Early research (Phase 1)WithdrawnNCT02241928What this trial is testingStem Cell Therapy in Muscular DystrophyWho this might be right forMuscular Dystrophy Neurogen Brain and Spine Institute
Large-scale testing (Phase 3)Enrolling By InvitationNCT07008469What this trial is testingGlobal Open-Label Extension Study of Del-desiran for the Treatment of DM1Who this might be right forMyotonic Dystrophy Type 1DM1Myotonic Dystrophy+5 more Avidity Biosciences, Inc. 199
Not applicableNot Yet RecruitingNCT07732439What this trial is testingAn Ambispective Natural History Study in Myotonic Dystrophy Patients Linking Retrospective Data Captured From the DM-Scope Registry With a Prospective 24-month Follow-up PeriodWho this might be right forMyotonic Dystrophy 1Myotonic Dystrophy 2 Lupin Ltd. 100
Testing effectiveness (Phase 2)WithdrawnNCT02704325What this trial is testingGene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2Who this might be right forDuchenne Muscular Dystrophy Kevin Flanigan
Not applicableStudy completedNCT01990976What this trial is testingStudy of Morphology and Functional Magnetic Resonance Imaging (MRI) Muscle Patients With Muscular Dystrophy Type FSHD Benefiting a Physical Training Introduced.Who this might be right forMuscular DystrophyFacioscapulohumeral Centre Hospitalier Universitaire de Saint Etienne 15
Not applicableStudy completedNCT02815878What this trial is testingEnhance Wellness for Individuals With Long-Term Physical DisabilitiesWho this might be right forMultiple SclerosisMuscular DystrophyPost-polio Syndrome+1 more University of Washington 240
Not applicableUnknownNCT04967716What this trial is testingGenetics of Charcot-Marie-Tooth Dystrophy and Related DiseasesWho this might be right forPeroneal Muscular Atrophy Peking University Third Hospital 200
Not applicableLooking for participantsNCT06755138What this trial is testingResearch on the Relationship Between Scoliosis, Pain, Quality of Life, and Trunk Muscle Compensation Patterns Among Patients with Duchenne Muscular Dystrophy.Who this might be right forDuchenne Muscular Dystrophy (DMD) Seoul National University Hospital 30
Not applicableWithdrawnNCT02385162What this trial is testingBiomarker for Glycogen Storage Diseases (BioGlycogen)Who this might be right forFructose Metabolism, Inborn ErrorsGlycogen Storage DiseaseGlycogen Storage Disease Type I+7 more CENTOGENE GmbH Rostock
Early research (Phase 1)Study completedNCT06204809What this trial is testingSafety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy 1 PepGen Inc 24
Not applicableActive Not RecruitingNCT01851447What this trial is testingSkeletal Muscle Biomarkers in People With Fragile Sarcolemmal Muscular DystrophyWho this might be right forGenetic Disorder Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 11
Not applicableStudy completedNCT01098708What this trial is testingThis is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Washington University School of Medicine 50
Not applicableStudy completedNCT05945784What this trial is testingExploring Accessible Beauty for Individuals With Upper Extremity DeficitsWho this might be right forStroke, IschemicStroke HemorrhagicStroke (CVA) or TIA+11 more Casa Colina Hospital and Centers for Healthcare 57
Not applicableStudy completedNCT01066455What this trial is testingCardiac Outcome Measures in Children With Muscular DystrophyWho this might be right forDuchenne Muscular DystrophyBecker Muscular DystrophyLimb Girdle Muscular Dystrophy Cooperative International Neuromuscular Research Group 48
Not applicableLooking for participantsNCT06756633What this trial is testingRespiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular DiseasesWho this might be right forNeuromuscular Diseases in ChildrenRespiratory Function ImpairedRespiratory Insufficiency+3 more Lokman Hekim University 42
Not applicableLooking for participantsNCT00138931What this trial is testingGenetics of Cardiovascular and Neuromuscular DiseaseWho this might be right forCardiomyopathyArrhythmiaMuscular Dystrophy University of Chicago 2,000
Testing effectiveness (Phase 2)Study completedNCT03333590What this trial is testingGene Transfer Clinical Trial to Deliver rAAVrh74.MCK.GALGT2 for Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Kevin Flanigan 2
Not applicableStudy completedNCT01638169What this trial is testingThe Contribution of Heels for Walking Quality Among Children With Muscular DystrophyWho this might be right forStep Time and LengthSymmetryStep Time and Length Variability+2 more Alyn Pediatric & Adolescent Rehabilitation Hospital 11
Not applicableLooking for participantsNCT07378553What this trial is testingMultiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular DystrophiesWho this might be right forDuchene Muscular DystrophyBecker Muscular Dystrophy Nantes University Hospital 60
Testing effectiveness (Phase 2)Study completedNCT04129294What this trial is testingExploratory Study of NS-089/NCNP-02 in DMDWho this might be right forDuchenne Muscular Dystrophy National Center of Neurology and Psychiatry, Japan 6