Early research (Phase 1)Active Not RecruitingNCT05876780
What this trial is testing
A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)
Who this might be right for
Limb Girdle Muscular Dystrophy
Sarepta Therapeutics, Inc. 6