Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Beta Thalassemia Transfusion Dependent”

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 0 results

Early research (Phase 1)Study completedNCT04718844
What this trial is testing

A Study Investigate the Safety, Tolerability, Pharmacokinetic, and Pharmacodynamic Response of SLN124 in Adults With Alpha/Beta-thalassaemia and Very Low- and Low-risk Myelodysplastic Syndrome

Who this might be right for
Non-transfusion-dependent ThalassemiaLow Risk Myelodysplastic SyndromeVery-Low Risk Myelodysplastic Syndrome
Silence Therapeutics plc 44
Early research (Phase 1)Ended earlyNCT02274233
What this trial is testing

Safety and Pharmacokinetic Study of Escalating Doses of SP-420, an Iron Chelator, in Patients With β-Thalassemia

Who this might be right for
Iron OverloadBeta-Thalassemia
Sideris Pharmaceuticals 24
Testing effectiveness (Phase 2)Study completedNCT01740713
What this trial is testing

Pharmacokinetic Study of Deferiprone in Paediatric Patients

Who this might be right for
Chronic Iron Overload
Consorzio per Valutazioni Biologiche e Farmacologiche 23
Not applicableUnknownNCT02067130
What this trial is testing

Utility of Fibroscan in Estimating Hepatic Iron Concentration

Who this might be right for
Hereditary Anemias
University of British Columbia 30
Testing effectiveness (Phase 2)Active Not RecruitingNCT05577312
What this trial is testing

Safety and Efficacy Evaluation of BRL-101 in Subjects With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta-Thalassemia
Bioray Laboratories 39
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07721480
What this trial is testing

Gene Therapy for Patients With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta Thalassemia Transfusion Dependent
Prince of Wales Hospital, Shatin, Hong Kong 6
Testing effectiveness (Phase 2)Study completedNCT04987489
What this trial is testing

Etavopivat in Patients With Thalassemia or Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseThalassemia
Forma Therapeutics, Inc. 53
Not applicableNot Yet RecruitingNCT06512298
What this trial is testing

Plasticizer Exposure and Its Consequences on Health

Who this might be right for
Beta-thalassemiaGliomaHealthy Controls+3 more
Medical University of Vienna 120
Very early researchLooking for participantsNCT05762510
What this trial is testing

A Study Evaluating the Safety and Efficacy of LentiRed Drug Product in Transfusion-dependent β-Thalassemia [TDT]

Who this might be right for
Transfusion Dependent Beta-Thalassemia
First Affiliated Hospital of Guangxi Medical University 5
Testing effectiveness (Phase 2)UnknownNCT02453477
What this trial is testing

Gene Therapy for Transfusion Dependent Beta-thalassemia

Who this might be right for
Beta-Thalassemia
IRCCS San Raffaele 10
Not applicableLooking for participantsNCT05776173
What this trial is testing

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia

Who this might be right for
β-thalassemia Major
Shanghai BDgene Co., Ltd. 10
Early research (Phase 1)Looking for participantsNCT06647979
What this trial is testing

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseSickle Cell Anemia (HbSS, or HbSβ-thalassemia0)Beta-Thalassemia+1 more
Daniel Bauer 10
Testing effectiveness (Phase 2)Study completedNCT03802201
What this trial is testing

Study of PTG-300 in Non-Transfusion Dependent and Transfusion-Dependent Beta-Thalassemia Subjects With Chronic Anemia

Who this might be right for
β-thalassemiaIneffective ErythropoiesisChronic Anemia
Protagonist Therapeutics, Inc. 63
Testing effectiveness (Phase 2)Active Not RecruitingNCT05444894
What this trial is testing

EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)

Who this might be right for
Transfusion Dependent Beta ThalassemiaHemoglobinopathiesThalassemia Major+1 more
Editas Medicine, Inc. 9
Testing effectiveness (Phase 2)WithdrawnNCT03801889
What this trial is testing

SP-420 in Subjects With Transfusion-dependent Beta-Thalassemia or Other Rare Anemias

Who this might be right for
Iron OverloadBeta-Thalassemia
Abfero Pharmaceuticals, Inc
Not applicableLooking for participantsNCT07207577
What this trial is testing

Evaluation of Physiological and Psychological Factors Involved in Exercise Intolerance in Patients With β-TTD

Who this might be right for
Beta Thalassemia Transfusion Dependent
Centre Hospitalier Metropole Savoie 36
Not applicableEnrolling By InvitationNCT06664541
What this trial is testing

Decision-Making and Quality of Life Surrounding Hematologic Disease and Gene Therapy

Who this might be right for
Transfusion Dependent Beta ThalassemiaSickle Cell Disease
Georgetown University 100
Testing effectiveness (Phase 2)Study completedNCT02151526
What this trial is testing

A Study Evaluating the Safety and Efficacy of LentiGlobin BB305 Drug Product in β-Thalassemia Major (Also Referred to as Transfusion-dependent β-Thalassemia [TDT]) and Sickle Cell Disease

Who this might be right for
Beta-Thalassemia MajorSickle Cell Disease
Genetix Biotherapeutics Inc. 7
Early research (Phase 1)Study completedNCT02950857
What this trial is testing

EPEG in Beta Thalassemia Patients

Who this might be right for
Beta-Thalassemia
Prolong Pharmaceuticals 6
Post-approval studies (Phase 4)Study completedNCT00749515
What this trial is testing

Pilot Study for Patients With Poor Response to Deferasirox

Who this might be right for
Transfusion-dependent HemachromatosisThalassemia MajorSickle Cell Disease
Boston Children's Hospital 15
Next Page