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Results for “Juvenile Spinal Muscular Atrophy”

35 trials

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Showing 20 of 35 results

Not applicableUnknownNCT05272969
What this trial is testing

Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease

Who this might be right for
Pompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more
LMU Klinikum 95
Testing effectiveness (Phase 2)Study completedNCT03921528
What this trial is testing

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+6 more
Scholar Rock, Inc. 58
Not applicableActive Not RecruitingNCT04690998
What this trial is testing

Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients

Who this might be right for
Spinal Muscular Atrophy
Assistance Publique Hopitaux De Marseille 104
Testing effectiveness (Phase 2)Ended earlyNCT00439569
What this trial is testing

Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III

Who this might be right for
Spinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III
Westat 9
Not applicableUnknownNCT05544994
What this trial is testing

The Effect of Aerobic Exercise Training in Patients With Type III Spinal Muscular Atrophy

Who this might be right for
Neuromuscular DiseasesSpinal Muscular Atrophy Type 3
Istanbul Medipol University Hospital 20
Not applicableStudy completedNCT00466349
What this trial is testing

International SMA Patient Registry

Who this might be right for
Muscular Atrophy, Spinal
Indiana University School of Medicine 3,000
Not applicableActive Not RecruitingNCT03709784
What this trial is testing

Spinraza in Adult Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type 3
Washington University School of Medicine 148
Testing effectiveness (Phase 2)Study completedNCT00568802
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 27
Not applicableLooking for participantsNCT06562283
What this trial is testing

Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal AmyotrophyInfantile Spinal Muscular AtrophyJuvenile Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Saint Etienne 80
Testing effectiveness (Phase 2)Study completedNCT02227823
What this trial is testing

Safety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3

Who this might be right for
Spinal Muscular Atrophy Type 3
Centre Hospitalier Régional de la Citadelle 4
Not applicableUnknownNCT02831296
What this trial is testing

Prospective Evaluation of Infants With Spinal Muscular Atrophy:

Who this might be right for
Spinal Muscular Atrophy
Massachusetts General Hospital 1,000
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025
What this trial is testing

Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more
Novartis Gene Therapies 85
Testing effectiveness (Phase 2)Study completedNCT03781479
What this trial is testing

Controlled Trial to Evaluate Amifampridine Phosphate in Spinal Muscular Atrophy Type 3 Patients

Who this might be right for
Muscular Atrophy, Spinal
Catalyst Pharmaceuticals, Inc. 13
Not applicableLooking for participantsNCT06839469
What this trial is testing

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Who this might be right for
Spinal Muscular Atrophy Type 3Duchenne Muscular Dystrophy (DMD)
Columbia University 106
Testing effectiveness (Phase 2)Looking for participantsNCT07047144
What this trial is testing

Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySMASpinal Muscular Atrophy Type 2+3 more
Scholar Rock, Inc. 52
Not applicableStudy completedNCT02522507
What this trial is testing

A Peer E-mentoring Intervention to Improve Employment

Who this might be right for
Cerebral PalsySpina BifidaJuvenile Arthritis+3 more
Holland Bloorview Kids Rehabilitation Hospital 44
Not applicableActive Not RecruitingNCT05430113
What this trial is testing

Spinal Cord Stimulation in Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 4
Marco Capogrosso 3
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Not applicableLooking for participantsNCT07400198
What this trial is testing

Gait and Bone Health in SMA

Who this might be right for
Spinal Muscular Atrophy Type 3Ambulatory Spinal Muscular Atrophy
Jacqueline Montes 22
Testing effectiveness (Phase 2)Study completedNCT02941328
What this trial is testing

SPACE Trial: Pyridostigmine vs Placebo in SMA Types 2, 3 and 4

Who this might be right for
Spinal Muscular AtrophySMAKugelberg-Welander Disease
UMC Utrecht 39
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