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Results for “Hereditary Blood Disorders”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Study completedNCT00410657
What this trial is testing

Alemtuzumab and Glucocorticoids in Treating Newly Diagnosed Acute Graft-Versus-Host Disease in Patients Who Have Undergone a Donor Stem Cell Transplant

Who this might be right for
Breast CancerChronic Myeloproliferative DisordersGestational Trophoblastic Tumor+9 more
Fred Hutchinson Cancer Center 53
Not applicableApproved For MarketingNCT05770219
What this trial is testing

Expanded Access Program of TAK-755 for Congenital Thrombotic Thrombocytopenic Purpura (cTTP)

Who this might be right for
Thrombotic Thrombocytopenic Purpura (TTP)
Takeda
Not applicableStudy completedNCT04584528
What this trial is testing

Implementing an Individualized Pain Plan (IPP) for ED Treatment of VOE's in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseGenetic DiseaseHematologic Diseases+1 more
Duke University 279
Large-scale testing (Phase 3)Study completedNCT01175083
What this trial is testing

Immunization of Children Between 8 Weeks and 2 Years of Age With GSK Pneumococcal Vaccine GSK1024850A

Who this might be right for
Infections, Streptococcal
GlaxoSmithKline 300
Not applicableLooking for participantsNCT04728841
What this trial is testing

Gene Therapy for Chinese Hemophilia A

Who this might be right for
Hemophilia AGene Therapy
Institute of Hematology & Blood Diseases Hospital, China 12
Not applicableStudy completedNCT00408681
What this trial is testing

Lithium Carbonate in Treating Patients With Acute Intestinal Graft-Versus-Host-Disease (GVHD) After Donor Stem Cell Transplant

Who this might be right for
Accelerated Phase Chronic Myelogenous LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+111 more
Fred Hutchinson Cancer Center 20
Not applicableStudy completedNCT01873183
What this trial is testing

Perioperative Fluid Management in Morbidly Obese Patients

Who this might be right for
HypotensionAnomaly; Venous ReturnDehydration
Umeå University 50
Not applicableEnrolling By InvitationNCT06816953
What this trial is testing

Cartilage Biomarkers and HEAD-US Score in Severe Hemophilia A Patients Receiving FVIII Prophylaxis

Who this might be right for
Hemophilia A
Chulalongkorn University 19
Not applicableStudy completedNCT01755455
What this trial is testing

Does a Daily Iron Tablet Improve Anemia in Cystic Fibrosis

Who this might be right for
Cystic FibrosisAnemia, Iron-Deficiency
Dartmouth-Hitchcock Medical Center 22
Testing effectiveness (Phase 2)Looking for participantsNCT05735717
What this trial is testing

MT2021-08T Cell Receptor Alpha/Beta Depletion PBSC Transplantation for Heme Malignancies

Who this might be right for
Hematologic MalignancyAcute LeukemiaRemission+21 more
Masonic Cancer Center, University of Minnesota 70
Testing effectiveness (Phase 2)Ended earlyNCT00392782
What this trial is testing

Donor Stem Cell Transplant in Treating Patients With Myeloid Cancer or Other Disease

Who this might be right for
LeukemiaMyelodysplastic Syndromes
Masonic Cancer Center, University of Minnesota 24
Early research (Phase 1)Study completedNCT02497924
What this trial is testing

The Absorption, Metabolism, and Excretion of GBT440 in Healthy Male Subjects

Who this might be right for
Anemia, Sickle Cell
Global Blood Therapeutics 7
Not applicableUnknownNCT05105659
What this trial is testing

Assessment of Cognitive Functions, Psychological Symptoms, and Quality of Life Among B Thalassemia Patients and Their Clinical Correlates.

Who this might be right for
B Thalassemia
Assiut University 60
Testing effectiveness (Phase 2)Study completedNCT01749540
What this trial is testing

Study to Evaluate the Safety and Efficacy of Luspatercept (ACE-536) in Participants With Beta-thalassemia (A536-04/MK-6143-002)

Who this might be right for
B-Thalassemia
Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA 64
Not applicableUnknownNCT01608620
What this trial is testing

Meta-analyses of Total and Individual Fructose-containing Sugars and Incident Cardiometabolic Disease

Who this might be right for
OverweightObesityDyslipidemia+9 more
John Sievenpiper 1
Testing effectiveness (Phase 2)Study completedNCT01732718
What this trial is testing

Effect of Atorvastatin on Endothelial Dysfunction and Albuminuria in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseSickle Cell Nephropathy
University of North Carolina, Chapel Hill 13
Not applicableActive Not RecruitingNCT03412760
What this trial is testing

Hydrops: Diagnosing & Redefining Outcomes With Precision Study

Who this might be right for
Hydrops FetalisBirth DefectFetal Anomaly
University of California, San Francisco 500
Early research (Phase 1)Study completedNCT03329950
What this trial is testing

CDX-1140 (CD40) as Monotherapy or in Combination in Patients With Advanced Malignancies

Who this might be right for
MelanomaNon-small Cell Lung CancerBreast Cancer+23 more
Celldex Therapeutics 132
Early research (Phase 1)Looking for participantsNCT05709288
What this trial is testing

Gene Therapy for Hemophilia B Patients Aged 12-18 Years Old

Who this might be right for
Hemophilia B
Institute of Hematology & Blood Diseases Hospital, China 9
Testing effectiveness (Phase 2)Study completedNCT02961218
What this trial is testing

Study of Efficacy, Safety and Tolerability of ACZ885 (Canakinumab) in Pediatric and Young Adult Patients With Sickle Cell Anemia

Who this might be right for
Sickle Cell Anemia
Novartis Pharmaceuticals 49
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