Testing effectiveness (Phase 2)Study completedNCT06304064What this trial is testingHalt cardiomyOPathy progrEssion in Duchenne (HOPE-OLE)Who this might be right forDuchenne Muscular Dystrophy Capricor Inc. 8
Not applicableLooking for participantsNCT04003363What this trial is testingThe United Kingdom National Registry for Myotonic DystrophyWho this might be right forMyotonic Dystrophy Newcastle University 900
Not applicableUnknownNCT04967716What this trial is testingGenetics of Charcot-Marie-Tooth Dystrophy and Related DiseasesWho this might be right forPeroneal Muscular Atrophy Peking University Third Hospital 200
Large-scale testing (Phase 3)Ended earlyNCT03439514What this trial is testingARRY-371797 (PF-07265803) in Patients With Symptomatic Dilated Cardiomyopathy Due to a Lamin A/C Gene MutationWho this might be right forDilated CardiomyopathyLamin A/C Gene Mutation Pfizer 77
Not applicableUnknownNCT06378216What this trial is testingMyotonic Dystrophy Type 1 Congenital and Juvenile Form: From Diagnosis to Rehabilitation [MDCJ-NeuBeRe]Who this might be right forMyotonic Dystrophy 1 IRCCS Eugenio Medea 30
Not applicableStudy completedNCT01116570What this trial is testingPhysical Training Introduction in Lifestyle of Facioscapulohumeral Dystrophy PatientsWho this might be right forMuscular Dystrophy, Facioscapulohumeral Centre Hospitalier Universitaire de Saint Etienne 15
Large-scale testing (Phase 3)Ended earlyNCT05397470What this trial is testingEfficacy and Safety of Losmapimod in Treating Participants With Facioscapulohumeral Muscular Dystrophy (FSHD) (REACH)Who this might be right forFacioscapulohumeral Muscular Dystrophy (FSHD) Fulcrum Therapeutics 260
Not applicableActive Not RecruitingNCT05072288What this trial is testingA Remote Physical Activity Program in the Population Suffering from Type 1 Myotonic DystrophyWho this might be right forMyotonic Dystrophy Type 1 (DM1) Université du Québec à Chicoutimi 40
Not applicableLooking for participantsNCT06094205What this trial is testingFeasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02)Who this might be right forAnarthriaDysarthriaTetraplegia+5 more Leigh R. Hochberg, MD, PhD. 2
Large-scale testing (Phase 3)Ended earlyNCT04371666What this trial is testingPhase 3 Trial of Pamrevlumab or Placebo With Systemic Corticosteroids in Participants With Non-ambulatory Duchenne Muscular Dystrophy (DMD)Who this might be right forDuchenne Muscular Dystrophy Kyntra Bio 98
Not applicableStudy completedNCT04616807What this trial is testingAn Observational Study in Adult Patients With Non-dystrophic Myotonic DisordersWho this might be right forMyotonic Dystrophy Lupin Ltd. 53
Not applicableStudy completedNCT04634682What this trial is testingEffect of MYODM on Quality of Life, Fatigue and Hypersomnia in Patients With Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy 1 Myogem Health Company, S.L. 30
Early research (Phase 1)Ended earlyNCT03362502What this trial is testingEvaluate the Safety and Tolerability of PF-06939926 Gene Therapy in Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Pfizer 23
Testing effectiveness (Phase 2)Enrolling By InvitationNCT07573631What this trial is testingAn Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of BMN 351 in Participants With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy (DMD) BioMarin Pharmaceutical 18
Not applicableStudy completedNCT03603171What this trial is testingClinical Outcome Measures in Myotonic Dystrophy Type 2Who this might be right forMyotonic Dystrophy Type 2 Prof. Dr. Benedikt Schoser 60
Testing effectiveness (Phase 2)Looking for participantsNCT06131983What this trial is testingStudy of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular Dystrophy Type 1Who this might be right forMuscular Dystrophy, Facioscapulohumeral Sarepta Therapeutics, Inc. 60
Early research (Phase 1)Active Not RecruitingNCT06114056What this trial is testingA Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)Who this might be right forDuchenne Muscular Dystrophy West China Hospital 3
Testing effectiveness (Phase 2)Study completedNCT02667483What this trial is testingStudy of DS-5141b in Patients With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Daiichi Sankyo Co., Ltd. 8
Early research (Phase 1)Study completedNCT02530905What this trial is testingDose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) PatientsWho this might be right forDuchenne Muscular Dystrophy Sarepta Therapeutics, Inc. 12
Not applicableLooking for participantsNCT00272883What this trial is testingMolecular and Genetic Studies of Congenital MyopathiesWho this might be right forCentral Core DiseaseCentronuclear MyopathyCongenital Fiber Type Disproportion+5 more Boston Children's Hospital 4,000