Not applicableStudy completedNCT03820804What this trial is testingNutritional Status in PhenylketonuriaWho this might be right forPhenylketonurias Universidade do Porto 94
Testing effectiveness (Phase 2)Looking for participantsNCT07558733What this trial is testingSapanisertib and Serabelisib (PIKTOR) in Various Combinations in Patients With HR+/HER2- Advanced/Metastatic Breast CancerWho this might be right forHR+ HER2- Breast Cancer Faeth Therapeutics 32
Not applicableStudy completedNCT01610011What this trial is testingAcute Glycine Pharmacodynamic StudyWho this might be right forSchizophreniaPsychotic Disorders Mclean Hospital 21
Not applicableLooking for participantsNCT06734611What this trial is testingFolic Acid Salt Study (FISFA Zambia)Who this might be right forFolate DeficiencyNeural Tube Defects University of Alabama at Birmingham 250
Not applicableStudy completedNCT04190147What this trial is testingEye and Growth in Adolescents Born Moderate-to-late PretermWho this might be right forPreterm BirthVisual ImpairmentEye Abnormalities Vastra Gotaland Region 100
Not applicableLooking for participantsNCT05128149What this trial is testingMetabolic Control and Patient Well-being in Phenylketonuria: do Guidelines Make a Difference?Who this might be right forPhenylketonurias University Children's Hospital, Zurich 200
Not applicableUnknownNCT03840928What this trial is testingPatientSpot Formerly Known as ArthritisPowerWho this might be right forRheumatoid ArthritisAnkylosing SpondylitisFibromyalgia+61 more Global Healthy Living Foundation 40,000
Early research (Phase 1)Study completedNCT02240407What this trial is testingRe-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe DiseaseWho this might be right forPompe Disease University of Florida 2
Not applicableStudy completedNCT02354664What this trial is testingDynamic Respiratory Muscle Function in Late-Onset Pompe DiseaseWho this might be right forPompe Disease University of Florida 14
Not applicableWithdrawnNCT03527498What this trial is testingEvaluation of Long-term Neurodevelopment in Neonatal Encephalopathy by Infant TreadmillWho this might be right forHypoxic-Ischemic EncephalopathyPeriventricular LeukomalaciaIntraventricular Hemorrhage+4 more Children's Hospital of Fudan University
Not applicableActive Not RecruitingNCT04612764What this trial is testingLiver Disease in Urea Cycle DisordersWho this might be right forUrea Cycle DisorderOrnithine Transcarbamylase DeficiencyCitrullinemia 1+5 more Baylor College of Medicine 62
Not applicableLooking for participantsNCT05760287What this trial is testingEchocardiographic Characterization of Cardiac AmyloidosisWho this might be right forCardiac Amyloidosis Fondazione Policlinico Universitario Agostino Gemelli IRCCS 255
Testing effectiveness (Phase 2)Study completedNCT02489292What this trial is testingStudy to Evaluate the Efficacy of HepaStem in Urea Cycle Disorders Paediatric Patients (HEP002)Who this might be right forUrea Cycle Disorders Cellaion SA 5
Large-scale testing (Phase 3)UnknownNCT01316744What this trial is testingKetamine Hydrochloride and Best Pain Management in Treating Cancer Patients With Neuropathic PainWho this might be right forCancer University of Glasgow 214
Large-scale testing (Phase 3)Ended earlyNCT00603109What this trial is testingEffect of Rimonabant on Weight Gain and Body Composition in Adults With Prader Willi SyndromeWho this might be right forPrader-willi Syndrome Weill Medical College of Cornell University 10
Post-approval studies (Phase 4)Study completedNCT02405598What this trial is testingEvaluation of Salbutamol as an Adjuvant Therapy for Pompe DiseaseWho this might be right forPompe Disease National Taiwan University Hospital 14
Not applicableWithdrawnNCT05041114What this trial is testingSWITCH II Early Feasibility Study: Implantable BCI to Control a Digital Device for People With ParalysisWho this might be right forNeurologic DisorderParalysisParalysis; Stroke+7 more Synchron Medical, Inc.
Not applicableStudy completedNCT02801539What this trial is testingRespiratory Muscle Training in L-Onset Pompe Disease (LOPD)Who this might be right forGlycogen Storage Disease Type II Duke University 22
Not applicableEnrolling By InvitationNCT07635030What this trial is testingGABA and GSH in FRDAWho this might be right forFriedreich's AtaxiaFRDA Children's Hospital of Philadelphia 60
Large-scale testing (Phase 3)WithdrawnNCT05815004What this trial is testingAn Efficacy and Safety Study of AVR-RD-02 Compared to Enzyme Replacement Therapy for Treatment of Gaucher Disease Type 3Who this might be right forGaucher Disease, Type 3 AVROBIO