatment of Fanconi Anemia

Who this might be right for
Fanconi Anemia
Julian Sevilla 8
Not applicableStudy completedNCT00499070
What this trial is testing

Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment

Who this might be right for
Dyskeratosis CongenitaFanconi AnemiaMyelodysplastic Syndromes+2 more
University Hospital Freiburg 119
Not applicableStudy completedNCT00899522
What this trial is testing

Tissue Sample Collection From Patients With Fanconi Anemia

Who this might be right for
Fanconi AnemiaUnspecified Adult Solid Tumor, Protocol SpecificUnspecified Childhood Solid Tumor, Protocol Specific
OHSU Knight Cancer Institute 8
Not applicableStudy completedNCT00595127
What this trial is testing

Hematopoietic Stem Cell Transplantation for Treatment of Patients With Fanconi Anemia Lacking a Genotypically Identical Donor, Using Total Body Irradiation, Cyclophosphamide and Fludarabine

Who this might be right for
Fanconi Anemia
Memorial Sloan Kettering Cancer Center 21
Testing effectiveness (Phase 2)Looking for participantsNCT04232085
What this trial is testing

Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures

Who this might be right for
Primary Immune Deficiency DisorderImmune Deficiency DiseaseBone Marrow Failure+7 more
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins 27
Large-scale testing (Phase 3)Study completedNCT00176878
What this trial is testing

Stem Cell Transplant for Bone Marrow Failure Syndromes

Who this might be right for
Diamond-Blackfan AnemiaKostmann's NeutropeniaShwachman-Diamond Syndrome
Masonic Cancer Center, University of Minnesota 10
Testing effectiveness (Phase 2)Study completedNCT03476330
What this trial is testing

Quercetin Chemoprevention for Squamous Cell Carcinoma in Patients With Fanconi Anemia

Who this might be right for
Fanconi AnemiaSquamous Cell Carcinoma
Children's Hospital Medical Center, Cincinnati 48
Not applicableLooking for participantsNCT00106015
What this trial is testing

Diamond Blackfan Anemia Registry (DBAR)

Who this might be right for
AnemiaBlood Disease
Northwell Health 900
Testing effectiveness (Phase 2)Study completedNCT03398824
What this trial is testing

Pilot Study of Metformin for Patients With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Boston Children's Hospital 15
Not applicableNot Yet RecruitingNCT07005297
What this trial is testing

Clinical Genetics Branch Eligibility Screening Survey

Who this might be right for
MelanomaLi-Fraumeni SyndromePulmonary Blastoma+7 more
National Cancer Institute (NCI) 1,000
Testing effectiveness (Phase 2)Study completedNCT00005898
What this trial is testing

Phase I/II Study of Total Body Irradiation, Cyclophosphamide, and Fludarabine Followed by Alternate Donor Hematopoietic Cell Transplantation in Patients With Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
University of Minnesota 30
Early research (Phase 1)Study completedNCT00243399
What this trial is testing

Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 10
Testing effectiveness (Phase 2)Study completedNCT02797977
What this trial is testing

A Phase 1/2 Trial SRA737 in Combination With Gemcitabine and Cisplatin or Gemcitabine Alone in Advanced Cancer Subjects

Who this might be right for
Advanced Solid Tumors
Sierra Oncology LLC - a GSK company 153
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