Not applicableAvailableNCT03863119What this trial is testingExpanded Access Protocol for Boys With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Santhera Pharmaceuticals
Not applicableStudy completedNCT05280730What this trial is testingAssessment of Neurodevelopmental Needs in Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Virginia Commonwealth University 50
Testing effectiveness (Phase 2)Ended earlyNCT02515669What this trial is testingStudy of an Investigational Drug, RO7239361 (BMS-986089), in Ambulatory Boys With DMDWho this might be right forMuscular Dystrophy (DMD) Hoffmann-La Roche 43
Large-scale testing (Phase 3)Active Not RecruitingNCT03992430What this trial is testingCompare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)Who this might be right forMuscular Dystrophy, Duchenne Sarepta Therapeutics, Inc. 160
Not applicableNot Yet RecruitingNCT06917430What this trial is testingMuscle MRI Outlining of Neuromuscular Diseases Using Artificial IntelligenceWho this might be right forBecker Muscular DystrophyFSHD - Facioscapulohumeral Muscular DystrophyHypokalemic Periodic Paralysis Rigshospitalet, Denmark 120
Not applicableLooking for participantsNCT07580365What this trial is testingVirtualPark_PediatricWho this might be right forDystrophinopathyMuscular DystrophiesCongenital Myopathies Istituto di Sistemi e Tecnologie Industriali Intelligenti per il Manifatturiero Avanzato 22
Early research (Phase 1)Study completedNCT02710500What this trial is testingRAAVrh74.MHCK7.DYSF.DV for Treatment of DysferlinopathiesWho this might be right forDysferlinopathy Sarepta Therapeutics, Inc. 2
Not applicableLooking for participantsNCT00390104What this trial is testingMolecular Analysis of Patients With Neuromuscular DiseaseWho this might be right forNeuromuscular; Disorder, HereditaryDuchenne/Becker Muscular DystrophyLimb-girdle Muscular Dystrophy Boston Children's Hospital 1,000
Not applicableEnded earlyNCT03531788What this trial is testingUse of Dynamic Arm Supports to Promote Activities of Daily Living in Individuals With DMDWho this might be right forDuchenne Muscular Dystrophy Roxanna Marie Bendixen 18
Not applicableStudy completedNCT05464446What this trial is testingExamination of Lower Urinary System Symptoms With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular DystrophyLower Urinary Tract SymptomsMuscle Weakness+4 more Lokman Hekim University 45
Not applicableLooking for participantsNCT02069756What this trial is testingThe Duchenne RegistryWho this might be right forDuchenne Muscular DystrophyBecker Muscular DystrophyDystrophinopathy+2 more The Duchenne Registry 10,000
Not applicableNot Yet RecruitingNCT06874166What this trial is testingSocial Cognition in Dystrophinopathies and Neurodevelopmental DisordersWho this might be right forDuchenne / Becker Muscular DystrophyOsteogenesis Imperfecta (OI)Social Cognition IRCCS Eugenio Medea 45
Not applicableWithdrawnNCT06270186What this trial is testingEvaluation of Cognitive Functions in 20 Patients With Type 1 Myotonic Dystrophy With Virtual Reality ApproachWho this might be right forMyotonic Dystrophy 1 Centre Hospitalier Universitaire de Nice
Very early researchActive Not RecruitingNCT06594094What this trial is testingAn Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its Long-Lasting Effects in DMD Patients (MUSCLE)Who this might be right forDuchenne Muscular Dystrophin (DMD) HuidaGene Therapeutics Co., Ltd. 4
Large-scale testing (Phase 3)WithdrawnNCT04700046What this trial is testingStudy to Investigate the Efficacy and Safety of Mexiletine in Patients With Myotonic Dystrophy Type 1 and Type 2Who this might be right forMyotonic Dystrophy Type 1 and Type 2 Lupin Ltd.
Not applicableNot Yet RecruitingNCT07664124What this trial is testingDigital Monitoring of Upper Limb Function in Non-Ambulant DMDWho this might be right forDuchenne Muscular Dystrophy (DMD) Centre Hospitalier Universitaire de Liege 50
Not applicableStudy completedNCT03424460What this trial is testingVenous Thromboembolism in Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy 1 Assistance Publique - Hôpitaux de Paris 130
Testing effectiveness (Phase 2)WithdrawnNCT04226924What this trial is testingTreatment of Oculopharyngeal Muscular Dystrophy With TrehaloseWho this might be right forOculopharyngeal Muscular Dystrophy Bioblast Pharma Ltd.
Not applicableLooking for participantsNCT06756633What this trial is testingRespiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular DiseasesWho this might be right forNeuromuscular Diseases in ChildrenRespiratory Function ImpairedRespiratory Insufficiency+3 more Lokman Hekim University 42
Not applicableStudy completedNCT07437378What this trial is testingRelation Between Muscle Architecture and Functional Ability in Children With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy (DMD)Neuromuscular DisordersMuscle Architecture Deraya University 26