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Results for “Juvenile Spinal Muscular Atrophy”

35 trials

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Showing 20 of 35 results

Large-scale testing (Phase 3)Study completedNCT05156320
What this trial is testing

Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+7 more
Scholar Rock, Inc. 188
Testing effectiveness (Phase 2)Looking for participantsNCT06421831
What this trial is testing

Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients

Who this might be right for
Spinal Muscular Atrophy Type 3
GeneCradle Inc 21
Testing effectiveness (Phase 2)Study completedNCT02941328
What this trial is testing

SPACE Trial: Pyridostigmine vs Placebo in SMA Types 2, 3 and 4

Who this might be right for
Spinal Muscular AtrophySMAKugelberg-Welander Disease
UMC Utrecht 39
Not applicableActive Not RecruitingNCT04690998
What this trial is testing

Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients

Who this might be right for
Spinal Muscular Atrophy
Assistance Publique Hopitaux De Marseille 104
Large-scale testing (Phase 3)Active Not RecruitingNCT05626855
What this trial is testing

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+7 more
Scholar Rock, Inc. 238
Testing effectiveness (Phase 2)Study completedNCT01302600
What this trial is testing

Safety and Efficacy of Olesoxime (TRO19622) in 3-25 Years SMA Patients.

Who this might be right for
Spinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III Non Ambulant
Hoffmann-La Roche 165
Not applicableLooking for participantsNCT06562283
What this trial is testing

Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy

Who this might be right for
Spinal AmyotrophyInfantile Spinal Muscular AtrophyJuvenile Spinal Muscular Atrophy
Centre Hospitalier Universitaire de Saint Etienne 80
Not applicableStudy completedNCT00756821
What this trial is testing

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy
Carelon Research 130
Testing effectiveness (Phase 2)Study completedNCT00568802
What this trial is testing

A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients

Who this might be right for
Muscular Atrophy, Spinal
Stanford University 27
Not applicableStudy completedNCT04907162
What this trial is testing

Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders

Who this might be right for
Pompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more
LMU Klinikum 82
Not applicableEnded earlyNCT03056144
What this trial is testing

Whole Body Vibration Therapy in Children With Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type 3
The Hong Kong Polytechnic University 1
Testing effectiveness (Phase 2)Ended earlyNCT00439569
What this trial is testing

Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III

Who this might be right for
Spinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III
Westat 9
Not applicableUnknownNCT02831296
What this trial is testing

Prospective Evaluation of Infants With Spinal Muscular Atrophy:

Who this might be right for
Spinal Muscular Atrophy
Massachusetts General Hospital 1,000
Not applicableStudy completedNCT05430113
What this trial is testing

Spinal Cord Stimulation in Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 4
Marco Capogrosso 3
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025
What this trial is testing

Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

Who this might be right for
Spinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more
Novartis Gene Therapies 85
Not applicableUnknownNCT03840928
What this trial is testing

PatientSpot Formerly Known as ArthritisPower

Who this might be right for
Rheumatoid ArthritisAnkylosing SpondylitisFibromyalgia+61 more
Global Healthy Living Foundation 40,000
Not applicableStudy completedNCT02895789
What this trial is testing

Oxidative Capacity and Exercise Tolerance in Ambulatory SMA

Who this might be right for
Spinal Muscular Atrophy Type 3Mitochondrial Myopathy
Columbia University 42
Testing effectiveness (Phase 2)Looking for participantsNCT07047144
What this trial is testing

Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySMASpinal Muscular Atrophy Type 2+3 more
Scholar Rock, Inc. 52
Not applicableActive Not RecruitingNCT03709784
What this trial is testing

Spinraza in Adult Spinal Muscular Atrophy

Who this might be right for
Spinal Muscular AtrophySpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type 3
Washington University School of Medicine 148
Testing effectiveness (Phase 2)Ended earlyNCT03819660
What this trial is testing

Long Term Safety of Amifampridine Phosphate in Spinal Muscular Atrophy 3

Who this might be right for
Spinal Muscular Atrophy Type 3
Catalyst Pharmaceuticals, Inc. 13
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