Early research (Phase 1)Not Yet RecruitingNCT03961243What this trial is testingLentiviral FIX Gene TherapyWho this might be right forHemophilia B Shenzhen Geno-Immune Medical Institute 10
Testing effectiveness (Phase 2)Study completedNCT01175785What this trial is testingInfusion of Off-the-Shelf Expanded Cord Blood Cells to Augment Cord Blood Transplant in Patients With Hematologic MalignanciesWho this might be right forAccelerated Phase Chronic Myelogenous LeukemiaAdult Acute Myeloid Leukemia in RemissionAdult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities+17 more Nohla Therapeutics, Inc. 15
Not applicableUnknownNCT05510518What this trial is testingLate Gestational Diabetes Mellitus Diagnosis in Obese WomenWho this might be right forGestational Diabetes Mellitus in PregnancyMacrosomia, FetalDystocia, Shoulder+5 more Western Galilee Hospital-Nahariya 150
Large-scale testing (Phase 3)Study completedNCT03984890What this trial is testingVitamin D3 For CGD Patients With BCGosis/ItisWho this might be right forVitamin D3Chronic-granulomatous DiseaseBCG Children's Hospital of Fudan University 50
Early research (Phase 1)WithdrawnNCT01851460What this trial is testingRadiofrequency Ablation for Liver Abscesses From Chronic Granulomatous DiseaseWho this might be right forChronic Granulomatous Diseases (CGD) and Liver Lesions National Institute of Allergy and Infectious Diseases (NIAID)
Not applicableUnknownNCT01446380What this trial is testingPhenotypic Expressions in a French Pseudoxanthoma-Elasticum CohortWho this might be right forPseudoxanthoma Elasticum University Hospital, Angers 350
Post-approval studies (Phase 4)UnknownNCT02999308What this trial is testingA Clinical Phenotype Based Individualized Prophylaxis in Chinese Hemophilia A ChildrenWho this might be right forHaemophilia Beijing Children's Hospital 40
Testing effectiveness (Phase 2)UnknownNCT04614610What this trial is testingLidocaine Intravenous in the Emergency Department For Sickle Cell CrisisWho this might be right forSickle Cell DiseaseSickle Cell CrisisPain, Acute Community Medical Center, Toms River, NJ 100
Not applicableStudy completedNCT00736060What this trial is testingClinical and Laboratory Characteristics of Sickle Cell Anemia Patients Admitted With FeverWho this might be right forSickle Cell AnemiaSickle Cell Thalassemia HaEmek Medical Center, Israel 60
Not applicableStudy completedNCT03179748What this trial is testingStudy Investigating Novoeight®/NovoEight® (Turoctocog Alfa) in Mexican Haemophilia A PatientsWho this might be right forCongenital Bleeding DisorderHaemophilia A Novo Nordisk A/S 10
Large-scale testing (Phase 3)Ended earlyNCT03933397What this trial is testingComparing Individualized vs. Weight Based Protocols to Treat Vaso-Occlusive Episodes in Sickle Cell DiseaseWho this might be right forSickle Cell Disease Duke University 328
Not applicableStudy completedNCT06281340What this trial is testingChanges in Intra-articular Parameters by Doppler Ultrasound in Patients With Hemophilic Ankle ArthropathyWho this might be right forHemophilia Investigación en Hemofilia y Fisioterapia 20
Not applicableLooking for participantsNCT06646640What this trial is testingLong Term Follow-Up Study for Individuals With Hemoglobin Disorders After Hematopoietic Cell Transplant or Gene TherapyWho this might be right forHemoglobin Disorder St. Jude Children's Research Hospital 200
Large-scale testing (Phase 3)Study completedNCT00393250What this trial is testingHypnosis to Manage Pain and Symptoms in Patients With Sickle Cell DiseaseWho this might be right forSickle Cell DiseasePain Management National Institutes of Health Clinical Center (CC) 31
Early research (Phase 1)Looking for participantsNCT06647979What this trial is testingHematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-HemoglobinopathiesWho this might be right forSickle Cell DiseaseSickle Cell Anemia (HbSS, or HbSβ-thalassemia0)Beta-Thalassemia+1 more Daniel Bauer 10
Testing effectiveness (Phase 2)Study completedNCT00049179What this trial is testingS0117 Gemtuzumab Ozogamicin Plus Cytarabine in Treating Patients With Relapsed Acute Myeloid LeukemiaWho this might be right forLeukemia SWOG Cancer Research Network 33
Not applicableStudy completedNCT00005893What this trial is testingStudy of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic DisordersWho this might be right forNeutropeniaSickle Cell AnemiaThalassemia Major+1 more Fairview University Medical Center
Large-scale testing (Phase 3)Study completedNCT00866606What this trial is testingStudy Evaluating On-Demand Treatment With BeneFIX In Chinese SubjectsWho this might be right forHemophilia B Wyeth is now a wholly owned subsidiary of Pfizer 35
Not applicableActive Not RecruitingNCT06285604What this trial is testingEffect Evaluation of Different Blood Products Infusion on Neonatal AnemiaWho this might be right forNeonatal Anemia Women's Hospital School Of Medicine Zhejiang University 200
Not applicableNot Yet RecruitingNCT06583304What this trial is testingHematological Indices in Pediatric Diagnosed With Familial Mediterranean FeverWho this might be right forFamilial Mediterranean Fever (FMF ) Assiut University 93