Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Congenital Anemias”

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 0 results

Testing effectiveness (Phase 2)Ended earlyNCT02564796
What this trial is testing

Erythropoietin to Prevent Unnecessary Transfusions In Patients With Cyanotic CHD - A Prospective Control Trial

Who this might be right for
Cyanotic Congenital Heart DiseaseAnemiaCyanosis+1 more
University of California, San Diego 4
Testing effectiveness (Phase 2)Study completedNCT03263559
What this trial is testing

Haploidentical Bone Marrow Transplantation in Sickle Cell Patients (BMTCTN1507)

Who this might be right for
Sickle Cell Disease
Medical College of Wisconsin 95
Not applicableStudy completedNCT05730374
What this trial is testing

Benson's Relaxation Technique, Music Therapy for Children With Thalassemia

Who this might be right for
Thalassemia in Children
Alexandria University 120
Very early researchWithdrawnNCT04776850
What this trial is testing

Pre-transplant Immunosuppression and Donor Stem Cell Transplant for the Treatment of Severe Hemoglobinopathies

Who this might be right for
Beta Thalassemia MajorSickle Beta 0 ThalassemiaSickle Beta Plus Thalassemia+3 more
M.D. Anderson Cancer Center
Not applicableLooking for participantsNCT06770010
What this trial is testing

Advancing Feasibility and Acceptability of Digital Cognitive Rehabilitation in Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
Children's National Research Institute 50
Not applicableStudy completedNCT03291613
What this trial is testing

Gaming Technology to Engage Adolescent Sickle Cell Patients in Pain Management

Who this might be right for
Sickle Cell Disease
Klein Buendel, Inc. 13
Not applicableTemporarily pausedNCT05442346
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
Thalassemia Major
Bioray Laboratories 5
Not applicableStudy completedNCT02258997
What this trial is testing

Hepcidin Levels in Sickle Cell Disease (SCD)

Who this might be right for
Sickle Cell AnemiaSickle - Beta Thalassemia
Kenneth Ataga, MD 42
Not applicableNo Longer AvailableNCT01200017
What this trial is testing

Expanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell Transplant

Who this might be right for
Acute Lymphoblastic LeukemiaAcute Myeloid LeukemiaChronic Myeloid Leukemia+9 more
Christopher Dvorak
Testing effectiveness (Phase 2)Study completedNCT01392989
What this trial is testing

Post T-plant Infusion of Allogeneic Cytokine Induced Killer (CIK) Cells as Consolidative Therapy in Myelodysplastic Syndromes/Myeloproliferative Disorders

Who this might be right for
Neural Tube DefectsAnemiaLeukemia, Myeloid+3 more
Everett Meyer 44
Early research (Phase 1)Study completedNCT00255710
What this trial is testing

Cyclophosphamide and/or Mycophenolate Mofetil With or Without Tacrolimus in Treating Patients Who Are Undergoing a Donor Bone Marrow or Peripheral Stem Cell Transplant for Hematologic Cancer

Who this might be right for
Chronic Myeloproliferative DisordersGraft Versus Host DiseaseLeukemia+4 more
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins 60
Not applicableStudy completedNCT04171635
What this trial is testing

Quantitative Susceptibility Mapping (QSM) to Guide Iron Chelating Therapy

Who this might be right for
MRI Scans
Weill Medical College of Cornell University 55
Not applicableStudy completedNCT01793740
What this trial is testing

Cognitive Rehabilitation in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseCognitive Impairment
Duke University 18
Early research (Phase 1)Ended earlyNCT00004058
What this trial is testing

12-O-Tetradecanoylphorbol-13-acetate in Treating Patients With Hematologic Cancer or Bone Marrow Disorder

Who this might be right for
Chronic Myeloproliferative DisordersLeukemiaLymphoma+4 more
University of Medicine and Dentistry of New Jersey
Testing effectiveness (Phase 2)Study completedNCT01789255
What this trial is testing

Vorinostat, Tacrolimus, and Methotrexate in Preventing GVHD After Stem Cell Transplant in Patients With Hematological Malignancies

Who this might be right for
Accelerated Phase Chronic Myelogenous LeukemiaAdult Acute Myeloid Leukemia in RemissionAdult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities+115 more
National Cancer Institute (NCI) 12
Not applicableStudy completedNCT03621826
What this trial is testing

Evaluating Barriers to Stroke Screening and Prevention in Children With Sickle Cell Disease

Who this might be right for
Stroke IschemicSickle Cell Disease
Medical University of South Carolina 5,247
Not applicableStudy completedNCT03624335
What this trial is testing

Influence of Umbilical Cord Clamping Time in the Newborn

Who this might be right for
Anemia NeonatalPolycythemia SecondaryHyperbilirubinemia, Neonatal
Pascual Gregori Roig 195
Not applicableEnded earlyNCT04964323
What this trial is testing

Pyruvate Kinase (PK) Deficiency Global Longitudinal Registry: Patient-Reported Outcomes (PRO)

Who this might be right for
Pyruvate Kinase DeficiencyPyruvate Kinase Deficiency AnemiaAnemia+1 more
Agios Pharmaceuticals, Inc. 15
Testing effectiveness (Phase 2)Study completedNCT01749540
What this trial is testing

Study to Evaluate the Safety and Efficacy of Luspatercept (ACE-536) in Participants With Beta-thalassemia (A536-04/MK-6143-002)

Who this might be right for
B-Thalassemia
Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA 64
Not applicableUnknownNCT04929574
What this trial is testing

Evaluation of Heart Status in Patients of Beta Thalassemia Using Echocardiogram

Who this might be right for
Beta Thalassemia
Nanfang Hospital, Southern Medical University 1,200
Next Page