Not applicableStudy completedNCT00519701What this trial is testingHydroxyurea in Young Children With Sickle Cell AnemiaWho this might be right forSickle Cell Anemia Duke University 14
Not applicableWithdrawnNCT04541875What this trial is testingMedication Adherence and Non-adherence in Adults With Rare DiseaseWho this might be right forCystic FibrosisHemophilia AHemophilia B+3 more Xperiome
Testing effectiveness (Phase 2)Study completedNCT03842189What this trial is testingEvaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of M281 Administered to Pregnant Women at High Risk for Early Onset Severe Hemolytic Disease of the Fetus and Newborn (HDFN)Who this might be right forHemolytic Disease of the Fetus and Newborn Janssen Research & Development, LLC 25
Not applicableLooking for participantsNCT04218318What this trial is testingSafe Threshold to Discontinue Phototherapy in Hemolytic Disease of NewbornWho this might be right forHemolytic Disease of NewbornNeonatal Hyperbilirubinemia Ministry of Health, Saudi Arabia 84
Not applicableStudy completedNCT03167450What this trial is testingExamining the Knowledge, Attitudes, and Beliefs of Sickle Cell Disease Patients, Parents of Patients With Sickle Cell Disease, and Providers Towards the Integration of CRISPR in Clinical CareWho this might be right forSickle Cell Disease National Human Genome Research Institute (NHGRI) 109
Not applicableLooking for participantsNCT06734520What this trial is testingClinical Study of Super Transplantation in the Treatment of Severe β-thalassemiaWho this might be right forThalassemia Majors (Beta-Thalassemia Major)Haplo-identical Donors Guangzhou Women and Children's Medical Center 3
Testing effectiveness (Phase 2)Looking for participantsNCT06481306What this trial is testingEvaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell DiseaseWho this might be right forAnemia, Sickle CellHealthy Volunteers Bristol-Myers Squibb 224
Large-scale testing (Phase 3)Study completedNCT07210450What this trial is testingEffect of L-Glutamine on Pulmonary Artery Pressure in Patients With Non-Transfusion-Dependent ThalassemiaWho this might be right forPulmonary Artery PressureThalassemiaNon-transfusion Dependent Thalassemia Mazandaran University of Medical Sciences 8
Not applicableStudy completedNCT04582110What this trial is testingThe Role of OCTA in Patients Affected by Beta ThalassemiaWho this might be right forThalassemia Federico II University 82
Not applicableUnknownNCT02474420What this trial is testingAmlodipine as Adjuvant Treatment to Iron Chelation for Prevention of Cardiac Iron Overload in Thalassemia PatientsWho this might be right forBeta-ThalassemiaIron Overload Kevin H.M. Kuo, MD, MSc, FRCPC 60
Testing effectiveness (Phase 2)Study completedNCT03653247What this trial is testingAssess the Safety, Tolerability, and Efficacy of BIVV003 for Autologous Hematopoietic Stem Cell Transplantation in Patients With Severe Sickle Cell DiseaseWho this might be right forSickle Cell Disease Sangamo Therapeutics 7
Large-scale testing (Phase 3)Looking for participantsNCT07247188What this trial is testingStudy of a Single Dose of a 21-valent Pneumococcal Conjugate Vaccine in Children and Adolescents With Sickle Cell DiseaseWho this might be right forSickle Cell Disease Sanofi 100
Testing effectiveness (Phase 2)Study completedNCT00879242What this trial is testingEffect of Deferasirox on Patients With Cardiac MRI T2* < 20 MsecWho this might be right forBeta Thalassemia Transfusion Dependent Novartis Pharmaceuticals 20
Large-scale testing (Phase 3)Study completedNCT00560261What this trial is testingEvaluation of the Lung Capillary Blood Volume in Children With Sickle Cell DiseaseWho this might be right forSickle Cell Disease Assistance Publique - Hôpitaux de Paris 120
Large-scale testing (Phase 3)Study completedNCT02174900What this trial is testingSafety of Primaquine + Artemether-lumefantrine in G6PD Deficient Males With an Asymptomatic Malaria Infection (SAFEPRIM)Who this might be right forMalaria London School of Hygiene and Tropical Medicine 70
Not applicableStudy completedNCT02316366What this trial is testingThe Use of Warmed Saline in Vaso-occlusive EpisodesWho this might be right forSickle Cell DiseaseSickle Cell Crisis Nationwide Children's Hospital 80
Testing effectiveness (Phase 2)Study completedNCT01119833What this trial is testingStudy of GMI-1070 for the Treatment of Sickle Cell Pain CrisisWho this might be right forSickle Cell DiseaseVaso-occlusive CrisisPain Crisis GlycoMimetics Incorporated 81
Post-approval studies (Phase 4)Study completedNCT01609192What this trial is testingFuture of Spermatogenesis in Men With Sickle Cell Disease Medically TreatedWho this might be right forDrepanocytic Men Treated by Hydroxyurea for the First Time Assistance Publique - Hôpitaux de Paris 50
Testing effectiveness (Phase 2)Study completedNCT00094887What this trial is testingNitric Oxide Inhalation to Treat Sickle Cell Pain CrisesWho this might be right forAnemia, Sickle Cell Mallinckrodt 150
Not applicableUnknownNCT04264871What this trial is testingIs the Preoperative Preparation of Sickle Cell Patients Optimal: Assessment of Practices and Post-operative ComplicationsWho this might be right forSickle Cell Disease Queen Fabiola Children's University Hospital 250