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Results for “Dyskeratosis-congenita”

20 trials

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Showing 20 of 20 results

Testing effectiveness (Phase 2)Active Not RecruitingNCT01659606
What this trial is testing

Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita

Who this might be right for
Dyskeratosis CongenitaHoyeraal Hreidarsson SyndromeRevesz Syndrome+1 more
Boston Children's Hospital 40
Not applicableStudy completedNCT04959188
What this trial is testing

Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD)

Who this might be right for
Dyskeratosis CongenitaTelomere Biology Disorders
National Cancer Institute (NCI) 53
Not applicableStudy completedNCT00499070
What this trial is testing

Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment

Who this might be right for
Dyskeratosis CongenitaFanconi AnemiaMyelodysplastic Syndromes+2 more
University Hospital Freiburg 119
Testing effectiveness (Phase 2)Ended earlyNCT01001598
What this trial is testing

Safety and Efficacy Trial of Danazol in Patients With Fanconi Anemia or Dyskeratosis Congenita

Who this might be right for
Fanconi AnemiaDyskeratosis Congenita
Boston Children's Hospital 5
Not applicableStudy completedNCT02162420
What this trial is testing

Hematopoietic Stem Cell Transplant for Dyskeratosis Congenita or Severe Aplastic Anemia

Who this might be right for
Dyskeratosis CongenitaAplastic Anemia
Masonic Cancer Center, University of Minnesota 61
Testing effectiveness (Phase 2)Looking for participantsNCT04232085
What this trial is testing

Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures

Who this might be right for
Primary Immune Deficiency DisorderImmune Deficiency DiseaseBone Marrow Failure+7 more
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins 27
Testing effectiveness (Phase 2)Study completedNCT00919503
What this trial is testing

Treosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited Disorders

Who this might be right for
Non-Neoplastic Hematologic and Lymphocytic Disorder
Fred Hutchinson Cancer Center 98
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Early research (Phase 1)Ended earlyNCT02231710
What this trial is testing

Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant Diseases

Who this might be right for
Primary Immune Deficiency DisordersHemophagocytic LymphohistiocytosisInherited Bone Marrow Failure Syndrome+2 more
Bellicum Pharmaceuticals 1
Not applicableAvailableNCT06731036
What this trial is testing

Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts

Who this might be right for
Severe Combined ImmunodeficiencyFanconi AnemiaDyskeratosis Congenita+1 more
University of Florida
Large-scale testing (Phase 3)Study completedNCT00455312
What this trial is testing

Stem Cell Transplant (SCT) for Dyskeratosis Congenita or SAA

Who this might be right for
Dyskeratosis CongenitaAplastic Anemia
Masonic Cancer Center, University of Minnesota 36
Testing effectiveness (Phase 2)Study completedNCT00004787
What this trial is testing

Phase II Pilot Study of Granulocyte Colony-Stimulating Factor for Inherited Bone Marrow Failure Syndromes

Who this might be right for
Shwachman SyndromeFanconi's AnemiaDyskeratosis Congenita+1 more
National Center for Research Resources (NCRR) 20
Early research (Phase 1)Study completedNCT01917708
What this trial is testing

Bone Marrow Transplant With Abatacept for Non-Malignant Diseases

Who this might be right for
Hurler SyndromeFanconi AnemiaGlanzmann Thrombasthenia+12 more
Emory University 10
Not applicableLooking for participantsNCT00027274
What this trial is testing

Cancer in Inherited Bone Marrow Failure Syndromes

Who this might be right for
Diamond Blackfan AnemiaDyskeratosis CongenitaFanconi Anemia+2 more
National Cancer Institute (NCI) 4,000
Not applicableLooking for participantsNCT02720679
What this trial is testing

Investigation of the Genetics of Hematologic Diseases

Who this might be right for
Bone Marrow Failure SyndromesErythrocyte DisorderLeukocyte Disorder+10 more
St. Jude Children's Research Hospital 1,716
Not applicableLooking for participantsNCT03050268
What this trial is testing

Familial Investigations of Childhood Cancer Predisposition

Who this might be right for
Acute LeukemiaAdenomatous PolyposisAdrenocortical Carcinoma+43 more
St. Jude Children's Research Hospital 1,500
Testing effectiveness (Phase 2)Ended earlyNCT04638517
What this trial is testing

The TELO-SCOPE Study: Attenuating Telomere Attrition With Danazol. Is There Scope to Dramatically Improve Health Outcomes for Adults and Children With Pulmonary Fibrosis

Who this might be right for
Pulmonary FibrosisTelomere ShorteningTelomere Disease+1 more
The University of Queensland 29
Early research (Phase 1)Looking for participantsNCT06817590
What this trial is testing

Nucleoside Therapy in Patients With Telomere Biology Disorders

Who this might be right for
Telomere Biology DisordersDyskeratosis CongenitaRevesz Syndrome+4 more
Suneet Agarwal 36
Testing effectiveness (Phase 2)Looking for participantsNCT03579875
What this trial is testing

Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders

Who this might be right for
Fanconi AnemiaSevere Aplastic AnemiaMyelodysplastic Syndromes+5 more
Masonic Cancer Center, University of Minnesota 48
Not applicableEnded earlyNCT01319851
What this trial is testing

Alefacept and Allogeneic Hematopoietic Stem Cell Transplantation

Who this might be right for
ThalassemiaSickle Cell DiseaseGlanzmann Thrombasthenia+10 more
Emory University 3