Not applicableStudy completedNCT02003937What this trial is testingAerobic Training in Patients With Spinal Muscular Atrophy Type IIIWho this might be right forSpinal Muscular Atrophy Rigshospitalet, Denmark 15
Not applicableActive Not RecruitingNCT04690998What this trial is testingOutcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV PatientsWho this might be right forSpinal Muscular Atrophy Assistance Publique Hopitaux De Marseille 104
Not applicableEnded earlyNCT03056144What this trial is testingWhole Body Vibration Therapy in Children With Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Type 3 The Hong Kong Polytechnic University 1
Large-scale testing (Phase 3)Active Not RecruitingNCT04042025What this trial is testingLong-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioiWho this might be right forSpinal Muscular Atrophy Type ISpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III+1 more Novartis Gene Therapies 85
Not applicableActive Not RecruitingNCT03709784What this trial is testingSpinraza in Adult Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type 3 Washington University School of Medicine 148
Not applicableUnknownNCT05272969What this trial is testingPompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe DiseaseWho this might be right forPompe Disease (Late-onset)Inclusion Body MyositisSpinal Muscular Atrophy Type 3+1 more LMU Klinikum 95
Not applicableUnknownNCT02831296What this trial is testingProspective Evaluation of Infants With Spinal Muscular Atrophy:Who this might be right forSpinal Muscular Atrophy Massachusetts General Hospital 1,000
Testing effectiveness (Phase 2)Looking for participantsNCT07047144What this trial is testingEvaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySMASpinal Muscular Atrophy Type 2+3 more Scholar Rock, Inc. 52
Testing effectiveness (Phase 2)Study completedNCT03781479What this trial is testingControlled Trial to Evaluate Amifampridine Phosphate in Spinal Muscular Atrophy Type 3 PatientsWho this might be right forMuscular Atrophy, Spinal Catalyst Pharmaceuticals, Inc. 13
Not applicableStudy completedNCT02522507What this trial is testingA Peer E-mentoring Intervention to Improve EmploymentWho this might be right forCerebral PalsySpina BifidaJuvenile Arthritis+3 more Holland Bloorview Kids Rehabilitation Hospital 44
Not applicableUnknownNCT05544994What this trial is testingThe Effect of Aerobic Exercise Training in Patients With Type III Spinal Muscular AtrophyWho this might be right forNeuromuscular DiseasesSpinal Muscular Atrophy Type 3 Istanbul Medipol University Hospital 20
Testing effectiveness (Phase 2)Study completedNCT03921528What this trial is testingAn Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular AtrophyWho this might be right forSpinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+6 more Scholar Rock, Inc. 58
Not applicableStudy completedNCT02895789What this trial is testingOxidative Capacity and Exercise Tolerance in Ambulatory SMAWho this might be right forSpinal Muscular Atrophy Type 3Mitochondrial Myopathy Columbia University 42
Not applicableStudy completedNCT00756821What this trial is testingA Pilot Study of Biomarkers for Spinal Muscular AtrophyWho this might be right forSpinal Muscular Atrophy Carelon Research 130
Not applicableLooking for participantsNCT06839469What this trial is testingEstablishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular DisordersWho this might be right forSpinal Muscular Atrophy Type 3Duchenne Muscular Dystrophy (DMD) Columbia University 106
Testing effectiveness (Phase 2)Ended earlyNCT00439569What this trial is testingClinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or IIIWho this might be right forSpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III Westat 9
Not applicableLooking for participantsNCT06562283What this trial is testingEvaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular AtrophyWho this might be right forSpinal AmyotrophyInfantile Spinal Muscular AtrophyJuvenile Spinal Muscular Atrophy Centre Hospitalier Universitaire de Saint Etienne 80
Not applicableStudy completedNCT04193085What this trial is testingWearable Technology to Assess Gait Function in SMA and DMDWho this might be right forSpinal Muscular Atrophy Type 3Duchenne Muscular Dystrophy Columbia University 39
Large-scale testing (Phase 3)Study completedNCT05156320What this trial is testingEfficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or RisdiplamWho this might be right forSpinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type 2+7 more Scholar Rock, Inc. 188
Testing effectiveness (Phase 2)Study completedNCT01302600What this trial is testingSafety and Efficacy of Olesoxime (TRO19622) in 3-25 Years SMA Patients.Who this might be right forSpinal Muscular Atrophy Type IISpinal Muscular Atrophy Type III Non Ambulant Hoffmann-La Roche 165