Early research (Phase 1)Ended earlyNCT04800822What this trial is testingPF-07284892 in Participants With Advanced Solid TumorsWho this might be right forSolid Tumor Pfizer 53
Testing effectiveness (Phase 2)Study completedNCT01733407What this trial is testingL-Serine Supplementation in Hereditary Sensory Neuropathy Type 1Who this might be right forHereditary Sensory and Autonomic Neuropathy Type I Massachusetts General Hospital 18
Early research (Phase 1)Looking for participantsNCT03423628What this trial is testingAssess the Safety and Tolerability of AZD1390 Given With Radiation Therapy in Patients With Brain CancerWho this might be right forRecurrent Glioblastoma MultiformePrimary Glioblastoma MultiformeBrain Neoplasms, Malignant+1 more AstraZeneca 180
Large-scale testing (Phase 3)Study completedNCT00790400What this trial is testingEfficacy and Safety of RAD001 in Patients Aged 18 and Over With Angiomyolipoma Associated With Either Tuberous Sclerosis Complex (TSC) or Sporadic Lymphangioleiomyomatosis (LAM)Who this might be right forTuberous Sclerosis Complex (TSC)Lymphangioleiomyomatosis (LAM) Novartis Pharmaceuticals 118
Not applicableStudy completedNCT06218134What this trial is testingEvaluate the Safety and Potential Efficacy of Human Wharton's Jelly-derived Mesenchymal Stem Cells With Charcot-Marie-Tooth Disease Type 1EWho this might be right forCharcot-Marie-Tooth Disease, Type 1 Samsung Medical Center 3
Testing effectiveness (Phase 2)WithdrawnNCT01960023What this trial is testingSafety and Efficacy Study of Neratinib and Cetuximab to Treat Patients With Quadruple Wild-Type Metastatic Colorectal CancerWho this might be right forColorectal Cancer NSABP Foundation Inc
Testing effectiveness (Phase 2)Study completedNCT00457964What this trial is testingRAD001 Therapy of Angiomyolipomata in Patients With TS Complex and Sporadic LAMWho this might be right forTuberous SclerosisLymphangioleiomyomatosis Children's Hospital Medical Center, Cincinnati 36
Testing effectiveness (Phase 2)Study completedNCT00411619What this trial is testingEverolimus (RAD001) Therapy of Giant Cell Astrocytoma in Patients With Tuberous Sclerosis ComplexWho this might be right forTuberous SclerosisSubependymal Giant Cell Astrocytoma Children's Hospital Medical Center, Cincinnati 28
Not applicableLooking for participantsNCT01668186What this trial is testingLongitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)Who this might be right forPeroxisome Biogenesis DisorderZellweger Spectrum DisorderRCDP - Rhizomelic Chondrodysplasia Punctata+8 more McGill University Health Centre/Research Institute of the McGill University Health Centre 244
Early research (Phase 1)Study completedNCT00726583What this trial is testingPhase I Trial of Oral PX-866Who this might be right forAdvanced Solid Tumors Cascadian Therapeutics Inc. 90
Not applicableStudy completedNCT07263256What this trial is testingMedian Nerve Decompression for Complex Regional Pain Syndrome: A Clinical StudyWho this might be right forComplex Regional Pain Syndrome I (CRPS I)Nerve Entrapment Syndrome Jitka Fricova 74
Large-scale testing (Phase 3)UnknownNCT02055079What this trial is testingPulsed Oral Sirolimus in Autosomal Dominant Polycystic Kidney DiseaseWho this might be right forPolycystic Kidney, Type 1 Autosomal Dominant DiseasePolycystic Kidney, Type 2 Autosomal Dominant Disease Medical University of Vienna 68
Testing effectiveness (Phase 2)Looking for participantsNCT04657068What this trial is testingART0380 for the Treatment of Advanced or Metastatic Solid TumorsWho this might be right forAdvanced CancerMetastatic CancerOvarian Cancer+6 more Artios Pharma Ltd 442
Not applicableLooking for participantsNCT06708468What this trial is testingPersonalized Training for People With Rare Neuromuscular DisordersWho this might be right forNeuromuscular Diseases (NMD)Charcot Marie Tooth Disease (CMT)Facioscapulohumeral Muscular Dystrophy+1 more Oslo University Hospital 120
Early research (Phase 1)Study completedNCT05947578What this trial is testingThe Safety and Tolerability of CLZ-2002 in Patients With Charcot-Marie Tooth Disease.Who this might be right forCharcot Marie Tooth Disease, Type 1 Cellatoz Therapeutics, Inc 9
Testing effectiveness (Phase 2)Not Yet RecruitingNCT03520751What this trial is testingPhase I/IIa Trial of scAAV1.tMCK.NTF3 for Treatment of CMT1AWho this might be right forCharcot-Marie-Tooth Neuropathy Type 1A Nationwide Children's Hospital 3
Testing effectiveness (Phase 2)Study completedNCT06482437What this trial is testingSafety and Efficacy of NMD670 in Adult Patients With Type 1 and Type 2 Charcot-Marie-Tooth DiseaseWho this might be right forCharcot-Marie-Tooth Disease NMD Pharma A/S 81
Not applicableStudy completedNCT04980807What this trial is testingObservational Study of Neuromuscular Function in CMT Type 1&2 and Healthy ControlsWho this might be right forCharcot-Marie-Tooth Disease NMD Pharma A/S 30
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Not applicableLooking for participantsNCT01793168What this trial is testingRare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordWho this might be right forRare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more Sanford Health 20,000