Early research (Phase 1)Ended earlyNCT02012777What this trial is testingPropanolol and Red Cell Adhesion Non-asthmatic Children Sickle Cell DiseaseWho this might be right forSickle Cell Disease University of Miami 9
Not applicableStudy completedNCT04606160What this trial is testingUtilizing A Single Session Problem-Solving Intervention With Caregivers of Pediatric Patients Receiving Chronic Transfusion to Treat Sickle Cell DiseaseWho this might be right forSickle Cell Disease University of Texas Southwestern Medical Center 20
Not applicableStudy completedNCT05879224What this trial is testingShort Course Primaquine for the Radical Cure of P. Vivax Malaria - IndonesiaWho this might be right forVivax MalariaG6PD Deficiency Menzies School of Health Research 2,999
Not applicableUnknownNCT04864041What this trial is testingEvaluation of Left Ventricular Function by Speckle Tracking Echocardiography in Patient Hospitalised in Intensive Care Unit for Vaso-occlusive CrisisWho this might be right forSickle Cell Disease Bicetre Hospital 30
Testing effectiveness (Phase 2)Active Not RecruitingNCT06308159What this trial is testingAn Open-label Study of a Gene Therapy Product (Vebeglogene Autotemcel) in Transfusion Dependent Beta-ThalassemiaWho this might be right forBeta-Thalassemia Lantu Biopharma 6
Not applicableNot Yet RecruitingNCT07788703What this trial is testingNeoSpHb Study: Can a Painless Device Detect Anaemia in Babies Without Blood Tests? A Study in the Neonatal Intensive Care Unit (NICU)Who this might be right forAnemia University of Malaya 30
Testing effectiveness (Phase 2)Study completedNCT01788631What this trial is testingA Phase II Trial of Regadenoson in Sickle Cell AnemiaWho this might be right forSickle Cell Anemia Dana-Farber Cancer Institute 100
Not applicableStudy completedNCT04273022What this trial is testingEffect of Exercise on Biomarkers in SCTWho this might be right forSickle Cell Trait St. Louis University 12
Not applicableLooking for participantsNCT06757829What this trial is testingPulmonary Functions in Sickle Cell Disease: Response to Acu-TENSWho this might be right forSickle Cell Disease Cairo University 40
Large-scale testing (Phase 3)Study completedNCT05253781What this trial is testingLow Dose Aspirin for Preventing Intrauterine Growth Restriction and Preeclampsia in Sickle Cell Pregnancy (PIPSICKLE)Who this might be right forIntrauterine Growth RestrictionPreeclampsiaSickle Cell Disease+1 more University of Lagos, Nigeria 476
Testing effectiveness (Phase 2)Study completedNCT00229619What this trial is testingRituximab to Treat Moderate Aplastic Anemia, Pure Red Cell Aplasia, or Diamond Blackfan AnemiaWho this might be right forAnemia, AplasticRed-Cell Aplasia, PureAnemia, Diamond-Blackfan National Heart, Lung, and Blood Institute (NHLBI) 11
Testing effectiveness (Phase 2)Active Not RecruitingNCT04248439What this trial is testingGene Therapy for Fanconi Anemia, Complementation Group AWho this might be right forFanconi Anemia Complementation Group A Rocket Pharmaceuticals Inc. 5
Testing effectiveness (Phase 2)Study completedNCT03041909What this trial is testingAn Extension Study to Further Evaluate the Safety, Tolerability of GBT440 in Patients With Sickle Cell Disease Who Participated in the Study GBT440-001Who this might be right forSickle Cell Disease Global Blood Therapeutics 5
Not applicableStudy completedNCT03462511What this trial is testingHydroxyurea Adherence for Personal Best in Sickle Cell Disease (HABIT): Efficacy TrialWho this might be right forSickle Cell Disease Columbia University 50
Testing effectiveness (Phase 2)Study completedNCT02797964What this trial is testingA Phase 1/2 Trial of SRA737 in Subjects With Advanced CancerWho this might be right forAdvanced Solid Tumors or Non-Hodgkin's Lymphoma (NHL) Sierra Oncology LLC - a GSK company 107
Not applicableLooking for participantsNCT06887907What this trial is testingPhenotypic and Transcriptomic Description of Megakaryocytes in Sickle Cell PatientWho this might be right forSickle Cell Disease (SCD) University Hospital, Toulouse 40
Not applicableLooking for participantsNCT07776444What this trial is testingCerebrovascular Reactivity Measurements With High-Density Diffuse Optical TomographyWho this might be right forSickle Cell DiseaseCerebral Stroke Washington University School of Medicine 120
Early research (Phase 1)Study completedNCT00744692What this trial is testingReduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant DisordersWho this might be right forNon Malignant DisordersImmunodeficienciesCongenital Marrow Failures+5 more Duke University 22
Not applicableEnrolling By InvitationNCT07527975What this trial is testingLong-Term Follow-up: Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of RP-L102Who this might be right forFanconi Anemia Rocket Pharmaceuticals Inc. 14
Not applicableStudy completedNCT03687567What this trial is testingA Retrospective Study on the Effect of HBA or HBB Genetic Defects on Early Embryonic DevelopmentWho this might be right forThalassemia,Embryonic Development,Reproductive Sterility and Infertility Reproductive & Genetic Hospital of CITIC-Xiangya 737