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Results for “Bone Marrow Failure”

669 trials

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Showing 20 of 669 results

Not applicableStudy completedNCT04959188
What this trial is testing

Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD)

Who this might be right for
Dyskeratosis CongenitaTelomere Biology Disorders
National Cancer Institute (NCI) 53
Not applicableStudy completedNCT00134342
What this trial is testing

Tuberculosis (TB) Screening for the Diagnosis of Latent TB in Immunocompromised Populations

Who this might be right for
Tuberculosis
University Health Network, Toronto 203
Not applicableUnknownNCT04001686
What this trial is testing

Ambispective Observational Study to Evaluate the Incidence and Management of Aplastic Anemia in Spain

Who this might be right for
Aplastic Anemia
Biogipuzkoa Health Research Institute 109
Testing effectiveness (Phase 2)Study completedNCT01362595
What this trial is testing

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan AnemiaBlackfan Diamond SyndromeDBA+2 more
Northwell Health 55
Not applicableUnknownNCT06335277
What this trial is testing

Total Body Irradiation Treatments for Patients Treated at European Institute of Oncology

Who this might be right for
LeukemiaLeukemia, ChronicLeukemia, Acute+2 more
European Institute of Oncology 50
Very early researchStudy completedNCT00965666
What this trial is testing

Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 3
Not applicableLooking for participantsNCT06650553
What this trial is testing

Umbilical Cord Blood-Supported Haplo-HSCT for Aplastic Anemia Treatment Study

Who this might be right for
Aplastic Anemias
Shanxi Bethune Hospital 110
Not applicableAvailableNCT06731036
What this trial is testing

Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts

Who this might be right for
Severe Combined ImmunodeficiencyFanconi AnemiaDyskeratosis Congenita+1 more
University of Florida
Testing effectiveness (Phase 2)Study completedNCT01297972
What this trial is testing

Mesenchymal Stem Cells in the Treatment of Relapsed/Refractory Severe Acquired Aplastic Anemia

Who this might be right for
Aplastic Anemia
University of Sao Paulo 9
Testing effectiveness (Phase 2)Ended earlyNCT00720629
What this trial is testing

Visilizumab for the Prevention of Graft-versus-Host Disease After Allogeneic Hematopoietic Cell Transplantation

Who this might be right for
Graft Versus Host Disease
H. Lee Moffitt Cancer Center and Research Institute 8
Testing effectiveness (Phase 2)Looking for participantsNCT03173937
What this trial is testing

Unrelated Umbilical Cord Blood Transplantation for Severe Aplastic Anemia and Hypo-plastic MDS Using CordIn(TM), Umbilical Cord Blood-Derived Ex Vivo Expanded Stem and Progenitor Cells to Expedite Engraftment and Improve Transplant Outcome

Who this might be right for
Severe Aplastic AnemiaHypo-Plastic MDSMyelodysplastic Syndrome (MDS)
National Heart, Lung, and Blood Institute (NHLBI) 37
Testing effectiveness (Phase 2)Ended earlyNCT01748240
What this trial is testing

Addition of Vorinostat to Azacitidine in Higher Risk MDS a Phase II add-on Study in Patients With Azacitidine Failure

Who this might be right for
Myelodysplastic Syndrome
Groupe Francophone des Myelodysplasies 21
Not applicableStudy completedNCT06669221
What this trial is testing

Effectiveness of Early Intervention in Transfusion Independent Aplastic Anemia: a Retrospective Medical Claims Database Study

Who this might be right for
Aplastic Anemia (AA)
Novartis Pharmaceuticals 1,603
Not applicableUnknownNCT02172365
What this trial is testing

Allogeneic SCT for CML, TKI Failure After TKI Failure

Who this might be right for
Chronic Myeloid Leukemia
University Health Network, Toronto 350
Testing effectiveness (Phase 2)UnknownNCT04069533
What this trial is testing

Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A

Who this might be right for
Fanconi Anemia Complementation Group A
Rocket Pharmaceuticals Inc. 7
Testing effectiveness (Phase 2)UnknownNCT01844063
What this trial is testing

Safety and Efficacy of Diverse Mesenchymal Stem Cells Transplantation for Liver Failure

Who this might be right for
Liver Failure
Third Affiliated Hospital, Sun Yat-Sen University 210
Not applicableStudy completedNCT00701844
What this trial is testing

Sharing Our Strength: A Research Study for Bone Marrow/Stem Cell Transplant Survivors

Who this might be right for
LeukemiaAcute LeukemiaAcute Lymphocytic Leukemia+3 more
University of North Carolina, Chapel Hill 315
Testing effectiveness (Phase 2)WithdrawnNCT01419704
What this trial is testing

Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies

Who this might be right for
Anemia, Sickle CellComplex and Transfusion-dependent HemoglobinopathiesThalassemia+4 more
Talaris Therapeutics Inc.
Early research (Phase 1)Looking for participantsNCT03896269
What this trial is testing

CPX-351 in Treating Patients With Relapsed or Refractory High Risk Myelodysplastic Syndrome or Chronic Myelomonocytic Leukemia

Who this might be right for
Blasts 10-19 Percent of Bone Marrow Nucleated CellsBlasts More Than 5 Percent of Bone Marrow Nucleated CellsHigh Risk Chronic Myelomonocytic Leukemia+4 more
M.D. Anderson Cancer Center 38
Not applicableStudy completedNCT06991894
What this trial is testing

Real-world Outcomes of Aplastic Anemia Patients Treated With Eltrombopag: A Medical Claims Database Study

Who this might be right for
Anemia, Aplastic
Novartis Pharmaceuticals 2,517
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