Not applicableWithdrawnNCT01093105What this trial is testingAn Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (GLD)Who this might be right forLeukodystrophy, Globoid Cell Shire
Not applicableStudy completedNCT00983879What this trial is testingThe Natural History of Infantile Globoid Cell LeukodystrophyWho this might be right forInfantile Globoid Cell Leukodystrophy Zymenex A/S 6
Testing effectiveness (Phase 2)Active Not RecruitingNCT05739643What this trial is testingGene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCTWho this might be right forKrabbe Disease Forge Biologics, Inc 9
Testing effectiveness (Phase 2)Active Not RecruitingNCT02171104What this trial is testingMT2013-31: Allo HCT for Metabolic Disorders and Severe OsteopetrosisWho this might be right forMucopolysaccharidosis DisordersHurler SyndromeHunter Syndrome+26 more Masonic Cancer Center, University of Minnesota 149
Testing effectiveness (Phase 2)Temporarily pausedNCT04771416What this trial is testingStudy of Safety, Tolerability and Efficacy of PBKR03 in Pediatric Subjects With Early Infantile Krabbe DiseaseWho this might be right forLeukodystrophy, Globoid Cell Gemma Biotherapeutics 24