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Results for “Isolated PREPL Deficiency”

1 trials

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Showing 1 of 1 results

Testing effectiveness (Phase 2)UnknownNCT02640443
What this trial is testing

Sulfamethoxazole for the Treatment of Primary PREPL Deficiency

Who this might be right for
Hypotonia Cystinuria SyndromeIsolated PREPL Deficiency
Universitair Ziekenhuis Brussel 15