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Results for “Glycogen Storage Disease Type II (GSD-II)”

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Showing 20 of 0 results

Not applicableLooking for participantsNCT00567073
What this trial is testing

Pompe Pregnancy Sub-Registry

Who this might be right for
Glycogen Storage Disease Type II (GSD-II)Pompe Disease (Late-onset)Glycogenesis 2 Acid Maltase Deficiency
Genzyme, a Sanofi Company 20
Not applicableUnknownNCT02527239
What this trial is testing

Prevalence of Pompe's Disease in Respiratory Clinics

Who this might be right for
Pompe's Disease
Royal Brompton & Harefield NHS Foundation Trust 400
Testing effectiveness (Phase 2)Study completedNCT02140151
What this trial is testing

Prophylactic Ranibizumab for Exudative Age-related Macular Degeneration

Who this might be right for
Age-related Macular Degeneration
Southern California Desert Retina Consultants, MC 108
Testing effectiveness (Phase 2)Study completedNCT00053573
What this trial is testing

RhGAA in Patients With Infantile-onset Glycogen Storage Disease-II (Pompe Disease)

Who this might be right for
Glycogen Storage Disease Type IIPompe DiseaseAcid Maltase Deficiency Disease+1 more
Genzyme, a Sanofi Company 20
Large-scale testing (Phase 3)Active Not RecruitingNCT03911505
What this trial is testing

ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD

Who this might be right for
Pompe Disease (Late-onset)
Amicus Therapeutics 21
Not applicableEnded earlyNCT02191917
What this trial is testing

Respiratory Muscle Strength in Patients With Late-onset Pompe Disease (LOPD)

Who this might be right for
Late-onset Pompe Disease
BioMarin Pharmaceutical 8
Early research (Phase 1)Study completedNCT01859624
What this trial is testing

Albuterol in Individuals With Late Onset Pompe Disease (LOPD)

Who this might be right for
Pompe Disease
Duke University 8
Not applicableStudy completedNCT05083806
What this trial is testing

MSOT in Pompe Disease

Who this might be right for
Pompe DiseasePompe Disease (Late-onset)Pompe's Disease Juvenile Onset+1 more
University of Erlangen-Nürnberg Medical School 20
Testing effectiveness (Phase 2)Study completedNCT01885936
What this trial is testing

Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease

Who this might be right for
Pompe Disease
Duke University 16
Early research (Phase 1)Study completedNCT02240407
What this trial is testing

Re-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe Disease

Who this might be right for
Pompe Disease
University of Florida 2
Not applicableStudy completedNCT02354664
What this trial is testing

Dynamic Respiratory Muscle Function in Late-Onset Pompe Disease

Who this might be right for
Pompe Disease
University of Florida 14
Post-approval studies (Phase 4)Study completedNCT02405598
What this trial is testing

Evaluation of Salbutamol as an Adjuvant Therapy for Pompe Disease

Who this might be right for
Pompe Disease
National Taiwan University Hospital 14
Not applicableStudy completedNCT02801539
What this trial is testing

Respiratory Muscle Training in L-Onset Pompe Disease (LOPD)

Who this might be right for
Glycogen Storage Disease Type II
Duke University 22
Testing effectiveness (Phase 2)Study completedNCT00763932
What this trial is testing

Extension Study of Long-term Safety and Efficacy of Myozyme in Patients With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored Enzyme Replacement Therapy (ERT) Studies

Who this might be right for
Pompe Disease Infantile-OnsetGlycogen Storage Disease Type II
Genzyme, a Sanofi Company 7
Not applicableLooking for participantsNCT02399748
What this trial is testing

A Long-term Study for the Outcome of Pompe Disease

Who this might be right for
Pompe Disease
National Taiwan University Hospital 50
Not applicableEnded earlyNCT00277979
What this trial is testing

3D Echocardiography Managing Infantile Pompe's Disease

Who this might be right for
Congenital Disorders
Children's Healthcare of Atlanta 2
Testing effectiveness (Phase 2)Study completedNCT00467935
What this trial is testing

Scotoma Reduction in AMD Patients Treated With Ranibizumab

Who this might be right for
Macular Degeneration
Retina Research Foundation 20
Post-approval studies (Phase 4)Active Not RecruitingNCT05164055
What this trial is testing

Avalglucosidase Alfa French Post-trial Access for Participants With Pompe Disease (PTA Avalglucosidase)

Who this might be right for
Glycogen Storage Disease Type II
Genzyme, a Sanofi Company 17
Not applicableUnknownNCT06539169
What this trial is testing

FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

Who this might be right for
Alpha-ThalassemiaBeta-ThalassemiaAmyloidosis+14 more
xCures 1,000
Not applicableStudy completedNCT02654886
What this trial is testing

Safety and Effectiveness of Resistance Exercise Training in Patients With Pompe Disease.

Who this might be right for
Pompe DiseaseMuscle Weakness
University of California, Irvine 10
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