Not applicableEnrolling By InvitationNCT04574076What this trial is testingA Study Following Males With Haemophilia A on Prophylaxis With Esperoct®Who this might be right forHaemophilia A Novo Nordisk A/S 60
Not applicableUnknownNCT06104826What this trial is testingHealth-Related Quality of Life Outcomes and Bleeding Rates Among Patients With Severe Hemophilia A on EmicizumabWho this might be right forHemophilia A Newark Beth Israel Medical Center 50
Large-scale testing (Phase 3)Study completedNCT00157040What this trial is testingStudy of Pharmacokinetics, Efficacy, and Safety of a Recombinant and Protein-Free Factor VIII (rAHF-PFM) in Pediatric Patients With Hemophilia AWho this might be right forHemophilia A Baxalta now part of Shire 50
Not applicableStudy completedNCT00932555What this trial is testingEffeKt Taiwan- Efficacy and Safety of Long-term Treatment With KOGENATE® FS in TaiwanWho this might be right forHemophilia A Bayer 82
Not applicableStudy completedNCT01953016What this trial is testingParticipation in a Research Registry for Immune DisordersWho this might be right forPrimary ImmunodeficienciesAPECEDCGD+2 more National Human Genome Research Institute (NHGRI) 716
Not applicableStudy completedNCT00386048What this trial is testingPain Management Protocol for Pediatric Sickle Cell DiseaseWho this might be right forSickle Cell Disease University of South Carolina 50
Testing effectiveness (Phase 2)Study completedNCT00003408What this trial is testingBiological Therapy Following Chemotherapy and Peripheral Stem Cell Transplantation in Treating Patients With CancerWho this might be right forBreast CancerChronic Myeloproliferative DisordersGestational Trophoblastic Tumor+9 more Cancer Treatment Centers of America 40
Not applicableStudy completedNCT02143076What this trial is testingMedication Adherence in Youth With Sickle Cell Disease (SCD)Who this might be right forSickle Cell Disease St. Jude Children's Research Hospital 36
Not applicableEnded earlyNCT00255684What this trial is testingFludarabine, Cyclophosphamide, and Total-Body Irradiation Followed by Cyclosporine and Mycophenolate Mofetil in Treating Patients Who Are Undergoing a Donor Umbilical Cord Blood Transplant for Hematologic CancerWho this might be right forChronic Myeloproliferative DisordersGraft Versus Host DiseaseLeukemia+4 more University of Rochester 16
Not applicableUnknownNCT01242878What this trial is testingMACS Study - Microparticles and Coagulation in Sickle Cell DiseaseWho this might be right forSickle Cell Disease University College, London 360
Testing effectiveness (Phase 2)Ended earlyNCT01601340What this trial is testingEffects of HQK-1001 in Patients With Sickle Cell DiseaseWho this might be right forSickle Cell DiseaseSickle Cell AnemiaSickle Cell Disorders+2 more HemaQuest Pharmaceuticals Inc. 77
Testing effectiveness (Phase 2)Looking for participantsNCT07681089What this trial is testingFoscenvivint in Liver Cirrhosis Patients Caused by HIV/HCV Co-infection With HemophiliaWho this might be right forLiver Cirrhosis Kiminori Kimura, MD 4
Post-approval studies (Phase 4)Active Not RecruitingNCT05891249What this trial is testingEvaluate the Safety and Effectiveness of Luspatercept for the Treatment of Transfusion-dependent (TD) Anemia Associated With Myelodysplastic Syndromes (MDS) & Beta-thalassemia (β-Thal) in IndiaWho this might be right forAnemia Bristol-Myers Squibb 85
Post-approval studies (Phase 4)UnknownNCT06320626What this trial is testingPharmacokinetic-guided Dosing of EmicizumabWho this might be right forHemophilia A With InhibitorHemophilia A Without InhibitorHemophilia A, Severe+3 more Kathelijn Fischer 95
Early research (Phase 1)Study completedNCT01848925What this trial is testingStudy of SANGUINATE™ Versus Hydroxyurea in Sickle Cell Disease (SCD) PatientsWho this might be right forSickle Cell Disease Prolong Pharmaceuticals 24
Not applicableUnknownNCT04706585What this trial is testingThalassemia Knowledge in Young People of IndonesiaWho this might be right forThalassemia Fakultas Kedokteran Universitas Indonesia 1,010
Early research (Phase 1)Ended earlyNCT02678143What this trial is testingNonmyeloablative Conditioning for Mismatched Hematopoietic Stem Cell Transplantation for Severe Sickle Cell DiseaseWho this might be right forSickle Cell Disease Washington University School of Medicine 1
Large-scale testing (Phase 3)Study completedNCT01863758What this trial is testingAssess the Safety and Efficacy of Individually Tailored Prophylaxis With Human-cl rhFVIII in Patients With Severe Haemophilia AWho this might be right forSevere Haemophilia A Octapharma 66
Not applicableStudy completedNCT00456443What this trial is testingInvasive Infections in Children With HemoglobinopathiesWho this might be right forThalassemiaSickle Cell Anemia HaEmek Medical Center, Israel 200
Not applicableStudy completedNCT03311243What this trial is testingPeriodontal Therapy in Thalassemia Major PatientsWho this might be right forThalassemia MajorChronic Periodontitis King Saud University 52