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Results for “Inherited Bone Marrow Failure Syndrome, Aplastic Anemia”

173 trials

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Showing 20 of 173 results

Not applicableActive Not RecruitingNCT05236764
What this trial is testing

Haploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion

Who this might be right for
Acute Lymphoblastic Leukemia in RemissionAcute Myeloid Leukemia in RemissionMyelodysplastic Syndromes+8 more
Baylor College of Medicine 3
Not applicableEnded earlyNCT00896740
What this trial is testing

Gene Function in Bone Marrow Cells From Patients With Fanconi Anemia and From Healthy Participants

Who this might be right for
Fanconi Anemia
OHSU Knight Cancer Institute 90
Testing effectiveness (Phase 2)Study completedNCT00630253
What this trial is testing

Cytoxan, Fludara, and Antithymocyte Globulin Conditioning Followed By Stem Cell Transplant in Treating Fanconi Anemia

Who this might be right for
Fanconi Anemia
Masonic Cancer Center, University of Minnesota 31
Large-scale testing (Phase 3)Study completedNCT00176878
What this trial is testing

Stem Cell Transplant for Bone Marrow Failure Syndromes

Who this might be right for
Diamond-Blackfan AnemiaKostmann's NeutropeniaShwachman-Diamond Syndrome
Masonic Cancer Center, University of Minnesota 10
Testing effectiveness (Phase 2)Study completedNCT00919503
What this trial is testing

Treosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited Disorders

Who this might be right for
Non-Neoplastic Hematologic and Lymphocytic Disorder
Fred Hutchinson Cancer Center 98
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07408583
What this trial is testing

Prenatal Transplantation for Fetuses With Fanconi Anemia

Who this might be right for
Fanconi AnemiaAnemia, Hypoplastic, CongenitalCongenital Bone Marrow Failure Syndromes+5 more
Agnieszka Czechowicz 12
Testing effectiveness (Phase 2)Ended earlyNCT00167206
What this trial is testing

Stem Cell Transplantation for Fanconi Anemia

Who this might be right for
Fanconi Anemia
Masonic Cancer Center, University of Minnesota 16
Testing effectiveness (Phase 2)Study completedNCT00578435
What this trial is testing

Allogeneic Bone Marrow Transplantation for the Treatment of Genetic Disorders of Erythropoiesis

Who this might be right for
Genetic DisordersSickle Cell Anemia
Memorial Sloan Kettering Cancer Center 25
Very early researchEnded earlyNCT00212407
What this trial is testing

New York Blood Center National Cord Blood Program

Who this might be right for
LeukemiaLymphomaGenetic Disease+2 more
New York Blood Center 4,476
Not applicableActive Not RecruitingNCT01199562
What this trial is testing

Infection Prophylaxis and Management in Treating Cytomegalovirus (CMV) Infection in Patients With Hematologic Malignancies Previously Treated With Donor Stem Cell Transplant

Who this might be right for
Hematopoietic/Lymphoid CancerAccelerated Phase Chronic Myelogenous LeukemiaAcute Undifferentiated Leukemia+151 more
City of Hope Medical Center 153
Very early researchLooking for participantsNCT02928991
What this trial is testing

Fludarabine Based RIC for Bone Marrow Failure Syndromes

Who this might be right for
Bone Marrow Failure Syndromes
Children's Hospital of Philadelphia 25
Early research (Phase 1)UnknownNCT00006127
What this trial is testing

Phase I Study of Amifostine in Patients With Bone Marrow Failure Related to Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
Dana-Farber Cancer Institute 21
Testing effectiveness (Phase 2)UnknownNCT02386267
What this trial is testing

L-leucine in Diamond Blackfan Anemia Patients

Who this might be right for
Diamond Blackfan Anemia
Federal Scientific Clinical Centre of Pediatric Hematology, Oncology and Immunology named after Dmitry Rogache 30
Testing effectiveness (Phase 2)Study completedNCT01362595
What this trial is testing

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan AnemiaBlackfan Diamond SyndromeDBA+2 more
Northwell Health 55
Testing effectiveness (Phase 2)Study completedNCT00004143
What this trial is testing

Allogeneic Mixed Chimerism Stem Cell Transplant Using Campath for Hemoglobinopathies & Bone Marrow Failure Syndromes

Who this might be right for
Sickle Cell AnemiaSevere Aplastic AnemiaParoxysmal Nocturnal Hemoglobinuria (PNH)+1 more
David Rizzieri, MD 2
Testing effectiveness (Phase 2)Active Not RecruitingNCT02061800
What this trial is testing

CD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell Transplant

Who this might be right for
Chronic Myeloid Leukemia (CML)Acute Myelogenous Leukemia (AML)Myelodysplastic Syndrome (MDS)+3 more
Diane George 14
Testing effectiveness (Phase 2)Ended earlyNCT02065869
What this trial is testing

Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant

Who this might be right for
Acute Lymphoblastic LeukemiaLeukemia, Acute Myeloid (AML), ChildLymphoma, Non-Hodgkin+10 more
Bellicum Pharmaceuticals 187
Not applicableStudy completedNCT06490510
What this trial is testing

Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau 227
Not applicableEnrolling By InvitationNCT04437771
What this trial is testing

Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

Who this might be right for
Fanconi Anemia Complementation Group AFanconi Anemia
Rocket Pharmaceuticals Inc. 9
Not applicableStudy completedNCT00005893
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders

Who this might be right for
NeutropeniaSickle Cell AnemiaThalassemia Major+1 more
Fairview University Medical Center
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