Not applicableLooking for participantsNCT06843330What this trial is testingAccuracy of Lactate Meter in GSDIaWho this might be right forGlycogen Storage Disease Type Ia Connecticut Children's Medical Center 10
Not applicableLooking for participantsNCT06396546What this trial is testing'Glycogen Storage Diseases (GSDs) in Indian Children- Establishing an Indian GSD (I-GSD) Registry'Who this might be right forGlycogen Storage Diseases Institute of Liver and Biliary Sciences, India 250
Not applicableWithdrawnNCT02385162What this trial is testingBiomarker for Glycogen Storage Diseases (BioGlycogen)Who this might be right forFructose Metabolism, Inborn ErrorsGlycogen Storage DiseaseGlycogen Storage Disease Type I+7 more CENTOGENE GmbH Rostock
Large-scale testing (Phase 3)Active Not RecruitingNCT05139316What this trial is testingAdeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia (GSDIa)Who this might be right forGlycogen Storage Disease Type IA Ultragenyx Pharmaceutical Inc 49
Not applicableStudy completedNCT02176096What this trial is testingComparison of the Effect of a Novel Starch (Glycosade) Versus Gastrostomy Tube-Dextrose Infusion on Overnight Euglycaemia Control in Children With Glycogen Storage Disease Type I: Open Label Demonstration TrialWho this might be right forGlycogen Storage Disorder Type 1HypoglycemiaCornstarch+1 more University of Manitoba 4
Not applicableStudy completedNCT03871673What this trial is testingThe Use of Uncooked Sweet Manioc Starch to Treat Hepatic Glycogen Storage DiseasesWho this might be right forGlycogen Storage Disease Type I Hospital de Clinicas de Porto Alegre 11
Not applicableStudy completedNCT03970278What this trial is testingStudy of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type IaWho this might be right forGlycogen Storage Disease Type IAVon Gierke's Disease (GSD Type Ia) Ultragenyx Pharmaceutical Inc 12
Testing effectiveness (Phase 2)Active Not RecruitingNCT05095727What this trial is testingMRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)Who this might be right forGlycogen Storage Disease ModernaTX, Inc. 15
Not applicableStudy completedNCT03218904What this trial is testingGlycogen Storage Disease Breath Test StudyWho this might be right forPatient ComplianceHealthy University of British Columbia 14
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Testing effectiveness (Phase 2)UnknownNCT04930627What this trial is testingSafety and Efficacy of Empagliflozin in GSD1b Patients With NeutropeniaWho this might be right forGlucose 6 Phosphatase Deficiency Children's Memorial Health Institute, Poland 20
Not applicableLooking for participantsNCT06636383What this trial is testingGlycogen Storage Disease Type Ia (GSDIa) Disease Monitoring ProgramWho this might be right forGlycogen Storage Disease Type Ia Ultragenyx Pharmaceutical Inc 140
Not applicableStudy completedNCT01961076What this trial is testingOvernight Feeding Study in Glycogen Storage Disease Type 1Who this might be right forGlycogen Storage Disease Type 1 (GSD 1) University of Zurich 5
Not applicableLooking for participantsNCT06852612What this trial is testingDietary Treatment Strategies and Metabolic Control in Glycogen Storage Disease Type IWho this might be right forGlycogen Storage Disease Type I Insel Gruppe AG, University Hospital Bern 20
Testing effectiveness (Phase 2)Study completedNCT03517085What this trial is testingSafety and Dose-Finding Study of DTX401 (AAV8G6PC) in Adults With Glycogen Storage Disease Type Ia (GSDIa)Who this might be right forGSD1 Ultragenyx Pharmaceutical Inc 12
Very early researchStudy completedNCT03665636What this trial is testingAnaplerotic Therapy Using Triheptanoin for Patients With Glycogen Storage Disease Type IWho this might be right forGlycogen Storage Disease Type I Areeg El-Gharbawy 4
Testing effectiveness (Phase 2)UnknownNCT04138251What this trial is testingSafety, Efficacy Evaluation of Empagliflozin Administration for Neutropenia in Glycogenosis Type 1b and G6PC3 DeficiencyWho this might be right forGlycogen Storage Disease Type IGlucose 6 Phosphatase Deficiency Cliniques universitaires Saint-Luc- Université Catholique de Louvain 5