Not applicableStudy completedNCT03650569What this trial is testingItalian Angelman Syndrome RegistryWho this might be right forAngelman Syndrome FROM- Fondazione per la Ricerca Ospedale di Bergamo- ETS 82
Testing effectiveness (Phase 2)WithdrawnNCT02226458What this trial is testingAn Exploratory Open Label Study of EPI-743 (Vincerinone TM) in Children With Autism Spectrum DisorderWho this might be right forAutism Spectrum Disorder Edison Pharmaceuticals Inc
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Not applicableStudy completedNCT02670694What this trial is testingSleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PWWho this might be right forRett SyndromePrader-Willi SyndromeAngelman Syndrome+1 more Baylor College of Medicine 804
Testing effectiveness (Phase 2)Study completedNCT04259281What this trial is testingThe Safety and Tolerability of GTX-102 in Children With Angelman SyndromeWho this might be right forAngelman Syndrome Ultragenyx Pharmaceutical Inc 74
Not applicableLooking for participantsNCT05945576What this trial is testingIDMet (RaDiCo Cohort) (RaDiCo-IDMet)Who this might be right forSilver Russell SyndromeBeckwith-Wiedemann SyndromeTransient Neonatal Diabetes Mellitus+6 more Institut National de la Santé Et de la Recherche Médicale, France 2,000
Not applicableUnknownNCT06337383What this trial is testingStudy of the Prevalence of Autistic Traits in Angelman SyndromeWho this might be right forAngelman Syndrome IRCCS Eugenio Medea 46
Large-scale testing (Phase 3)Ended earlyNCT03882918What this trial is testingAn Open-Label Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of OV101 in Individuals With Angelman SyndromeWho this might be right forAngelman Syndrome Healx AI 141
Not applicableEnrolling By InvitationNCT03836300What this trial is testingParent and Infant Inter(X)Action Intervention (PIXI)Who this might be right forFragile X SyndromeAngelman SyndromePrader-Willi Syndrome+11 more RTI International 120
Not applicableStudy completedNCT00773825What this trial is testingGenomic Imprinting and Assisted Reproductive TechnologiesWho this might be right forNatural PregnancyPregnancy, Ovarian Assistance Publique - Hôpitaux de Paris 542
Early research (Phase 1)Study completedNCT01903681What this trial is testingAssessment of the Pharmacokinetics of Circadin® in Children With Neurodevelopmental Disorders and Sleep DisturbancesWho this might be right forSleep Problems Neurim Pharmaceuticals Ltd. 16
Large-scale testing (Phase 3)Study completedNCT01906866What this trial is testingEfficacy and Safety of Circadin® in the Treatment of Sleep Disturbances in Children With Neurodevelopment DisabilitiesWho this might be right forSleep Disorders Neurim Pharmaceuticals Ltd. 125
Testing effectiveness (Phase 2)Study completedNCT05630066What this trial is testingInvestigate the Pharmacokinetics (PK) and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype.Who this might be right forAngelman Syndrome Hoffmann-La Roche 48
Not applicableStudy completedNCT05783791What this trial is testingDevelopment of a Newborn Screening Assay for Angelman Syndrome and Prader-Willi SyndromeWho this might be right forAngelman SyndromePrader-Willi Syndrome University of Wisconsin, Madison 11
Testing effectiveness (Phase 2)Study completedNCT02996305What this trial is testingA Study in Adults and Adolescents With Angelman Syndrome (STARS)Who this might be right forAngelman Syndrome Healx AI 88
Large-scale testing (Phase 3)Study completedNCT04106557What this trial is testingOV101 in Individuals With Angelman Syndrome (AS)Who this might be right forPrimary Disease or Condition Being Studied: Angelman Syndrome (AS) Healx AI 104
Not applicableStudy completedNCT04155944What this trial is testingDiagnosis of Prader-Willi Syndrome and Angelman SyndromeWho this might be right forMental DisorderFetus Disorder National Cheng-Kung University Hospital 60
Large-scale testing (Phase 3)Enrolling By InvitationNCT06415344What this trial is testingLong-term Extension of GTX-102 in Angelman SyndromeWho this might be right forAngelman Syndrome Ultragenyx Pharmaceutical Inc 255
Not applicableLooking for participantsNCT06737718What this trial is testingUse of Eye Tracking to Study Social Perception Abnormalities in Children With Angelman SyndromeWho this might be right forAngelman Syndrome Assistance Publique - Hôpitaux de Paris 60
Large-scale testing (Phase 3)Looking for participantsNCT06914609What this trial is testingREVEAL: A Phase 3 Study of ION582 in Angelman SyndromeWho this might be right forAngelman Syndrome Ionis Pharmaceuticals, Inc. 158